Understanding the Patient Experience of Hunger and Improved Quality of Life with Setmelanotide Treatment in POMC and LEPR Deficiencies.

Disease Burden Hyperphagia Leptin Receptor Melanocortin Receptor Pro-Opiomelanocortin Rare Genetic Diseases of Obesity

Journal

Advances in therapy
ISSN: 1865-8652
Titre abrégé: Adv Ther
Pays: United States
ID NLM: 8611864

Informations de publication

Date de publication:
04 2022
Historique:
received: 20 12 2021
accepted: 26 01 2022
pubmed: 23 2 2022
medline: 12 4 2022
entrez: 22 2 2022
Statut: ppublish

Résumé

In patients with pro-opiomelanocortin (POMC) or leptin receptor (LEPR) deficiency, managing obesity and hyperphagia can be burdensome for patients and caretakers. The impacts on health-related quality of life are under-recognized and are not well characterized. We conducted in-depth qualitative interviews in patients with POMC (n = 3) and LEPR (n = 2) deficiencies participating in an ongoing open-label extension of phase 3 clinical trials with the melanocortin receptor 4 agonist setmelanotide to describe the patient experience of hyperphagia and characterize changes following treatment with setmelanotide. Prior to setmelanotide treatment, all five patients described abnormal sensations of hunger with none indicating feeling satiated after meals and also reported that the burden of hyperphagia impacted their families, emotions, and work and/or school functioning. Following setmelanotide treatment, all five patients reported consistent reductions in hunger and weight, decreased eating, and feeling satiated after meals in addition to substantial improvements in each area of functioning they had previously reported. All five patients indicated they were very satisfied with the impact of setmelanotide on their quality of life and would be upset if treatment was discontinued. In patients with POMC or LEPR deficiency, hyperphagia and the inability to feel satiety negatively impacted quality of life. By reducing hunger and improving satiety, setmelanotide facilitated important changes in the lives of these patients. This qualitative research study suggests that the impact of setmelanotide goes beyond favorable clinical changes (e.g., weight and hunger) to also include quality of life improvements that are highly meaningful to patients.

Identifiants

pubmed: 35192151
doi: 10.1007/s12325-022-02059-8
pii: 10.1007/s12325-022-02059-8
pmc: PMC8862005
doi:

Substances chimiques

setmelanotide 0
alpha-MSH 581-05-5
Pro-Opiomelanocortin 66796-54-1

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Pagination

1772-1783

Informations de copyright

© 2022. The Author(s).

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Auteurs

Martin Wabitsch (M)

Division of Paediatric Endocrinology and Diabetes, Centre for Hormonal Disorders in Children and Adolescents, Department of Paediatrics and Adolescent Medicine, Ulm University Hospital, Eythstraße 24, 89075, Ulm, Germany. martin.wabitsch@uniklinik-ulm.de.

Sheri Fehnel (S)

RTI Health Solutions, Research Triangle Park, NC, USA.

Usha G Mallya (UG)

Rhythm Pharmaceuticals, Inc, Boston, MA, USA.

Martina Sluga-O'Callaghan (M)

RTI Health Solutions, Research Triangle Park, NC, USA.

David Richardson (D)

RTI Health Solutions, Research Triangle Park, NC, USA.

Mark Price (M)

RTI Health Solutions, Research Triangle Park, NC, USA.

Peter Kühnen (P)

Institute for Experimental Pediatric Endocrinology, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin, Humboldt-Universität Zu Berlin, and Berlin Institute of Health, Augustenburger Platz 1, 13353, Berlin, Germany. peter.kuehnen@charite.de.

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