Functional Evidence of

CCDC186 mutations DCVs dense-core vesicles growth hormone deficiency hypomyelination low levels of cortisol low levels of insulin non-ketotic hypoglycemia seizures

Journal

International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791

Informations de publication

Date de publication:
01 Aug 2023
Historique:
received: 05 07 2023
revised: 29 07 2023
accepted: 30 07 2023
medline: 14 8 2023
pubmed: 12 8 2023
entrez: 12 8 2023
Statut: epublish

Résumé

CCDC186 protein is involved in the maturation of dense-core vesicles (DCVs) in the trans-Golgi network in neurons and endocrine cells. Mutations in genes involved in DCV regulation, other than

Identifiants

pubmed: 37569695
pii: ijms241512319
doi: 10.3390/ijms241512319
pmc: PMC10419233
pii:
doi:

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Instituto de Salud Carlos III
ID : PI19/01310 and PI22/00856

Références

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Auteurs

Luisa Arrabal (L)

Pediatric Neurology Department, Hospital Virgen de las Nieves, 18014 Granada, Spain.

Gerard Muñoz-Pujol (G)

Section of Inborn Errors of Metabolism-IBC, Department of Biochemistry and Molecular Genetics, Hospital Clínic Barcelona, IDIBAPS, CIBERER, 08028 Barcelona, Spain.

Inmaculada Medina Martínez (I)

Pediatric Neurology Department, Hospital Virgen de las Nieves, 18014 Granada, Spain.

Laura Gort (L)

Section of Inborn Errors of Metabolism-IBC, Department of Biochemistry and Molecular Genetics, Hospital Clínic Barcelona, IDIBAPS, CIBERER, 08028 Barcelona, Spain.

Judit García-Villoria (J)

Section of Inborn Errors of Metabolism-IBC, Department of Biochemistry and Molecular Genetics, Hospital Clínic Barcelona, IDIBAPS, CIBERER, 08028 Barcelona, Spain.

Susana Roldán (S)

Pediatric Neurology Department, Hospital Virgen de las Nieves, 18014 Granada, Spain.

Frederic Tort (F)

Section of Inborn Errors of Metabolism-IBC, Department of Biochemistry and Molecular Genetics, Hospital Clínic Barcelona, IDIBAPS, CIBERER, 08028 Barcelona, Spain.

Antonia Ribes (A)

Section of Inborn Errors of Metabolism-IBC, Department of Biochemistry and Molecular Genetics, Hospital Clínic Barcelona, IDIBAPS, CIBERER, 08028 Barcelona, Spain.

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Classifications MeSH