Phase II Trial of Pembrolizumab after High-Dose Cytarabine in Relapsed/Refractory Acute Myeloid Leukemia.


Journal

Blood cancer discovery
ISSN: 2643-3249
Titre abrégé: Blood Cancer Discov
Pays: United States
ID NLM: 101764786

Informations de publication

Date de publication:
Nov 2021
Historique:
received: 23 04 2021
revised: 12 07 2021
accepted: 25 08 2021
entrez: 15 11 2021
pubmed: 16 11 2021
medline: 16 11 2021
Statut: epublish

Résumé

Immune suppression, exhaustion, and senescence are frequently seen throughout disease progression in acute myeloid leukemia (AML). We conducted a phase II study of high-dose cytarabine followed by pembrolizumab 200 mg i.v. on day 14 to examine whether PD-1 inhibition improves clinical responses in relapsed/refractory (R/R) AML. Overall responders could receive pembrolizumab maintenance up to 2 years. Among 37 patients enrolled, the overall response rate, composite complete remission (CRc) rate (primary endpoint), and median overall survival (OS) were 46%, 38%, and 11.1 months, respectively. Patients with refractory/early relapse and those receiving treatment as first salvage had encouraging outcomes (median OS, 13.2 and 11.3 months, respectively). Grade ≥3 immune-related adverse events were rare (14%) and self-limiting. Patients who achieved CRc had a higher frequency of progenitor exhausted CD8 Immune-checkpoint blockade with pembrolizumab was tolerable and feasible after high-dose cytarabine in R/R AML, with encouraging clinical activity, particularly in refractory AML and those receiving treatment as first salvage regimen. Further study of pembrolizumab and other immune-checkpoint blockade strategies after cytotoxic chemotherapy is warranted in AML.

Identifiants

pubmed: 34778801
doi: 10.1158/2643-3230.BCD-21-0070
pii: 2643-3230.BCD-21-0070
pmc: PMC8580622
doi:

Substances chimiques

Antibodies, Monoclonal, Humanized 0
Cytarabine 04079A1RDZ
pembrolizumab DPT0O3T46P

Types de publication

Clinical Trial, Phase II Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Pagination

616-629

Subventions

Organisme : NCI NIH HHS
ID : P50 CA058223
Pays : United States
Organisme : NCI NIH HHS
ID : R37 CA247676
Pays : United States

Commentaires et corrections

Type : CommentIn

Informations de copyright

©2021 American Association for Cancer Research.

Références

Clin Lymphoma Myeloma Leuk. 2020 Nov;20(11):e871-e882
pubmed: 32792304
J Immunother Cancer. 2015 Jun 16;3:23
pubmed: 26085931
Nat Med. 2020 Sep;26(9):1468-1479
pubmed: 32778827
Cancer Cell. 2020 Sep 14;38(3):380-399.e13
pubmed: 32649887
Cancer Cell. 2014 May 12;25(5):590-604
pubmed: 24794706
Blood. 2011 Nov 10;118(19):5084-95
pubmed: 21881045
Blood. 2015 Jan 1;125(1):133-9
pubmed: 25381062
Eur J Immunol. 2013 Mar;43(3):747-57
pubmed: 23175469
Blood. 2010 Aug 19;116(7):1124-31
pubmed: 20472834
JCI Insight. 2018 Nov 2;3(21):
pubmed: 30385732
Oncologist. 2020 Oct;25(10):878-885
pubmed: 32720734
Cancer Res. 2016 Jan 15;76(2):227-38
pubmed: 26637667
J Hematol Oncol. 2020 Apr 3;13(1):28
pubmed: 32245463
Blood. 2015 Feb 26;125(9):1367-76
pubmed: 25550361
Leuk Res. 1999 Sep;23(9):787-94
pubmed: 10475617
Nat Immunol. 2019 Mar;20(3):326-336
pubmed: 30778252
Lancet Oncol. 2015 Sep;16(9):1025-1036
pubmed: 26234174
Am J Hematol. 2019 Jan;94(1):111-117
pubmed: 30370956
Blood. 2010 Oct 7;116(14):2484-93
pubmed: 20570856
Blood. 2010 Jan 21;115(3):453-74
pubmed: 19880497
J Clin Oncol. 2012 Jul 10;30(20):2492-9
pubmed: 22585697
N Engl J Med. 2019 Oct 31;381(18):1728-1740
pubmed: 31665578
J Clin Oncol. 2014 Jun 20;32(18):1919-26
pubmed: 24841975
Blood. 2021 Feb 11;137(6):751-762
pubmed: 32929488
J Clin Oncol. 2005 Mar 20;23(9):1969-78
pubmed: 15632409
Immunity. 2019 Jan 15;50(1):195-211.e10
pubmed: 30635237
Blood. 2010 Aug 5;116(5):788-92
pubmed: 20442368
Haematologica. 2015 Oct;100(10):e409-11
pubmed: 26160876
Eur J Haematol. 2008 Feb;80(2):115-26
pubmed: 18076637
Immunity. 2019 Jan 15;50(1):181-194.e6
pubmed: 30635236
F1000Res. 2017 May 26;6:748
pubmed: 28663787
Cancer. 2019 May 1;125(9):1470-1481
pubmed: 30500073
Nat Immunol. 2020 Dec;21(12):1552-1562
pubmed: 33046887
Br J Haematol. 2003 Jun;121(5):692-702
pubmed: 12780783
Cancer Discov. 2019 Mar;9(3):370-383
pubmed: 30409776
Blood. 2011 Jan 13;117(2):608-17
pubmed: 20935254
Blood. 2017 Aug 10;130(6):722-731
pubmed: 28588020
Commun Biol. 2019 May 14;2:183
pubmed: 31098416
N Engl J Med. 2016 Jun 9;374(23):2209-2221
pubmed: 27276561
Cell Syst. 2015 Dec 23;1(6):417-425
pubmed: 26771021
Blood Adv. 2020 Oct 27;4(20):5011-5024
pubmed: 33057635
Eur J Haematol. 2014 Mar;92(3):195-203
pubmed: 24175978
Nature. 2019 Dec;576(7787):465-470
pubmed: 31827286
Lancet Haematol. 2019 Sep;6(9):e480-e488
pubmed: 31400961
Sci Transl Med. 2020 Jun 3;12(546):
pubmed: 32493790
N Engl J Med. 2018 Jun 21;378(25):2386-2398
pubmed: 29860938
J Clin Oncol. 2017 Mar;35(7):709-717
pubmed: 27646942
Blood. 1996 Jul 15;88(2):756
pubmed: 8695828
Blood. 2010 Dec 23;116(26):5818-23; quiz 6153
pubmed: 20923968
Clin Cancer Res. 2019 Jul 15;25(14):4231-4237
pubmed: 30992301
JAMA Oncol. 2020 Dec 1;6(12):1890-1899
pubmed: 33030517
Cancer Immunol Immunother. 2010 Dec;59(12):1839-49
pubmed: 20814675

