Fibroblast growth factor receptor 4 promotes glioblastoma progression: a central role of integrin-mediated cell invasiveness.


Journal

Acta neuropathologica communications
ISSN: 2051-5960
Titre abrégé: Acta Neuropathol Commun
Pays: England
ID NLM: 101610673

Informations de publication

Date de publication:
28 04 2022
Historique:
received: 16 02 2022
accepted: 08 04 2022
entrez: 28 4 2022
pubmed: 29 4 2022
medline: 3 5 2022
Statut: epublish

Résumé

Glioblastoma (GBM) is characterized by a particularly invasive phenotype, supported by oncogenic signals from the fibroblast growth factor (FGF)/ FGF receptor (FGFR) network. However, a possible role of FGFR4 remained elusive so far. Several transcriptomic glioma datasets were analyzed. An extended panel of primary surgical specimen-derived and immortalized GBM (stem)cell models and original tumor tissues were screened for FGFR4 expression. GBM models engineered for wild-type and dominant-negative FGFR4 overexpression were investigated regarding aggressiveness and xenograft formation. Gene set enrichment analyses of FGFR4-modulated GBM models were compared to patient-derived datasets. Despite widely absent in adult brain, FGFR4 mRNA was distinctly expressed in embryonic neural stem cells and significantly upregulated in glioblastoma. Pronounced FGFR4 overexpression defined a distinct GBM patient subgroup with dismal prognosis. Expression levels of FGFR4 and its specific ligands FGF19/FGF23 correlated both in vitro and in vivo and were progressively upregulated in the vast majority of recurrent tumors. Based on overexpression/blockade experiments in respective GBM models, a central pro-oncogenic function of FGFR4 concerning viability, adhesion, migration, and clonogenicity was identified. Expression of dominant-negative FGFR4 resulted in diminished (subcutaneous) or blocked (orthotopic) GBM xenograft formation in the mouse and reduced invasiveness in zebrafish xenotransplantation models. In vitro and in vivo data consistently revealed distinct FGFR4 and integrin/extracellular matrix interactions. Accordingly, FGFR4 blockade profoundly sensitized FGFR4-overexpressing GBM models towards integrin/focal adhesion kinase inhibitors. Collectively, FGFR4 overexpression contributes to the malignant phenotype of a highly aggressive GBM subgroup and is associated with integrin-related therapeutic vulnerabilities.

Identifiants

pubmed: 35484633
doi: 10.1186/s40478-022-01363-2
pii: 10.1186/s40478-022-01363-2
pmc: PMC9052585
doi:

Substances chimiques

Integrins 0
Zebrafish Proteins 0
Receptor, Fibroblast Growth Factor, Type 4 EC 2.7.10.1
fgfr4 protein, zebrafish EC 2.7.10.1

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

65

Informations de copyright

© 2022. The Author(s).

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Auteurs

Lisa Gabler (L)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.
Department of Neurosurgery, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Carola Nadine Jaunecker (CN)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.

Sonja Katz (S)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.

Sushilla van Schoonhoven (S)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.

Bernhard Englinger (B)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.
Department of Pediatric Oncology, Dana-Farber Boston Children's Cancer and Blood Disorders Center, Boston, MA, 02215, USA.
Broad Institute of Harvard and MIT, Cambridge, MA, 02142, USA.

Christine Pirker (C)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.

Thomas Mohr (T)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.

Petra Vician (P)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.

Mirjana Stojanovic (M)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.

Valentin Woitzuck (V)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.

Anna Laemmerer (A)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.
Department of Pediatrics and Adolescent Medicine and Comprehensive Center for Pediatrics, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Dominik Kirchhofer (D)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.
Department of Pediatrics and Adolescent Medicine and Comprehensive Center for Pediatrics, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Lisa Mayr (L)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Department of Pediatrics and Adolescent Medicine and Comprehensive Center for Pediatrics, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Mery LaFranca (M)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.
Department of Biological, Chemical and Pharmaceutical Sciences and Technologies, (STEBICEF), University of Palermo, via Archirafi 32, 90123, Palermo, Italy.

Friedrich Erhart (F)

Department of Neurosurgery, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.
St. Anna Children's Cancer Research Institute, Vienna, Austria.

Sarah Grissenberger (S)

St. Anna Children's Cancer Research Institute, Vienna, Austria.

Andrea Wenninger-Weinzierl (A)

St. Anna Children's Cancer Research Institute, Vienna, Austria.

Caterina Sturtzel (C)

St. Anna Children's Cancer Research Institute, Vienna, Austria.

Barbara Kiesel (B)

Department of Neurosurgery, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Alexandra Lang (A)

Department of Neurosurgery, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Brigitte Marian (B)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.

Bettina Grasl-Kraupp (B)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.

Martin Distel (M)

St. Anna Children's Cancer Research Institute, Vienna, Austria.

Julia Schüler (J)

Charles River Discovery Research Services Germany GmbH, Freiburg, Germany.

Johannes Gojo (J)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Department of Pediatrics and Adolescent Medicine and Comprehensive Center for Pediatrics, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Michael Grusch (M)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.

Sabine Spiegl-Kreinecker (S)

Department of Neurosurgery, Kepler University Hospital GmbH, Johannes Kepler University Linz, Wagner-Jauregg-Weg 15, 4020, Linz and Altenberger Strasse 69, 4020, Linz, Austria.

Daniel J Donoghue (DJ)

Department of Chemistry and Biochemistry, Moores UCSD Cancer Center, University of California San Diego, La Jolla, CA, 92093-0367, USA.

Daniela Lötsch (D)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria.
Department of Neurosurgery, Medical University of Vienna, Waehringer Guertel 18-20, 1090, Vienna, Austria.

Walter Berger (W)

Center for Cancer Research, Medical University of Vienna, Borschkegasse 8A, 1090, Vienna, Austria. walter.berger@meduniwien.ac.at.
Comprehensive Cancer Center-Central Nervous System Tumor Unit, Medical University of Vienna, Spitalgasse 23, 1090, Vienna, Austria. walter.berger@meduniwien.ac.at.

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