Hyperthyroidism in McCune-Albright Syndrome - a case report.


Journal

Journal of pediatric endocrinology & metabolism : JPEM
ISSN: 2191-0251
Titre abrégé: J Pediatr Endocrinol Metab
Pays: Germany
ID NLM: 9508900

Informations de publication

Date de publication:
28 Mar 2023
Historique:
received: 14 07 2022
accepted: 24 10 2022
pubmed: 10 11 2022
medline: 8 3 2023
entrez: 9 11 2022
Statut: epublish

Résumé

We intend to describe a case of McCune-Albright Syndrome (MAS), a rare disease characterized by fibrous dysplasia (FD), cutaneous hyperpigmentation and hyperfunctioning endocrinopathies (HFE). We report the case of a 13-year-old male child who presented with a This is a case of MAS-associated HT that reflects the deleterious effect of thyroid hormone excess on FD, reinforcing the need of having a low threshold for suspicion of HFE that may arise.

Identifiants

pubmed: 36351197
pii: jpem-2022-0357
doi: 10.1515/jpem-2022-0357
doi:

Substances chimiques

Hormones 0
Diphosphonates 0

Types de publication

Case Reports

Langues

eng

Sous-ensembles de citation

IM

Pagination

319-322

Informations de copyright

© 2022 Walter de Gruyter GmbH, Berlin/Boston.

Références

Javaid, MK, Boyce, A, Appelman-Dijkstra, N, Ong, J, Defabianis, P, Offiah, A, et al.. Best practice management guidelines for fibrous dysplasia/McCune-Albright Syndrome: a consensus statement from the FD/MAS international consortium. Orphanet J Rare Dis 2019;14. https://doi.org/10.1186/s13023-019-1102-9 .
doi: 10.1186/s13023-019-1102-9
Tessaris, D, Corrias, A, Matarazzo, P, De Sanctis, L, Wasniewska, M, Messina, MF, et al.. Thyroid abnormalities in children and adolescents with McCune-Albright Syndrome. Horm Res Paediatr 2012;78:151–7. https://doi.org/10.1159/000342641 .
doi: 10.1159/000342641
Hartley, I, Zhadina, M, Collins, MT, Boyce, AM. Fibrous dysplasia of bone and McCune-Albright Syndrome: a bench to bedside review. Calcif Tissue Int 2019;104:517–29. https://doi.org/10.1007/s00223-019-00550-z .
doi: 10.1007/s00223-019-00550-z
Spencer, T, Pan, KS, Collins, MT, Boyce, AM. The clinical spectrum of McCune-albright Syndrome and its management. Horm Res Paediatr 2019;92:347–56. https://doi.org/10.1159/000504802 .
doi: 10.1159/000504802
Collins, MT, Singer, FR, Eugster, E. McCune-Albright Syndrome and the extraskeletal manifestations of fibrous dysplasia. Orphanet J Rare Dis 2012;7(1: S4). https://doi.org/10.1186/1750-1172-7-S1-S4 .
doi: 10.1186/1750-1172-7-S1-S4
Merchant, N, Viau-Colindres, JM, Hicks, KA, Balazs, AE, Wesson, DE, Lopez, ME, et al.. McCune-albright Syndrome with unremitting hyperthyroidism at early age: management perspective for early thyroidectomy. Glob Pediatr Health 2019;6:1–5. https://doi.org/10.1177/2333794X19875153 .
doi: 10.1177/2333794X19875153
Sallum, ACR, Leonhardt, FD, Cervantes, O, Abrahão, M, Yazaki, RK. Hipertireoidismo relacionado à síndrome de McCune Albright: relato de dois casos e revisão da literatura. Arquivos Brasileiros Endocrinol Metabol 2008;52:556–61. https://doi.org/10.1590/s0004-27302008000300017 .
doi: 10.1590/s0004-27302008000300017
Geels, RES, Meier, ME, Saikali, A, Tsonaka, R, Appelman-Dijkstra, NM, Boyce, AM. Long bone fractures in fibrous dysplasia/McCune-albright Syndrome: prevalence, natural history, and risk factors. J Bone Miner Res 2022;37:236–43. https://doi.org/10.1002/jbmr.4463 .
doi: 10.1002/jbmr.4463

Auteurs

Patrícia Rosinha (P)

Department of Endocrinology, Centro Hospitalar Baixo Vouga, Aveiro, Portugal.

Diogo Ramalho (D)

Department of Endocrinology, Centro Hospitalar Vila Nova de Gaia/Espinho, Gaia, Portugal.

Orlando Rodrigues (O)

Medical Genetics Unit, Hospital Pediátrico, Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal.

Sérgio Sousa (S)

Medical Genetics Unit, Hospital Pediátrico, Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal.

Cristina Alves (C)

Department of Pediatric Orthopedics, Hospital Pediátrico, Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal.

Joana Lopes (J)

Department of Pediatric Surgery, Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal.

Joana Serra Caetano (JS)

Pediatric Endocrinology and Diabetology Unit, Department of Pediatrics, Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal.

Alice Mirante (A)

Pediatric Endocrinology and Diabetology Unit, Department of Pediatrics, Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH