Repurposing of Trimetazidine for amyotrophic lateral sclerosis: A study in SOD1


Journal

British journal of pharmacology
ISSN: 1476-5381
Titre abrégé: Br J Pharmacol
Pays: England
ID NLM: 7502536

Informations de publication

Date de publication:
04 2022
Historique:
revised: 09 09 2021
received: 16 07 2021
accepted: 23 10 2021
pubmed: 17 11 2021
medline: 14 4 2022
entrez: 16 11 2021
Statut: ppublish

Résumé

Amyotrophic lateral sclerosis (ALS), a neurodegenerative disease characterized by the degeneration of upper and lower motor neurons, progressive wasting and paralysis of voluntary muscles and is currently incurable. Although considered to be a pure motor neuron disease, increasing evidence indicates that the sole protection of motor neurons by a single targeted drug is not sufficient to improve the pathological phenotype. We therefore evaluated the therapeutic potential of the multi-target drug used to treatment of coronary artery disease, trimetazidine, in SOD1 As a metabolic modulator, trimetazidine improves glucose metabolism. Furthermore, trimetazidine enhances mitochondrial metabolism and promotes nerve regeneration, exerting an anti-inflammatory and antioxidant effect. We orally treated SOD1 Trimetazidine administration delays motor function decline, improves muscle performance and metabolism, and significantly extends overall survival of SOD1 In SOD1

Sections du résumé

BACKGROUND AND PURPOSE
Amyotrophic lateral sclerosis (ALS), a neurodegenerative disease characterized by the degeneration of upper and lower motor neurons, progressive wasting and paralysis of voluntary muscles and is currently incurable. Although considered to be a pure motor neuron disease, increasing evidence indicates that the sole protection of motor neurons by a single targeted drug is not sufficient to improve the pathological phenotype. We therefore evaluated the therapeutic potential of the multi-target drug used to treatment of coronary artery disease, trimetazidine, in SOD1
EXPERIMENTAL APPROACH
As a metabolic modulator, trimetazidine improves glucose metabolism. Furthermore, trimetazidine enhances mitochondrial metabolism and promotes nerve regeneration, exerting an anti-inflammatory and antioxidant effect. We orally treated SOD1
KEY RESULTS
Trimetazidine administration delays motor function decline, improves muscle performance and metabolism, and significantly extends overall survival of SOD1
CONCLUSION AND IMPLICATIONS
In SOD1

Identifiants

pubmed: 34783031
doi: 10.1111/bph.15738
pmc: PMC9305494
doi:

Substances chimiques

Superoxide Dismutase EC 1.15.1.1
Superoxide Dismutase-1 EC 1.15.1.1
Trimetazidine N9A0A0R9S8

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1732-1752

Informations de copyright

© 2021 The Authors. British Journal of Pharmacology published by John Wiley & Sons Ltd on behalf of British Pharmacological Society.

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Auteurs

Silvia Scaricamazza (S)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
Department of Biology, University of Rome "Tor Vergata", Rome, Italy.

Illari Salvatori (I)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
Department of Experimental Medicine, University of Roma "La Sapienza", Rome, Italy.

Susanna Amadio (S)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.

Valentina Nesci (V)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.

Alessio Torcinaro (A)

National Council of Research (CNR), Institute of Cell Biology and Neurology (IBCN), Rome, Italy.

Giacomo Giacovazzo (G)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
Department of Biology, University of Rome "Tor Vergata", Rome, Italy.

Aniello Primiano (A)

Department of Chemistry, Biochemistry and Molecular Biology Clinic, Università Cattolica del Sacro Cuore, Rome, Italy.
Department of Chemistry, Biochemistry and Molecular Biology Clinic, Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.

Michela Gloriani (M)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.

Niccolò Candelise (N)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
National Research Council (CNR), Institute of Translational Pharmacology (IFT), Rome, Italy.

Luisa Pieroni (L)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.

Jean-Philippe Loeffler (JP)

Centre de Recherche de Biomédecine de Strasbourg (CRBS), Université de Strasbourg, Strasbourg, France.
INSERM, U1118, Central and Peripheral Mechanisms of Neurodegeneration, Strasbourg, France.

Frederique Renè (F)

Centre de Recherche de Biomédecine de Strasbourg (CRBS), Université de Strasbourg, Strasbourg, France.
INSERM, U1118, Central and Peripheral Mechanisms of Neurodegeneration, Strasbourg, France.

Cyril Quessada (C)

Centre de Recherche de Biomédecine de Strasbourg (CRBS), Université de Strasbourg, Strasbourg, France.
INSERM, U1118, Central and Peripheral Mechanisms of Neurodegeneration, Strasbourg, France.

Tesfaye W Tefera (TW)

Australian Institute for Bioengineering and Nanotechnology, The University of Queensland, Brisbane, Queensland, Australia.

Hao Wang (H)

Australian Institute for Bioengineering and Nanotechnology, The University of Queensland, Brisbane, Queensland, Australia.

Frederik J Steyn (FJ)

School of Biomedical Sciences, The University of Queensland, Brisbane, Queensland, Australia.
Centre for Clinical Research, The University of Queensland, Brisbane, Queensland, Australia.

Shyuan T Ngo (ST)

Australian Institute for Bioengineering and Nanotechnology, The University of Queensland, Brisbane, Queensland, Australia.
Centre for Clinical Research, The University of Queensland, Brisbane, Queensland, Australia.

Gabriella Dobrowolny (G)

DAHFMO-Unit of Histology and Medical Embryology, Laboratory Affiliated to Istituto Pasteur Italia-Fondazione Cenci Bolognetti, University of Roma "La Sapienza", Rome, Italy.

Elisa Lepore (E)

DAHFMO-Unit of Histology and Medical Embryology, Laboratory Affiliated to Istituto Pasteur Italia-Fondazione Cenci Bolognetti, University of Roma "La Sapienza", Rome, Italy.

Andrea Urbani (A)

Department of Chemistry, Biochemistry and Molecular Biology Clinic, Fondazione Policlinico Universitario A. Gemelli IRCCS, Rome, Italy.
National Research Council (CNR), Institute of Translational Pharmacology (IFT), Rome, Italy.

Antonio Musarò (A)

DAHFMO-Unit of Histology and Medical Embryology, Laboratory Affiliated to Istituto Pasteur Italia-Fondazione Cenci Bolognetti, University of Roma "La Sapienza", Rome, Italy.

Cinzia Volonté (C)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
National Research Council (CNR), Institute for Systems Analysis and Computer Science (IASI), Rome, Italy.

Elisabetta Ferraro (E)

Department of Biology, University of Pisa, Pisa, Italy.

Roberto Coccurello (R)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
National Research Council (CNR), Institute for Complex System (ISC), Rome, Italy.

Cristiana Valle (C)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
National Research Council (CNR), Institute of Translational Pharmacology (IFT), Rome, Italy.

Alberto Ferri (A)

Division of Experimental Neuroscience, IRCCS Fondazione Santa Lucia, Via del Fosso di Fiorano 64, Rome, 00143, Italy.
National Research Council (CNR), Institute of Translational Pharmacology (IFT), Rome, Italy.

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Classifications MeSH