Case Report: X-Linked SASH3 Deficiency Presenting as a Common Variable Immunodeficiency.

SASH3 deficiency combined immunodeficiency common variable immunodeficiency genetics inborn errors of immunity mutation primary immunodeficiencies

Journal

Frontiers in immunology
ISSN: 1664-3224
Titre abrégé: Front Immunol
Pays: Switzerland
ID NLM: 101560960

Informations de publication

Date de publication:
2022
Historique:
received: 22 02 2022
accepted: 16 03 2022
entrez: 25 4 2022
pubmed: 26 4 2022
medline: 27 4 2022
Statut: epublish

Résumé

SASH3 is a lymphoid-specific adaptor protein. In a recent study, SASH3 deficiency was described as a novel X-linked combined immunodeficiency with immune dysregulation, associated with impaired TCR signaling and thymocyte survival in humans. The small number of patients reported to date showed recurrent sinopulmonary, cutaneous and mucosal infections, and autoimmune cytopenia. Here we describe an adult patient previously diagnosed with common variable immunodeficiency (CVID) due to low IgG and IgM levels and recurrent upper tract infections. Two separate, severe viral infections drew our attention and pointed to an underlying T cell defect: severe varicella zoster virus (VZV) infection at the age of 4 years and bilateral pneumonia due type A influenza infection at the age of 38. Genetic testing using an NGS-based custom-targeted gene panel revealed a novel hemizygous loss-of-function variant in the

Identifiants

pubmed: 35464398
doi: 10.3389/fimmu.2022.881206
pmc: PMC9027814
doi:

Substances chimiques

Vaccines 0

Types de publication

Case Reports Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

881206

Informations de copyright

Copyright © 2022 Labrador-Horrillo, Franco-Jarava, Garcia-Prat, Parra-Martínez, Antolín, Salgado-Perandrés, Aguiló-Cucurull, Martinez-Gallo and Colobran.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

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Auteurs

Moisés Labrador-Horrillo (M)

Allergy Section, Internal Medicine Department, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Research Institute (VHIR) RETIC ARADyal, Vall d'Hebron Barcelona Hospital, Autonomous University of Barcelona (UAB), Barcelona, Spain.

Clara Franco-Jarava (C)

Immunology Division, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Department of Cell Biology, Physiology and Immunology, Autonomous University of Barcelona (UAB), Bellaterra, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Marina Garcia-Prat (M)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.

Alba Parra-Martínez (A)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.

María Antolín (M)

Department of Clinical and Molecular Genetics, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.

Sandra Salgado-Perandrés (S)

Immunology Division, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Aina Aguiló-Cucurull (A)

Immunology Division, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Mónica Martinez-Gallo (M)

Immunology Division, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Department of Cell Biology, Physiology and Immunology, Autonomous University of Barcelona (UAB), Bellaterra, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Roger Colobran (R)

Immunology Division, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.
Department of Cell Biology, Physiology and Immunology, Autonomous University of Barcelona (UAB), Bellaterra, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.
Department of Clinical and Molecular Genetics, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital, Barcelona, Spain.

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