Circulating tumor DNA reveals complex biological features with clinical relevance in metastatic breast cancer.


Journal

Nature communications
ISSN: 2041-1723
Titre abrégé: Nat Commun
Pays: England
ID NLM: 101528555

Informations de publication

Date de publication:
01 03 2023
Historique:
received: 02 09 2022
accepted: 14 02 2023
entrez: 1 3 2023
pubmed: 2 3 2023
medline: 4 3 2023
Statut: epublish

Résumé

Liquid biopsy has proven valuable in identifying individual genetic alterations; however, the ability of plasma ctDNA to capture complex tumor phenotypes with clinical value is unknown. To address this question, we have performed 0.5X shallow whole-genome sequencing in plasma from 459 patients with metastatic breast cancer, including 245 patients treated with endocrine therapy and a CDK4/6 inhibitor (ET + CDK4/6i) from 2 independent cohorts. We demonstrate that machine learning multi-gene signatures, obtained from ctDNA, identify complex biological features, including measures of tumor proliferation and estrogen receptor signaling, similar to what is accomplished using direct tumor tissue DNA or RNA profiling. More importantly, 4 DNA-based subtypes, and a ctDNA-based genomic signature tracking retinoblastoma loss-of-heterozygosity, are significantly associated with poor response and survival outcome following ET + CDK4/6i, independently of plasma tumor fraction. Our approach opens opportunities for the discovery of additional multi-feature genomic predictors coming from ctDNA in breast cancer and other cancer-types.

Identifiants

pubmed: 36859416
doi: 10.1038/s41467-023-36801-9
pii: 10.1038/s41467-023-36801-9
pmc: PMC9977734
doi:

Substances chimiques

Circulating Tumor DNA 0
DNA, Neoplasm 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1157

Informations de copyright

© 2023. The Author(s).

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Auteurs

Aleix Prat (A)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain. alprat@clinic.cat.
Reveal Genomics, Barcelona, Spain. alprat@clinic.cat.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain. alprat@clinic.cat.
Department of Medicine, University of Barcelona, Barcelona, Spain. alprat@clinic.cat.
Institute of Oncology (IOB)-Hospital Quirónsalud, Barcelona, Spain. alprat@clinic.cat.
SOLTI cooperative group, Barcelona, Spain. alprat@clinic.cat.

Fara Brasó-Maristany (F)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.

Olga Martínez-Sáez (O)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.

Esther Sanfeliu (E)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Pathology, Hospital Clinic de Barcelona, Barcelona, Spain.

Youli Xia (Y)

Reveal Genomics, Barcelona, Spain.

Meritxell Bellet (M)

SOLTI cooperative group, Barcelona, Spain.
Department of Medical Oncology, Vall d'Hebron University Hospital, Autonomous University of Barcelona, Barcelona, Spain.
Breast Cancer and Melanoma Group, Vall d'Hebron Institute of Oncology, Barcelona, Spain.

Patricia Galván (P)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.

Débora Martínez (D)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.

Tomás Pascual (T)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain.
SOLTI cooperative group, Barcelona, Spain.
Lineberger Comprehensive Cancer Center, University of North Carolina, Chapel Hill, USA.

Mercedes Marín-Aguilera (M)

Reveal Genomics, Barcelona, Spain.

Anna Rodríguez (A)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain.

Nuria Chic (N)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain.

Barbara Adamo (B)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.

Laia Paré (L)

Reveal Genomics, Barcelona, Spain.

Maria Vidal (M)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.

Mireia Margelí (M)

Department of Medical Oncology, Institut Catalan of Oncology - Badalona, Hospital Germans Trias i Pujol, Badalona, Spain.

Ester Ballana (E)

AIDS Research Institute-IrsiCaixa and Health Research Institute Germans Trias i Pujol (IGTP), Hospital Germans Trias i Pujol, Badalona, Spain.

Marina Gómez-Rey (M)

Cancer Genomics Group, Vall d´Hebron Institute of Oncology (VHIO), Barcelona, Spain.

Mafalda Oliveira (M)

SOLTI cooperative group, Barcelona, Spain.
Department of Medical Oncology, Vall d'Hebron University Hospital, Autonomous University of Barcelona, Barcelona, Spain.
Breast Cancer and Melanoma Group, Vall d'Hebron Institute of Oncology, Barcelona, Spain.

Eudald Felip (E)

Department of Medical Oncology, Institut Catalan of Oncology - Badalona, Hospital Germans Trias i Pujol, Badalona, Spain.
AIDS Research Institute-IrsiCaixa and Health Research Institute Germans Trias i Pujol (IGTP), Hospital Germans Trias i Pujol, Badalona, Spain.

Judit Matito (J)

Cancer Genomics Group, Vall d´Hebron Institute of Oncology (VHIO), Barcelona, Spain.

Rodrigo Sánchez-Bayona (R)

Department of Medical Oncology, Hospital Universitario 12 de Octubre, Madrid, Spain.

Anna Suñol (A)

Department of Medical Oncology, Vall d'Hebron University Hospital, Autonomous University of Barcelona, Barcelona, Spain.
Breast Cancer and Melanoma Group, Vall d'Hebron Institute of Oncology, Barcelona, Spain.

Cristina Saura (C)

SOLTI cooperative group, Barcelona, Spain.
Department of Medical Oncology, Vall d'Hebron University Hospital, Autonomous University of Barcelona, Barcelona, Spain.
Breast Cancer and Melanoma Group, Vall d'Hebron Institute of Oncology, Barcelona, Spain.

Eva Ciruelos (E)

Department of Medical Oncology, Hospital Universitario 12 de Octubre, Madrid, Spain.

Pablo Tolosa (P)

Department of Medical Oncology, Hospital Universitario 12 de Octubre, Madrid, Spain.

Montserrat Muñoz (M)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.
SOLTI cooperative group, Barcelona, Spain.

Blanca González-Farré (B)

Translational Genomics and Targeted Therapies in Solid Tumors, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Pathology, Hospital Clinic de Barcelona, Barcelona, Spain.

Patricia Villagrasa (P)

Reveal Genomics, Barcelona, Spain.

Joel S Parker (JS)

Department of Genetics, University of North Carolina, Chapel Hill, USA.

Charles M Perou (CM)

Department of Genetics, University of North Carolina, Chapel Hill, USA.

Ana Vivancos (A)

Cancer Genomics Group, Vall d´Hebron Institute of Oncology (VHIO), Barcelona, Spain.

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Classifications MeSH