Methylphenidate Analogues as a New Class of Potential Disease-Modifying Agents for Parkinson's Disease: Evidence from Cell Models and Alpha-Synuclein Transgenic Mice.

Parkinson’s disease methylphenidate analogues motor recovery effect threo methyl 2-(piperidin-2-yl)-2-(p-tolyl)acetate hydrochloride α-synuclein/synapsin III complex

Journal

Pharmaceutics
ISSN: 1999-4923
Titre abrégé: Pharmaceutics
Pays: Switzerland
ID NLM: 101534003

Informations de publication

Date de publication:
30 Jul 2022
Historique:
received: 17 05 2022
revised: 20 07 2022
accepted: 26 07 2022
entrez: 26 8 2022
pubmed: 27 8 2022
medline: 27 8 2022
Statut: epublish

Résumé

Parkinson's disease (PD) is characterized by dopaminergic nigrostriatal neurons degeneration and Lewy body pathology, mainly composed of α-synuclein (αSyn) fibrillary aggregates. We recently described that the neuronal phosphoprotein Synapsin III (Syn III) participates in αSyn pathology in PD brains and is a permissive factor for αSyn aggregation. Moreover, we reported that the gene silencing of Syn III in a human αSyn transgenic (tg) mouse model of PD at a pathological stage, manifesting marked insoluble αSyn deposits and dopaminergic striatal synaptic dysfunction, could reduce αSyn aggregates, restore synaptic functions and motor activities and exert neuroprotective effects. Interestingly, we also described that the monoamine reuptake inhibitor methylphenidate (MPH) can recover the motor activity of human αSyn tg mice through a dopamine (DA) transporter-independent mechanism, which relies on the re-establishment of the functional interaction between Syn III and α-helical αSyn. These findings support that the pathological αSyn/Syn III interaction may constitute a therapeutic target for PD. Here, we studied MPH and some of its analogues as modulators of the pathological αSyn/Syn III interaction. We identified 4-methyl derivative

Identifiants

pubmed: 36015221
pii: pharmaceutics14081595
doi: 10.3390/pharmaceutics14081595
pmc: PMC9414221
pii:
doi:

