Coexistence of Genetic Diseases Is a New Clinical Challenge: Three Unrelated Cases of Dual Diagnosis.


Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
14 02 2023
Historique:
received: 14 01 2023
revised: 30 01 2023
accepted: 09 02 2023
entrez: 25 2 2023
pubmed: 26 2 2023
medline: 3 3 2023
Statut: epublish

Résumé

Technological advancements in molecular genetics and cytogenetics have led to the diagnostic definition of complex or atypical clinical pictures. In this paper, a genetic analysis identifies multimorbidities, one due to either a copy number variant or a chromosome aneuploidy, and a second due to biallelic sequence variants in a gene associated with an autosomal recessive disorder. We diagnosed the simultaneous presence of these conditions, which co-occurred by chance, in three unrelated patients: a 10q11.22q11.23 microduplication and a homozygous variant, c.3470A>G (p.Tyr1157Cys), in the

Identifiants

pubmed: 36833411
pii: genes14020484
doi: 10.3390/genes14020484
pmc: PMC9957527
pii:
doi:

Substances chimiques

ABCA4 protein, human 0
ATP-Binding Cassette Transporters 0

Types de publication

Case Reports

Langues

eng

Sous-ensembles de citation

IM

Références

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Auteurs

Anna Paola Capra (AP)

Department of Chemical, Biological, Pharmaceutical and Environmental Sciences, University of Messina, Viale Ferdinando Stagno D'Alcontres 31, 98166 Messina, Italy.

Maria Angela La Rosa (MA)

Genetics and Pharmacogenetics Unit, "Gaetano Martino" University Hospital, Via Consolare Valeria 1, 98125 Messina, Italy.

Sara Briguori (S)

Genetics and Pharmacogenetics Unit, "Gaetano Martino" University Hospital, Via Consolare Valeria 1, 98125 Messina, Italy.

Rosa Civa (R)

Genetics and Pharmacogenetics Unit, "Gaetano Martino" University Hospital, Via Consolare Valeria 1, 98125 Messina, Italy.

Chiara Passarelli (C)

Translational Cytogenomics Research Unit, Bambino Gesù Children's Hospital, IRCCS, 00165 Rome, Italy.

Emanuele Agolini (E)

Translational Cytogenomics Research Unit, Bambino Gesù Children's Hospital, IRCCS, 00165 Rome, Italy.

Antonio Novelli (A)

Translational Cytogenomics Research Unit, Bambino Gesù Children's Hospital, IRCCS, 00165 Rome, Italy.

Silvana Briuglia (S)

Genetics and Pharmacogenetics Unit, "Gaetano Martino" University Hospital, Via Consolare Valeria 1, 98125 Messina, Italy.
Department of Biomedical and Dental Sciences and Morphofunctional Imaging, University of Messina, Via Consolare Valeria 1, 98125 Messina, Italy.

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Classifications MeSH