Iterative computational design and crystallographic screening identifies potent inhibitors targeting the Nsp3 Macrodomain of SARS-CoV-2.

Nsp3 macrodomain coronavirus fragment-based drug discovery virtual screening

Journal

bioRxiv : the preprint server for biology
Titre abrégé: bioRxiv
Pays: United States
ID NLM: 101680187

Informations de publication

Date de publication:
28 Jul 2022
Historique:
pubmed: 8 7 2022
medline: 8 7 2022
entrez: 7 7 2022
Statut: epublish

Résumé

The nonstructural protein 3 (NSP3) of the severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) contains a conserved macrodomain enzyme (Mac1) that is critical for pathogenesis and lethality. While small molecule inhibitors of Mac1 have great therapeutic potential, at the outset of the COVID-19 pandemic there were no well-validated inhibitors for this protein nor, indeed, the macrodomain enzyme family, making this target a pharmacological orphan. Here, we report the structure-based discovery and development of several different chemical scaffolds exhibiting low- to sub-micromolar affinity for Mac1 through iterations of computer-aided design, structural characterization by ultra-high resolution protein crystallography, and binding evaluation. Potent scaffolds were designed with

Identifiants

pubmed: 35794891
doi: 10.1101/2022.06.27.497816
pmc: PMC9258288
pii:
doi:

Types de publication

Preprint

Langues

eng

Commentaires et corrections

Type : UpdateIn

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Auteurs

Stefan Gahbauer (S)

Department of Pharmaceutical Chemistry, University of California San Francisco, San Francisco, CA 94158, USA.

Galen J Correy (GJ)

Department of Bioengineering and Therapeutic Sciences, University of California San Francisco, San Francisco, CA 94158, USA.

Marion Schuller (M)

Sir William Dunn School of Pathology, University of Oxford, South Parks Road, Oxford, OX1 3RE, UK.

Matteo P Ferla (MP)

Wellcome Centre for Human Genetics, University of Oxford, Old Road Campus, Oxford OX3 7BN, UK.
National Institute for Health Research Oxford Biomedical Research Centre, Oxford, OX4 2PG, UK.

Yagmur Umay Doruk (YU)

Helen Diller Family Comprehensive Cancer Center, University of California San Francisco, San Francisco, CA 94158, USA.

Moira Rachman (M)

Department of Pharmaceutical Chemistry, University of California San Francisco, San Francisco, CA 94158, USA.

Taiasean Wu (T)

Institute for Neurodegenerative Disease, University of California San Francisco, San Francisco, CA 94158, USA.
Chemistry and Chemical Biology Graduate Program, University of California San Francisco, San Francisco, CA 94158, USA.

Morgan Diolaiti (M)

Helen Diller Family Comprehensive Cancer Center, University of California San Francisco, San Francisco, CA 94158, USA.

Siyi Wang (S)

Chemistry and Chemical Biology Graduate Program, University of California San Francisco, San Francisco, CA 94158, USA.

R Jeffrey Neitz (RJ)

Department of Pharmaceutical Chemistry and Small Molecule Discovery Center, University of California, San Francisco, California 94158, USA.

Daren Fearon (D)

Diamond Light Source Ltd., Harwell Science and Innovation Campus, Didcot, OX11 0DE, UK.
Research Complex at Harwell, Harwell Science and Innovation Campus, Didcot OX11 0FA, UK.

Dmytro Radchenko (D)

Enamine Ltd., Chervonotkatska Street 78, Kyiv 02094, Ukraine.
Taras Shevchenko National University of Kyiv, Volodymyrska Street 60, Kyiv, 01601, Ukraine.

Yurii Moroz (Y)

Taras Shevchenko National University of Kyiv, Volodymyrska Street 60, Kyiv, 01601, Ukraine.
Chemspace, Chervonotkatska Street 78, Kyiv, 02094, Ukraine.

John J Irwin (JJ)

Department of Pharmaceutical Chemistry, University of California San Francisco, San Francisco, CA 94158, USA.

Adam R Renslo (AR)

Helen Diller Family Comprehensive Cancer Center, University of California San Francisco, San Francisco, CA 94158, USA.
Department of Pharmaceutical Chemistry and Small Molecule Discovery Center, University of California, San Francisco, California 94158, USA.

Jenny C Taylor (JC)

Wellcome Centre for Human Genetics, University of Oxford, Old Road Campus, Oxford OX3 7BN, UK.
National Institute for Health Research Oxford Biomedical Research Centre, Oxford, OX4 2PG, UK.

Jason E Gestwicki (JE)

Institute for Neurodegenerative Disease, University of California San Francisco, San Francisco, CA 94158, USA.
Department of Pharmaceutical Chemistry and Small Molecule Discovery Center, University of California, San Francisco, California 94158, USA.

Frank von Delft (F)

Diamond Light Source Ltd., Harwell Science and Innovation Campus, Didcot, OX11 0DE, UK.
Research Complex at Harwell, Harwell Science and Innovation Campus, Didcot OX11 0FA, UK.
Centre for Medicines Discovery, University of Oxford, South Parks Road, Headington, OX3 7DQ, UK.
Structural Genomics Consortium, University of Oxford, Old Road Campus, Roosevelt Drive, Headington OX3 7DQ, UK.
Department of Biochemistry, University of Johannesburg, Auckland Park 2006, South Africa.

Alan Ashworth (A)

Helen Diller Family Comprehensive Cancer Center, University of California San Francisco, San Francisco, CA 94158, USA.

Ivan Ahel (I)

Sir William Dunn School of Pathology, University of Oxford, South Parks Road, Oxford, OX1 3RE, UK.

Brian K Shoichet (BK)

Department of Pharmaceutical Chemistry, University of California San Francisco, San Francisco, CA 94158, USA.

James S Fraser (JS)

Department of Bioengineering and Therapeutic Sciences, University of California San Francisco, San Francisco, CA 94158, USA.

Classifications MeSH