Types de publication

Journal Article

Langues

eng

Références

Int J Mol Sci. 2018 May 30;19(6):
pubmed: 29848975
Bioorg Med Chem Lett. 2004 Apr 5;14(7):1799-802
pubmed: 15026075
Mol Ther. 2022 Apr 6;30(4):1465-1483
pubmed: 35038583
J Neurosci. 2007 Feb 7;27(6):1405-10
pubmed: 17287515
Neuropharmacology. 2018 May 15;134(Pt A):133-140
pubmed: 28823611
Methods. 2001 Jul;24(3):289-96
pubmed: 11403577
Molecules. 2012 Apr 02;17(4):4047-132
pubmed: 22469598
Acta Neuropathol. 2010 Aug;120(2):131-43
pubmed: 20563819
J Am Chem Soc. 2010 Jun 30;132(25):8657-68
pubmed: 20524659
J Chem Inf Model. 2019 Aug 26;59(8):3485-3493
pubmed: 31322877
J Neurosci. 2010 Jul 21;30(29):9762-70
pubmed: 20660258
J Neurosci. 2006 Apr 12;26(15):3942-50
pubmed: 16611810
Mov Disord. 2012 Feb;27(2):312-5
pubmed: 22102531
Methods. 2014 Mar 15;66(2):131-8
pubmed: 23811334
Int J Mol Sci. 2019 Jan 02;20(1):
pubmed: 30609739
Sensors (Basel). 2016 Sep 14;16(9):
pubmed: 27649177
J Pharmacol Exp Ther. 2002 May;301(2):527-35
pubmed: 11961053
Org Lett. 2013 Feb 15;15(4):824-7
pubmed: 23379760
J Comput Chem. 2004 Oct;25(13):1605-12
pubmed: 15264254
Nat Protoc. 2020 May;15(5):1829-1852
pubmed: 32269383
J Med Chem. 1996 Mar 15;39(6):1201-9
pubmed: 8632426
Neurochem Int. 2015 Jun-Jul;85-86:14-23
pubmed: 25846226
DNA Cell Biol. 2013 Aug;32(8):430-4
pubmed: 23768104
PLoS One. 2011;6(12):e27959
pubmed: 22163275
Front Aging Neurosci. 2017 Oct 10;9:330
pubmed: 29066967
Cell Tissue Res. 2018 Jul;373(1):137-148
pubmed: 29119326
J Neurochem. 2008 Jul;106(2):560-77
pubmed: 18410503
Acta Neuropathol. 2018 Oct;136(4):621-639
pubmed: 30046897
Nucleic Acids Res. 2014 Apr;42(7):e55
pubmed: 24476917
Org Lett. 2021 Oct 15;23(20):7894-7899
pubmed: 34585940
Neurobiol Dis. 2020 May;138:104789
pubmed: 32032728
Nucleic Acids Res. 2017 Jul 3;45(W1):W365-W373
pubmed: 28521030
Brain. 2010 Jul;133(Pt 7):2032-44
pubmed: 20534649
J Parkinsons Dis. 2017;7(s1):S51-S69
pubmed: 28282814
Sci Rep. 2017 Mar 03;7:42717
pubmed: 28256516
Proteins. 2008 Aug;72(2):557-79
pubmed: 18247354
ChemMedChem. 2020 Jul 20;15(14):1330-1337
pubmed: 32452650
Eur J Med Chem. 2001 Apr;36(4):303-11
pubmed: 11461755
Proc Natl Acad Sci U S A. 2016 Feb 16;113(7):E912-21
pubmed: 26839406
J Chem Inf Model. 2017 Jul 24;57(7):1511-1516
pubmed: 28594549
J Comput Chem. 2010 Jan 30;31(2):455-61
pubmed: 19499576
Trends Neurosci. 2015 Mar;38(3):178-88
pubmed: 25639775
Bioorg Med Chem Lett. 2008 May 1;18(9):2860-4
pubmed: 18420409
Atten Defic Hyperact Disord. 2019 Mar;11(1):107-111
pubmed: 30927235
J Med Chem. 1998 Feb 12;41(4):591-601
pubmed: 9484508
Proteins. 2017 Mar;85(3):497-512
pubmed: 28026062
RSC Med Chem. 2021 Jun 9;12(7):1174-1186
pubmed: 34355183
Neuropathol Appl Neurobiol. 2016 Feb;42(1):77-94
pubmed: 26613567
Bioorg Med Chem. 2010 Oct 15;18(20):7221-38
pubmed: 20846865
Lancet Neurol. 2012 Jul;11(7):589-96
pubmed: 22658702
ChemMedChem. 2016 Jun 6;11(11):1117-21
pubmed: 27218427
Brain Pathol. 2018 Nov;28(6):875-888
pubmed: 29330884
J Neurochem. 1999 Dec;73(6):2266-71
pubmed: 10582583
ACS Chem Neurosci. 2020 Oct 21;11(20):3288-3300
pubmed: 32926777
J Pharmacol Exp Ther. 2012 May;341(2):484-92
pubmed: 22344407
Parkinsonism Relat Disord. 2018 Jun;51:49-54
pubmed: 29523394
Bioinformatics. 2017 Oct 01;33(19):3036-3042
pubmed: 28575181
J Cell Sci. 2015 Jul 1;128(13):2231-43
pubmed: 25967550
Neuropsychiatr Dis Treat. 2016 May 10;12:1141-9
pubmed: 27274248

Auteurs

Andrea Casiraghi (A)

Department of Pharmaceutical Sciences, University of Milan, Via Luigi Mangiagalli 25, 20133 Milano, Italy.

Francesca Longhena (F)

Department of Molecular and Translational Medicine, University of Brescia, Viale Europa 11, 25123 Brescia, Italy.

Gaia Faustini (G)

Department of Molecular and Translational Medicine, University of Brescia, Viale Europa 11, 25123 Brescia, Italy.

Giovanni Ribaudo (G)

Department of Molecular and Translational Medicine, University of Brescia, Viale Europa 11, 25123 Brescia, Italy.

Lorenzo Suigo (L)

Department of Pharmaceutical Sciences, University of Milan, Via Luigi Mangiagalli 25, 20133 Milano, Italy.

Gisela Andrea Camacho-Hernandez (GA)

Medicinal Chemistry Section, Molecular Targets and Medications Discovery Branch, NIDA-IRP, 333 Cassell Drive, Baltimore, MD 21224, USA.

Federica Bono (F)

Department of Molecular and Translational Medicine, University of Brescia, Viale Europa 11, 25123 Brescia, Italy.

Viviana Brembati (V)

Department of Molecular and Translational Medicine, University of Brescia, Viale Europa 11, 25123 Brescia, Italy.

Amy Hauck Newman (AH)

Medicinal Chemistry Section, Molecular Targets and Medications Discovery Branch, NIDA-IRP, 333 Cassell Drive, Baltimore, MD 21224, USA.

Alessandra Gianoncelli (A)

Department of Molecular and Translational Medicine, University of Brescia, Viale Europa 11, 25123 Brescia, Italy.

Valentina Straniero (V)

Department of Pharmaceutical Sciences, University of Milan, Via Luigi Mangiagalli 25, 20133 Milano, Italy.

Arianna Bellucci (A)

Department of Molecular and Translational Medicine, University of Brescia, Viale Europa 11, 25123 Brescia, Italy.

Ermanno Valoti (E)

Department of Pharmaceutical Sciences, University of Milan, Via Luigi Mangiagalli 25, 20133 Milano, Italy.

Classifications MeSH