Safety Profile and Lack of Immunogenicity of IncobotulinumtoxinA in Pediatric Spasticity and Sialorrhea: A Pooled Analysis.


Journal

Toxins
ISSN: 2072-6651
Titre abrégé: Toxins (Basel)
Pays: Switzerland
ID NLM: 101530765

Informations de publication

Date de publication:
25 08 2022
Historique:
received: 12 07 2022
revised: 16 08 2022
accepted: 19 08 2022
entrez: 22 9 2022
pubmed: 23 9 2022
medline: 28 9 2022
Statut: epublish

Résumé

IncobotulinumtoxinA, a pure botulinumtoxinA formulation, is free of accessory proteins. This analysis provides pooled safety data from phase 3 trials of children/adolescents (2-17 years), investigating incobotulinumtoxinA for the treatment of spasticity associated with cerebral palsy (at doses ≤20 U/kg (max. 500 U) per injection cycle (IC) for ≤6 ICs; three trials) or sialorrhea associated with neurologic disorders (at total doses of 20-75 U per IC for ≤4 ICs; one trial) for ≤96 weeks. Safety endpoints included the incidences of different types of treatment-emergent adverse events (TEAEs) and immunogenicity. IncobotulinumtoxinA dose groups were combined. Of 1159 patients (mean age 7.3 years, 60.4% males) treated with incobotulinumtoxinA, 3.9% experienced treatment-related TEAEs, with the most common being injection site reactions (1.3%) (both indications), muscular weakness (0.7%) (spasticity), and dysphagia (0.2%) (sialorrhea). Two patients (0.2%) experienced a treatment-related treatment-emergent serious adverse event, and 0.3% discontinued the study due to treatment-related TEAEs. No botulinumtoxinA-naïve patients developed neutralizing antibodies (NAbs) after incobotulinumtoxinA. All children/adolescents with known pre-treatment status and testing positive for Nabs at final visit (

Identifiants

pubmed: 36136523
pii: toxins14090585
doi: 10.3390/toxins14090585
pmc: PMC9505819
pii:
doi:

Substances chimiques

Antibodies, Neutralizing 0
Neuromuscular Agents 0
Botulinum Toxins, Type A EC 3.4.24.69
incobotulinumtoxinA EC 3.4.24.69

Banques de données

ClinicalTrials.gov
['NCT01893411', 'NCT01905683', 'NCT02002884', 'NCT02270736']
EudraCT
['2012-005054-30', '2012-005055-17', '2012-005496-14', '2013-004532-30']

Types de publication

Journal Article Meta-Analysis Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Références

