Primary ovarian insufficiency in RMND1 mitochondrial disease.


Journal

Mitochondrion
ISSN: 1872-8278
Titre abrégé: Mitochondrion
Pays: Netherlands
ID NLM: 100968751

Informations de publication

Date de publication:
09 2022
Historique:
received: 17 02 2022
revised: 28 06 2022
accepted: 14 07 2022
pubmed: 29 7 2022
medline: 28 9 2022
entrez: 28 7 2022
Statut: ppublish

Résumé

RMND1 (Required for Meiotic Nuclear Division 1 homolog) is a nuclear encoded mitochondrial protein. Biallelic variants inRMND1are described in patients with white matter encephalopathy, hearing loss and renal dysfunction. In addition to this phenotype, two independent families (3 patients) have been reported with ovarian failure. We report on a 17-year-old girl with RMND1 related mitochondrial disorder including white matter encephalopathy, hearing loss and renal insufficiency who presented primary ovarian insufficiency in whom a homozygous variant c.713 A > G (p.Asn238Ser) in the RMND1 gene was found. We report the fourth patient with RMND1 biallelic pathogenic variants and primary ovarian insufficiency.

Identifiants

pubmed: 35901949
pii: S1567-7249(22)00060-5
doi: 10.1016/j.mito.2022.07.004
pii:
doi:

Substances chimiques

Cell Cycle Proteins 0
Mitochondrial Proteins 0
RMND1 protein, human 0

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

51-53

Informations de copyright

Copyright © 2022 Elsevier B.V. and Mitochondria Research Society. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of Competing Interest The authors declare that they have no known competing financial interests or personal relationships that could have appeared to influence the work reported in this paper.

Auteurs

E Boros (E)

Paediatric Endocrinology, Hôpital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium.

F Elilié Mawa Ongoth (F)

Paediatric Endocrinology, Hôpital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium.

C Heinrichs (C)

Paediatric Endocrinology, Hôpital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium.

A L Mansbach (AL)

Paediatric Ear Nose and Throat Department, Hôpital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium.

S Seneca (S)

Center for Medical Genetics/Research Center Reproduction and Genetics, Universitair Ziekenhuis Brussel, Vrije Universiteit Brussel (VUB), Belgium.

A Aeby (A)

Paediatric Neurology, Hôpital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium.

K Ismaïli (K)

Paediatric Nephrology, Hôpital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium.

C Brachet (C)

Paediatric Endocrinology, Hôpital Universitaire des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium. Electronic address: Cecile.BRACHET@huderf.be.

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Classifications MeSH