Cysteine metabolic engineering and selective disulfide reduction produce superior antibody-drug-conjugates.


Journal

Scientific reports
ISSN: 2045-2322
Titre abrégé: Sci Rep
Pays: England
ID NLM: 101563288

Informations de publication

Date de publication:
04 05 2022
Historique:
received: 19 10 2021
accepted: 18 04 2022
entrez: 4 5 2022
pubmed: 5 5 2022
medline: 7 5 2022
Statut: epublish

Résumé

Next-generation site-specific cysteine-based antibody-drug-conjugates (ADCs) broaden therapeutic index by precise drug-antibody attachments. However, manufacturing such ADCs for clinical validation requires complex full reduction and reoxidation processes, impacting product quality. To overcome this technical challenge, we developed a novel antibody manufacturing process through cysteine (Cys) metabolic engineering in Chinese hamster ovary cells implementing a unique cysteine-capping technology. This development enabled a direct conjugation of drugs after chemoselective-reduction with mild reductant tris(3-sulfonatophenyl)phosphine. This innovative platform produces clinical ADC products with superior quality through a simplified manufacturing process. This technology also has the potential to integrate Cys-based site-specific conjugation with other site-specific conjugation methodologies to develop multi-drug ADCs and exploit multi-mechanisms of action for effective cancer treatments.

Identifiants

pubmed: 35508689
doi: 10.1038/s41598-022-11344-z
pii: 10.1038/s41598-022-11344-z
pmc: PMC9068625
doi:

Substances chimiques

Antibodies 0
Antineoplastic Agents 0
Disulfides 0
Immunoconjugates 0
Cysteine K848JZ4886

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

7262

Informations de copyright

© 2022. The Author(s).

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Auteurs

Renée Procopio-Melino (R)

BioProcess R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 1 Burtt Road, Andover, MA, 01810, USA.

Frank W Kotch (FW)

BioProcess R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 875 Chesterfield Parkway West, Chesterfield, MO, 63017, USA. Frank.W.Kotch@pfizer.com.

Amar S Prashad (AS)

BioProcess R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 875 Chesterfield Parkway West, Chesterfield, MO, 63017, USA.
Pearl River Laboratories Inc, 401 North Middletown Road, Pearl River, NY, 10965, USA.

Jose M Gomes (JM)

BioProcess R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 1 Burtt Road, Andover, MA, 01810, USA. Jose.Gomes@pfizer.com.

Wenge Wang (W)

BioProcess R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 1 Burtt Road, Andover, MA, 01810, USA.

Bo Arve (B)

BioProcess R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 875 Chesterfield Parkway West, Chesterfield, MO, 63017, USA.

Andrew Dawdy (A)

Analytical R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 875 Chesterfield Parkway West, Chesterfield, MO, 63017, USA. Andrew.W.Dawdy@pfizer.com.

Lawrence Chen (L)

Analytical R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 1 Burtt Road, Andover, MA, 01810, USA.

Justin Sperry (J)

Analytical R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 875 Chesterfield Parkway West, Chesterfield, MO, 63017, USA.

Christine Hosselet (C)

Vaccine Research, Pfizer Worldwide R&D, 401 North Middletown Road, Pearl River, NY, 10965, USA.

Tao He (T)

BioMedicine Design, Medicinal Sciences, Pfizer Worldwide R&D, 610 Main Street, Cambridge, MA, 02139, USA.
JOINN Biologics US Inc., 2600 Hilltop Dr., Richmond, CA, 94806, USA.

Ronald Kriz (R)

BioMedicine Design, Medicinal Sciences, Pfizer Worldwide R&D, 610 Main Street, Cambridge, MA, 02139, USA.

Laura Lin (L)

BioMedicine Design, Medicinal Sciences, Pfizer Worldwide R&D, 610 Main Street, Cambridge, MA, 02139, USA.

Kimberly Marquette (K)

BioMedicine Design, Medicinal Sciences, Pfizer Worldwide R&D, 610 Main Street, Cambridge, MA, 02139, USA.

Lioudmila Tchistiakova (L)

BioMedicine Design, Medicinal Sciences, Pfizer Worldwide R&D, 610 Main Street, Cambridge, MA, 02139, USA.

Will Somers (W)

BioMedicine Design, Medicinal Sciences, Pfizer Worldwide R&D, 610 Main Street, Cambridge, MA, 02139, USA.

Jason C Rouse (JC)

Analytical R&D, Biotherapeutics Pharmaceutical Sciences, Medicinal Sciences, Pfizer Worldwide R&D, 1 Burtt Road, Andover, MA, 01810, USA.

Xiaotian Zhong (X)

BioMedicine Design, Medicinal Sciences, Pfizer Worldwide R&D, 610 Main Street, Cambridge, MA, 02139, USA. Xiaotian.Zhong@pfizer.com.

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Classifications MeSH