Spermine-Based Poly(β-amino ester)s for siRNA Delivery against Mutated KRAS in Lung Cancer.


Journal

Molecular pharmaceutics
ISSN: 1543-8392
Titre abrégé: Mol Pharm
Pays: United States
ID NLM: 101197791

Informations de publication

Date de publication:
04 09 2023
Historique:
pmc-release: 04 09 2024
medline: 5 9 2023
pubmed: 14 8 2023
entrez: 14 8 2023
Statut: ppublish

Résumé

Polyethylenimine (PEI) is a highly efficient cationic polymer for nucleic acid delivery, and although it is commonly used in preclinical studies, its clinical application is limited because of concerns regarding its cytotoxicity. Poly(β-amino ester)s are a new group of biodegradable and biocompatible cationic polymers that can be used for siRNA delivery. In this study, we synthesized Boc-protected and deprotected poly(β-amino ester)s, P(BSpBAE) and P(SpBAE), respectively, based on spermine and 1,4-butanediol diacrylate to deliver siRNA. The polymers were synthesized by Michael addition in a step-growth polymerization and characterized via

Identifiants

pubmed: 37578116
doi: 10.1021/acs.molpharmaceut.3c00206
pmc: PMC7615020
mid: EMS185245
doi:

Substances chimiques

poly(beta-amino ester) 0
RNA, Small Interfering 0
Spermine 2FZ7Y3VOQX
Proto-Oncogene Proteins p21(ras) EC 3.6.5.2
Polymers 0
Polyethyleneimine 9002-98-6
KRAS protein, human 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

4505-4516

Subventions

Organisme : European Research Council
ID : 637830
Pays : International

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Auteurs

Yao Jin (Y)

Department of Pharmacy, Pharmaceutical Technology and Biopharmaceutics, Ludwig-Maximilians-University Munich, Butenandtstr. 5-13, Munich 81377, Germany.

Friederike Adams (F)

Department of Pharmacy, Pharmaceutical Technology and Biopharmaceutics, Ludwig-Maximilians-University Munich, Butenandtstr. 5-13, Munich 81377, Germany.
University of Stuttgart, Institute of Polymer Chemistry, Chair of Macromolecular Materials and Fiber Chemistry, Pfaffenwaldring 55, Stuttgart 70569, Germany.

Lorenz Isert (L)

Department of Pharmacy, Pharmaceutical Technology and Biopharmaceutics, Ludwig-Maximilians-University Munich, Butenandtstr. 5-13, Munich 81377, Germany.

Domizia Baldassi (D)

Department of Pharmacy, Pharmaceutical Technology and Biopharmaceutics, Ludwig-Maximilians-University Munich, Butenandtstr. 5-13, Munich 81377, Germany.

Olivia M Merkel (OM)

Department of Pharmacy, Pharmaceutical Technology and Biopharmaceutics, Ludwig-Maximilians-University Munich, Butenandtstr. 5-13, Munich 81377, Germany.

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Classifications MeSH