Auteurs

Joshua F Zeidner (JF)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina. Joshua_Zeidner@med.unc.edu.
Division of Hematology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.

Benjamin G Vincent (BG)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
Division of Hematology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.
University of North Carolina, Department of Microbiology and Immunology, Chapel Hill, North Carolina.
Program in Computational Medicine, University of North Carolina at Chapel Hill, Chapel Hill, North Carolina.

Anastasia Ivanova (A)

University of North Carolina School of Medicine, Department of Biostatistics, Chapel Hill, North Carolina.

Dominic Moore (D)

University of North Carolina School of Medicine, Department of Biostatistics, Chapel Hill, North Carolina.

Karen P McKinnon (KP)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
University of North Carolina, Department of Microbiology and Immunology, Chapel Hill, North Carolina.

Alec D Wilkinson (AD)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.

Rupkatha Mukhopadhyay (R)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.

Francesco Mazziotta (F)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
University of Siena, Department of Medical Biotechnologies, Siena, Italy.

Hanna A Knaus (HA)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.

Matthew C Foster (MC)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
Division of Hematology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.

Catherine C Coombs (CC)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
Division of Hematology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.

Katarzyna Jamieson (K)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
Division of Hematology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.

Hendrik Van Deventer (H)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
Division of Hematology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.

Jonathan A Webster (JA)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
Department of Oncology, Division of Hematological Malignancies, Johns Hopkins School of Medicine, Baltimore, Maryland.

Gabrielle T Prince (GT)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
Department of Oncology, Division of Hematological Malignancies, Johns Hopkins School of Medicine, Baltimore, Maryland.

Amy E DeZern (AE)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
Department of Oncology, Division of Hematological Malignancies, Johns Hopkins School of Medicine, Baltimore, Maryland.

B Douglas Smith (BD)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
Department of Oncology, Division of Hematological Malignancies, Johns Hopkins School of Medicine, Baltimore, Maryland.

Mark J Levis (MJ)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
Department of Oncology, Division of Hematological Malignancies, Johns Hopkins School of Medicine, Baltimore, Maryland.

Nathan D Montgomery (ND)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
Department of Pathology and Laboratory Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.

Leo Luznik (L)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
Department of Oncology, Division of Hematological Malignancies, Johns Hopkins School of Medicine, Baltimore, Maryland.

Jonathan S Serody (JS)

University of North Carolina School of Medicine, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina.
Division of Hematology, Department of Medicine, University of North Carolina School of Medicine, Chapel Hill, North Carolina.
University of North Carolina, Department of Microbiology and Immunology, Chapel Hill, North Carolina.
Program in Computational Medicine, University of North Carolina at Chapel Hill, Chapel Hill, North Carolina.

Ivana Gojo (I)

Johns Hopkins School of Medicine, Sidney Kimmel Comprehensive Cancer Center, Baltimore, Maryland.
University of Siena, Department of Medical Biotechnologies, Siena, Italy.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH