Resilience to autosomal dominant Alzheimer's disease in a Reelin-COLBOS heterozygous man.


Journal

Nature medicine
ISSN: 1546-170X
Titre abrégé: Nat Med
Pays: United States
ID NLM: 9502015

Informations de publication

Date de publication:
05 2023
Historique:
received: 18 10 2022
accepted: 22 03 2023
medline: 24 5 2023
pubmed: 16 5 2023
entrez: 15 5 2023
Statut: ppublish

Résumé

We characterized the world's second case with ascertained extreme resilience to autosomal dominant Alzheimer's disease (ADAD). Side-by-side comparisons of this male case and the previously reported female case with ADAD homozygote for the APOE3 Christchurch (APOECh) variant allowed us to discern common features. The male remained cognitively intact until 67 years of age despite carrying a PSEN1-E280A mutation. Like the APOECh carrier, he had extremely elevated amyloid plaque burden and limited entorhinal Tau tangle burden. He did not carry the APOECh variant but was heterozygous for a rare variant in RELN (H3447R, termed COLBOS after the Colombia-Boston biomarker research study), a ligand that like apolipoprotein E binds to the VLDLr and APOEr2 receptors. RELN-COLBOS is a gain-of-function variant showing stronger ability to activate its canonical protein target Dab1 and reduce human Tau phosphorylation in a knockin mouse. A genetic variant in a case protected from ADAD suggests a role for RELN signaling in resilience to dementia.

Identifiants

pubmed: 37188781
doi: 10.1038/s41591-023-02318-3
pii: 10.1038/s41591-023-02318-3
pmc: PMC10202812
doi:

Substances chimiques

Dab1 protein, mouse 0
Nerve Tissue Proteins 0
RELN protein, human EC 3.4.21.-

Types de publication

Case Reports Comparative Study Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1243-1252

Subventions

Organisme : NIH HHS
ID : DP5 OD019833
Pays : United States
Organisme : NIA NIH HHS
ID : R01 AG054671
Pays : United States
Organisme : NIA NIH HHS
ID : RF1 AG077627
Pays : United States

Informations de copyright

© 2023. The Author(s).

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Auteurs

Francisco Lopera (F)

Neuroscience Group of Antioquia, Medicine School, University of Antioquia, Medellín, Colombia.
Medicine School, University of Antioquia, Medellín, Colombia.

Claudia Marino (C)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Anita S Chandrahas (AS)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Michael O'Hare (M)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Nelson David Villalba-Moreno (ND)

Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.

David Aguillon (D)

Neuroscience Group of Antioquia, Medicine School, University of Antioquia, Medellín, Colombia.
Medicine School, University of Antioquia, Medellín, Colombia.

Ana Baena (A)

Neuroscience Group of Antioquia, Medicine School, University of Antioquia, Medellín, Colombia.

Justin S Sanchez (JS)

Department of Neurology at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA.

Clara Vila-Castelar (C)

Department of Psychiatry at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA.

Liliana Ramirez Gomez (L)

Department of Neurology at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA.

Natalia Chmielewska (N)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Gabriel M Oliveira (GM)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.
Department of Psychiatry at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA.

Jessica Lisa Littau (JL)

Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.

Kristin Hartmann (K)

Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.

Kyungeun Park (K)

Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.

Susanne Krasemann (S)

Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.

Markus Glatzel (M)

Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.

Dorothee Schoemaker (D)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.
Department of Psychiatry at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA.

Lucia Gonzalez-Buendia (L)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Santiago Delgado-Tirado (S)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Said Arevalo-Alquichire (S)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Kahira L Saez-Torres (KL)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Dhanesh Amarnani (D)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Leo A Kim (LA)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Randall C Mazzarino (RC)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Harper Gordon (H)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA.

Yamile Bocanegra (Y)

Neuroscience Group of Antioquia, Medicine School, University of Antioquia, Medellín, Colombia.

Andres Villegas (A)

Neuroscience Group of Antioquia, Medicine School, University of Antioquia, Medellín, Colombia.
Medicine School, University of Antioquia, Medellín, Colombia.

Xiaowu Gai (X)

Center for Personalized Medicine, Department of Pathology and Laboratory Medicine, Children's Hospital Los Angeles, Los Angeles, CA, USA.
Department of Pathology, Keck School of Medicine of University of Southern California, Los Angeles, CA, USA.

Moiz Bootwalla (M)

Center for Personalized Medicine, Department of Pathology and Laboratory Medicine, Children's Hospital Los Angeles, Los Angeles, CA, USA.

Jianling Ji (J)

Center for Personalized Medicine, Department of Pathology and Laboratory Medicine, Children's Hospital Los Angeles, Los Angeles, CA, USA.
Department of Pathology, Keck School of Medicine of University of Southern California, Los Angeles, CA, USA.

Lishuang Shen (L)

Center for Personalized Medicine, Department of Pathology and Laboratory Medicine, Children's Hospital Los Angeles, Los Angeles, CA, USA.

Kenneth S Kosik (KS)

Neuroscience Research Institute, Department of Molecular Cellular Developmental Biology, University of California, Santa Barbara, CA, USA.

Yi Su (Y)

The Banner Alzheimer's Institute, Phoenix, AZ, USA.

Yinghua Chen (Y)

The Banner Alzheimer's Institute, Phoenix, AZ, USA.

Aaron Schultz (A)

Department of Neurology at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA.

Reisa A Sperling (RA)

Department of Neurology at Harvard Medical School, Brigham and Women's Hospital, Boston, MA, USA.

Keith Johnson (K)

Department of Neurology at Harvard Medical School, Brigham and Women's Hospital, Boston, MA, USA.
Department of Radiology at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA.

Eric M Reiman (EM)

The Banner Alzheimer's Institute, Phoenix, AZ, USA.
University of Arizona, Tucson, AZ, USA.
Arizona State University, Tucson, AZ, USA.
Neurogenomics Division, Translational Genomics Research Institute, Phoenix, AZ, USA.

Diego Sepulveda-Falla (D)

Institute of Neuropathology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany. d.sepulveda-falla@uke.uni-hamburg.de.

Joseph F Arboleda-Velasquez (JF)

Schepens Eye Research Institute of Mass Eye and Ear and Department of Ophthalmology at Harvard Medical School, Boston, MA, USA. joseph_arboleda@meei.harvard.edu.

Yakeel T Quiroz (YT)

Neuroscience Group of Antioquia, Medicine School, University of Antioquia, Medellín, Colombia. yquiroz@mgh.harvard.edu.
Department of Neurology at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA. yquiroz@mgh.harvard.edu.
Department of Psychiatry at Harvard Medical School, Massachusetts General Hospital, Boston, MA, USA. yquiroz@mgh.harvard.edu.

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