Effectiveness and Safety of Adalimumab, Etanercept and Ustekinumab for Severe Psoriasis in Children Under 12 Years of Age: A French-Italian Daily Practice Cohort (BiPe Jr).


Journal

Paediatric drugs
ISSN: 1179-2019
Titre abrégé: Paediatr Drugs
Pays: Switzerland
ID NLM: 100883685

Informations de publication

Date de publication:
May 2022
Historique:
accepted: 13 03 2022
pubmed: 11 4 2022
medline: 7 5 2022
entrez: 10 4 2022
Statut: ppublish

Résumé

Biological therapies are valuable treatments for severe psoriasis. Children aged under 12 years are underrepresented in therapeutic trials for these drugs. The objective of the 'BiPe Jr' cohort study was to evaluate the drug survival, effectiveness, tolerance and switching patterns of biological therapies in children under 12 years of age with psoriasis. We conducted a multicentre retrospective study of children with psoriasis who received at least one injection of a biological agent, even off-licence, before the age of 12 years in France and Italy, collecting the data between April and August 2021. The data collected were from March 2012 up to August 2021. In total, 82 children (mean age: 9.1 years; females: 61.0%) received 106 treatments. The drugs administered were adalimumab (n = 49), etanercept (n = 37), ustekinumab (n = 15), anakinra (n = 2), infliximab (n = 2) and secukinumab (n = 1). The most common form of psoriasis was plaque psoriasis (62.9%). The Physician Global Assessment and the Psoriasis Area Severity Index (PASI) scores decreased significantly from baseline to 3 months after treatment initiation for the three main biological drugs; PASI went from 14.1 ± 9.4 to 4.1 ± 11.3 for adalimumab (p = 0.001), 14.9 ± 9.3 to 5.1 ± 4.0 for etanercept (p = 0.002) and 11.6 ± 8.3 to 2.6 ± 2.2 for ustekinumab (p = 0.007). A trend towards higher 2-year maintenance rates was observed for ustekinumab and adalimumab, compared with etanercept (p = 0.06). 52 children discontinued their biological therapy, most frequently due to inefficacy (n = 28) and remission (n = 14). Seven serious adverse events (SAEs) were reported, including four severe infections. Our analyses of drug survival and treatment patterns, combined with those of previous studies conducted in older children, indicate that there is a trend towards higher 2-year survival rates of ustekinumab and adalimumab. The SAEs identified were rare, but highlight the need for increased vigilance concerning infections. Overall, the biological therapies showed good effectiveness and safety profiles when used in daily practice for the treatment of young children with psoriasis.

Identifiants

pubmed: 35397731
doi: 10.1007/s40272-022-00501-6
pii: 10.1007/s40272-022-00501-6
doi:

Substances chimiques

Ustekinumab FU77B4U5Z0
Adalimumab FYS6T7F842
Etanercept OP401G7OJC

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

281-292

Informations de copyright

© 2022. The Author(s), under exclusive licence to Springer Nature Switzerland AG.

Références

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Auteurs

Jinane Zitouni (J)

Dermatology Department, Hôpital Victor Dupouy, Argenteuil, France.

Alain Beauchet (A)

Public Health Department, Centre Hospitalier Universitaire Ambroise Paré, Boulogne-Billancourt, France.

Raphaëlle Curmin (R)

Sorbonne University, INSERM, Institut Pierre Louis d'Epidémiologie et de Santé Publique, Paris, France.

Vito Di Lernia (V)

Dermatology unit, Arcispedale S. Maria Nuova IRCCS, Reggio Emilia, Italy.

Anne-Claire Bursztejn (AC)

Dermatology Department, Hôpitaux de Brabois, Centre Hospitalier Universitaire de Nancy, Vandoeuvre-lès-Nancy, France.

Juliette Mazereeuw-Hautier (J)

Dermatology Department, Centre de référence des maladies rares de la peau et des muqueuses, Hôpital Larrey, Toulouse, France.

Jérémy Gottlieb (J)

Immunology and Dermatology Department, Hôpital Bicêtre, CHU de Bicêtre, Assistance Publique-Hôpitaux de Paris, Université Paris-Saclay, Le Kremlin Bicêtre, France.

Audrey Lasek (A)

Dermatology Department,, Hôpital Saint Vincent de Paul, Université Catholique de Lille, Lille, France.

Hélène Aubert (H)

Dermatology Department, Centre Hospitalier Universitaire de Nantes, Nantes, France.

Catherine Droitcourt (C)

Dermatology Department, Centre Hospitalier Universitaire Pontchaillou, Rennes, France.

Cristina Bulai-Livideanu (C)

Dermatology Department, Hôpital Larrey, Toulouse, France.

Anna Belloni Fortina (AB)

Pediatric Dermatology Unit, Department of Medicine DIMED, University of Padova, Padua, Italy.

Francesca Caroppo (F)

Pediatric Dermatology Unit, Department of Medicine DIMED, University of Padova, Padua, Italy.

Nathalie Quiles-Tsimaratos (N)

Dermatology Department, Hôpital Saint-Joseph, Marseille, France.

Stéphanie Mallet (S)

Dermatology Department, Hôpital de la Timone, Assistance-publique-Hôpitaux de Marseille, Marseille, France.

Hugues Barthélémy (H)

Dermatology Department, Centre Hospitalier d'Auxerre, Auxerre, France.

Eve Puzenat (E)

Dermatology Department, Centre Hospitalier Universitaire Saint-Jacques, Besançon, France.

Danielle Bouilly-Auvray (D)

Dermatology Department, Centre Hospitalier Universitaire de Dijon, Dijon, France.

Iria Neri (I)

Dermatology, Department of Experimental, Diagnostic, and Specialty Medicine, Sant'Orsola-Malpighi Hospital, University of Bologna, Bologna, Italy.

Céline Phan (C)

Dermatology Department, Hôpital Victor Dupouy, Argenteuil, France.

Emmanuel Mahé (E)

Dermatology Department, Hôpital Victor Dupouy, Argenteuil, France. emmanuel.mahe@ch-argenteuil.fr.

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