Cadence discovery: study protocol for a dose-finding and mechanism of action clinical trial of sodium benzoate in people with treatment-refractory schizophrenia.


Journal

Trials
ISSN: 1745-6215
Titre abrégé: Trials
Pays: England
ID NLM: 101263253

Informations de publication

Date de publication:
13 Dec 2021
Historique:
received: 08 04 2021
accepted: 28 11 2021
entrez: 14 12 2021
pubmed: 15 12 2021
medline: 17 12 2021
Statut: epublish

Résumé

Schizophrenia is a persistent psychotic disorder often accompanied by severe disability and premature mortality. New pharmacological treatments are urgently needed. Sodium benzoate, a common food preservative holds potential to be an effective, accessible treatment for schizophrenia, though the optimal dosing and mechanism of action of the compound requires further investigation. Individuals with persistent treatment-refractory schizophrenia (n=52) will be recruited. Patients will be randomised in a 1:1:1:1 ratio to receive treatment of one of three active doses (1000, 2000 or 4000 mg daily) of sodium benzoate or placebo for 6 weeks duration. The primary outcome measurement is change in the Positive and Negative Syndrome Scale (PANSS) total score. Secondary outcome measurements are PANSS subscales, Global Assessment of Function (GAF), Clinical Global Impression (CGI) and Patient Global Impression (PGI-I). Change in concentrations of peripheral amino acids (D-alanine, L-alanine, D-serine, L-serine, glycine and glutamate), plasma sodium benzoate, plasma catalase, 3-nitrotyrosine, malondialdehyde and high-sensitivity C-reactive protein (hs-CRP) will be determined as tertiary measures. This trial seeks to build upon previous research indicating potential efficacy of sodium benzoate for reduction of symptoms in individuals with treatment-refractory schizophrenia. The trial aims to improve the understanding of the mechanism of action of the compound. Australian New Zealand Clinical Trials Registry (ANZCTR) ACTRN12621000327886 . Registered on 23 March 2021.

Sections du résumé

BACKGROUND BACKGROUND
Schizophrenia is a persistent psychotic disorder often accompanied by severe disability and premature mortality. New pharmacological treatments are urgently needed. Sodium benzoate, a common food preservative holds potential to be an effective, accessible treatment for schizophrenia, though the optimal dosing and mechanism of action of the compound requires further investigation.
METHODS METHODS
Individuals with persistent treatment-refractory schizophrenia (n=52) will be recruited. Patients will be randomised in a 1:1:1:1 ratio to receive treatment of one of three active doses (1000, 2000 or 4000 mg daily) of sodium benzoate or placebo for 6 weeks duration. The primary outcome measurement is change in the Positive and Negative Syndrome Scale (PANSS) total score. Secondary outcome measurements are PANSS subscales, Global Assessment of Function (GAF), Clinical Global Impression (CGI) and Patient Global Impression (PGI-I). Change in concentrations of peripheral amino acids (D-alanine, L-alanine, D-serine, L-serine, glycine and glutamate), plasma sodium benzoate, plasma catalase, 3-nitrotyrosine, malondialdehyde and high-sensitivity C-reactive protein (hs-CRP) will be determined as tertiary measures.
DISCUSSION CONCLUSIONS
This trial seeks to build upon previous research indicating potential efficacy of sodium benzoate for reduction of symptoms in individuals with treatment-refractory schizophrenia. The trial aims to improve the understanding of the mechanism of action of the compound.
TRIAL REGISTRATION BACKGROUND
Australian New Zealand Clinical Trials Registry (ANZCTR) ACTRN12621000327886 . Registered on 23 March 2021.

Identifiants

pubmed: 34903265
doi: 10.1186/s13063-021-05890-6
pii: 10.1186/s13063-021-05890-6
pmc: PMC8670031
doi:

Substances chimiques

Antipsychotic Agents 0
Sodium Benzoate OJ245FE5EU

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

918

Informations de copyright

© 2021. The Author(s).

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Auteurs

Andrea Baker (A)

QIMR Berghofer Medical Research Institute, Herston, QLD, Australia.
Queensland Centre for Mental Health Research, The Park Centre for Mental Health, Wacol, QLD, Australia.

Lachlan Clarke (L)

QIMR Berghofer Medical Research Institute, Herston, QLD, Australia.
Faculty of Medicine, The University of Queensland, Herston, QLD, Australia.

Peter Donovan (P)

Faculty of Medicine, The University of Queensland, Herston, QLD, Australia.
Clinical Pharmacology, Royal Brisbane and Women's Hospital, Herston, QLD, 4006, Australia.

Jacobus P J Ungerer (J)

School of Biomedical Sciences, The University of Queensland, Herston, QLD, Australia.
Pathology Queensland, Royal Brisbane and Women's Hospital, Herston, QLD, Australia.

Gunter Hartel (G)

QIMR Berghofer Medical Research Institute, Herston, QLD, Australia.

George Bruxner (G)

Metro North Mental Health Service, Caboolture Hospital, Caboolture, QLD, Australia.

Luca Cocchi (L)

QIMR Berghofer Medical Research Institute, Herston, QLD, Australia.

Anne Gordon (A)

Metro North Mental Health Service, The Prince Charles Hospital, Chermside, QLD, Australia.

Vikas Moudgil (V)

Metro North Mental Health Service, Royal Brisbane and Women's Hospital, Herston, QLD, Australia.

Gail Robinson (G)

Faculty of Medicine, The University of Queensland, Herston, QLD, Australia.
Metro North Mental Health Service, Caboolture Hospital, Caboolture, QLD, Australia.

Digant Roy (D)

Metro North Mental Health Service, The Prince Charles Hospital, Chermside, QLD, Australia.

Ravinder Sohal (R)

Metro North Mental Health Service, Royal Brisbane and Women's Hospital, Herston, QLD, Australia.

Emma Whittle (E)

Clinical Pharmacology, Royal Brisbane and Women's Hospital, Herston, QLD, 4006, Australia.

James G Scott (JG)

QIMR Berghofer Medical Research Institute, Herston, QLD, Australia. james.scott@qimrberghofer.edu.au.
Queensland Centre for Mental Health Research, The Park Centre for Mental Health, Wacol, QLD, Australia. james.scott@qimrberghofer.edu.au.
Faculty of Medicine, The University of Queensland, Herston, QLD, Australia. james.scott@qimrberghofer.edu.au.
Metro North Mental Health Service, Royal Brisbane and Women's Hospital, Herston, QLD, Australia. james.scott@qimrberghofer.edu.au.

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Classifications MeSH