Regulatory Programs of B-cell Activation and Germinal Center Reaction Allow B-ALL Escape from CD19 CAR T-cell Therapy.


Journal

Cancer immunology research
ISSN: 2326-6074
Titre abrégé: Cancer Immunol Res
Pays: United States
ID NLM: 101614637

Informations de publication

Date de publication:
01 09 2022
Historique:
received: 05 08 2021
revised: 13 04 2022
accepted: 23 06 2022
pubmed: 28 6 2022
medline: 9 9 2022
entrez: 27 6 2022
Statut: ppublish

Résumé

Chimeric antigen receptor (CAR) T-cell therapy has led to tremendous successes in the treatment of B-cell malignancies. However, a large fraction of treated patients relapse, often with disease expressing reduced levels of the target antigen. Here, we report that exposing CD19+ B-cell acute lymphoblastic leukemia (B-ALL) cells to CD19 CAR T cells reduced CD19 expression within hours. Initially, CD19 CAR T cells caused clustering of CD19 at the T cell-leukemia cell interface followed by CD19 internalization and decreased CD19 surface expression on the B-ALL cells. CD19 expression was then repressed by transcriptional rewiring. Using single-cell RNA sequencing and single-cell assay for transposase-accessible chromatin using sequencing, we demonstrated that a subset of refractory CD19low cells sustained decreased CD19 expression through transcriptional programs of physiologic B-cell activation and germinal center reaction. Inhibiting B-cell activation programs with the Bruton's tyrosine kinase inhibitor ibrutinib increased the cytotoxicity of CD19 CAR T cells without affecting CAR T-cell viability. These results demonstrate transcriptional plasticity as an underlying mechanism of escape from CAR T cells and highlight the importance of combining CAR T-cell therapy with targeted therapies that aim to overcome this plasticity. See related Spotlight by Zhao and Melenhorst, p. 1040.

Identifiants

pubmed: 35759797
pii: 705260
doi: 10.1158/2326-6066.CIR-21-0626
pmc: PMC9444959
mid: NIHMS1820964
doi:

Substances chimiques

Antigens, CD19 0
Receptors, Antigen, T-Cell 0

Types de publication

Editorial Research Support, Non-U.S. Gov't Research Support, N.I.H., Extramural

Langues

eng

Sous-ensembles de citation

IM

Pagination

1055-1068

Subventions

Organisme : NCI NIH HHS
ID : K08 CA191026
Pays : United States
Organisme : NCI NIH HHS
ID : K08 CA191091
Pays : United States

Commentaires et corrections

Type : CommentIn

Informations de copyright

©2022 American Association for Cancer Research.

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Auteurs

Nam Gyu Im (NG)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.
Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.
Institute for Translational Epigenetics, Faculty of Medicine and University Hospital Cologne, University of Cologne, Cologne, Germany.
Center for Molecular Medicine Cologne, Faculty of Medicine and University Hospital Cologne, Cologne, Germany.

Amy Guillaumet-Adkins (A)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.
Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.

Megha Wal (M)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.
Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.

Anna J Rogers (AJ)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Julia Frede (J)

Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.
Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Claire C Havig (CC)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Jing Yang (J)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.
Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.

Praveen Anand (P)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.
Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.
Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Sarah K Stegmann (SK)

Harvard Medical School, Boston, Massachusetts.

Johannes M Waldschmidt (JM)

Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.
Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Noori Sotudeh (N)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.
Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.

Leili Niu (L)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Jordan Voisine (J)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Michal R Schweiger (MR)

Institute for Translational Epigenetics, Faculty of Medicine and University Hospital Cologne, University of Cologne, Cologne, Germany.
Center for Molecular Medicine Cologne, Faculty of Medicine and University Hospital Cologne, Cologne, Germany.

Clemens Grassberger (C)

Department of Radiation Oncology, Massachusetts General Hospital and Harvard Medical School, Boston, Massachusetts.

Jens G Lohr (JG)

Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.
Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

Birgit Knoechel (B)

Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.
Harvard Medical School, Boston, Massachusetts.
Broad Institute of MIT and Harvard, Cambridge, Massachusetts.
Division of Hematology/Oncology, Department of Medicine, Boston Children's Hospital, Boston, Massachusetts.

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