Plast Reconstr Surg Glob Open. 2020 Jan 24;8(1):e2627
pubmed: 32095419
J Neuroimmunol. 2017 May 15;306:31-39
pubmed: 28385185
Neurol Neurochir Pol. 2021;55(2):133-140
pubmed: 33797747
Int Urol Nephrol. 2019 Aug;51(8):1321-1327
pubmed: 31183660
Toxins (Basel). 2020 Jul 06;12(7):
pubmed: 32640636
Dev Med Child Neurol. 2022 Feb;64(2):259-265
pubmed: 34423432
J Drugs Dermatol. 2019 Jan 01;18(1):52-57
pubmed: 30681794
BioDrugs. 2012 Apr 1;26(2):e1-9
pubmed: 22385408
J Neurol Neurosurg Psychiatry. 2013 Sep;84(9):1014-9
pubmed: 23687362
Neurology. 2019 Jan 1;92(1):e48-e54
pubmed: 30464031
Pediatrics. 2001 Nov;108(5):1062-71
pubmed: 11694682
Practitioner. 1964 Apr;192:540-2
pubmed: 14143329
Curr Opin Ophthalmol. 2017 Sep;28(5):460-464
pubmed: 28650877
Arch Pediatr Adolesc Med. 2000 Dec;154(12):1214-8
pubmed: 11115305
J Child Neurol. 2017 Nov;32(13):1058-1064
pubmed: 28914131
Ital J Pediatr. 2022 Jul 19;48(1):118
pubmed: 35854335
Toxins (Basel). 2020 Aug 04;12(8):
pubmed: 32759685
Dermatol Surg. 2017 Dec;43 Suppl 3:S293-S303
pubmed: 33065955
Neurology. 2017 Apr 04;88(14):1321-1328
pubmed: 28283596
Pediatr Neurol. 2021 Oct;123:10-20
pubmed: 34339951
Eur J Paediatr Neurol. 2010 Jan;14(1):45-66
pubmed: 19914110
Neuropediatrics. 2020 Feb;51(1):1-5
pubmed: 31486052
Drugs R D. 2015 Mar;15(1):1-9
pubmed: 25559581
Neurology. 2021 Aug 2;:
pubmed: 34341153
NeuroRehabilitation. 2022;50(1):33-46
pubmed: 34957954
Dev Med Child Neurol. 2021 May;63(5):592-600
pubmed: 33206382
Adv Ther. 2021 Oct;38(10):5046-5064
pubmed: 34515975
Drugs R D. 2010;10(2):67-73
pubmed: 20698714
Neurology. 2019 Apr 23;92(17):e1982-e1991
pubmed: 30918101
Neurol Neurochir Pol. 2021;55(2):158-164
pubmed: 33861462
J Neurol. 2020 May;267(5):1340-1347
pubmed: 31960136
Aesthet Surg J. 2022 Jan 1;42(1):106-120
pubmed: 33528495
Dev Med Child Neurol. 1997 Apr;39(4):214-23
pubmed: 9183258
Children (Basel). 2021 Nov 25;8(12):
pubmed: 34943284
BMC Neurol. 2020 Apr 8;20(1):126
pubmed: 32268880
J Pediatr Rehabil Med. 2022;15(1):113-127
pubmed: 34957963
J Pediatr Rehabil Med. 2021;14(2):183-197
pubmed: 34092664
Toxins (Basel). 2019 Aug 26;11(9):
pubmed: 31454941

Auteurs

Steffen Berweck (S)

Schön Klinik Vogtareuth, Krankenhausstraße 20, 83569 Vogtareuth, Germany.
Dr. von Hauner Children's Hospital, Munich University, Lindwurmstrasse 4, 80337 Munich, Germany.

Marta Banach (M)

Jagiellonian University Medical College, Świętej Anny 12, 31-008 Krakow, Poland.

Deborah Gaebler-Spira (D)

Shirley Ryan AbilityLab, Northwestern Feinberg School of Medicine, 355 E. Erie St, Chicago, IL 60611, USA.

Henry G Chambers (HG)

Rady Children's Hospital, 3030 Children's Way MC 5062, San Diego, CA 92123, USA.

A S Schroeder (AS)

Division of Paediatric Neurology and Developmental Medicine, LMU Center for Children with Medical Complexity, Dr. von Hauner Children's Hospital, Ludwig Maximilian University of Munich, Lindwurmstrasse 4, 80337 Munich, Germany.

Thorin L Geister (TL)

Merz Therapeutics GmbH, Eckenheimer Landstraße 100, 60318 Frankfurt am Main, Germany.

Michael Althaus (M)

Merz Therapeutics GmbH, Eckenheimer Landstraße 100, 60318 Frankfurt am Main, Germany.

Angelika Hanschmann (A)

Merz Therapeutics GmbH, Eckenheimer Landstraße 100, 60318 Frankfurt am Main, Germany.

Matteo Vacchelli (M)

Merz Therapeutics GmbH, Eckenheimer Landstraße 100, 60318 Frankfurt am Main, Germany.

Michaela V Bonfert (MV)

Division of Paediatric Neurology and Developmental Medicine, LMU Center for Children with Medical Complexity, Dr. von Hauner Children's Hospital, Ludwig Maximilian University of Munich, Lindwurmstrasse 4, 80337 Munich, Germany.

Florian Heinen (F)

Division of Paediatric Neurology and Developmental Medicine, LMU Center for Children with Medical Complexity, Dr. von Hauner Children's Hospital, Ludwig Maximilian University of Munich, Lindwurmstrasse 4, 80337 Munich, Germany.

Edward Dabrowski (E)

Beaumont Pediatric Physical Medicine & Rehabilitation-Royal Oak, 3535 W 13 Mile Rd #307, Royal Oak, MI 48073, USA.

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Classifications MeSH