Lipid profile in Noonan syndrome and related disorders: trend by age, sex and genotype.


Journal

Frontiers in endocrinology
ISSN: 1664-2392
Titre abrégé: Front Endocrinol (Lausanne)
Pays: Switzerland
ID NLM: 101555782

Informations de publication

Date de publication:
2023
Historique:
received: 20 04 2023
accepted: 12 07 2023
medline: 18 8 2023
pubmed: 17 8 2023
entrez: 17 8 2023
Statut: epublish

Résumé

RASopathies are developmental disorders caused by dysregulation of the RAS-MAPK signalling pathway, which contributes to the modulation of multiple extracellular signals, including hormones and growth factors regulating energetic metabolism, including lipid synthesis, storage, and degradation. We evaluated the body composition and lipid profiles of a single-centre cohort of 93 patients with a molecularly confirmed diagnosis of RASopathy by assessing height, BMI, and total cholesterol, HDL, triglycerides, apolipoprotein, fasting glucose, and insulin levels, in the context of a cross sectional and longitudinal study. We specifically investigated and compared anthropometric and haematochemistry data between the Noonan syndrome (NS) and Mazzanti syndrome (NS/LAH) groups. At the first evaluation (9.5 ± 6.2 years), reduced growth (-1.80 ± 1.07 DS) was associated with a slightly reduced BMI (-0.34 DS ± 1.15 DS). Lipid profiling documented low total cholesterol levels (< 5 The present findings document an unfavourable lipid profile in subjects with NS, in particular

Sections du résumé

Background
RASopathies are developmental disorders caused by dysregulation of the RAS-MAPK signalling pathway, which contributes to the modulation of multiple extracellular signals, including hormones and growth factors regulating energetic metabolism, including lipid synthesis, storage, and degradation.
Subjects and methods
We evaluated the body composition and lipid profiles of a single-centre cohort of 93 patients with a molecularly confirmed diagnosis of RASopathy by assessing height, BMI, and total cholesterol, HDL, triglycerides, apolipoprotein, fasting glucose, and insulin levels, in the context of a cross sectional and longitudinal study. We specifically investigated and compared anthropometric and haematochemistry data between the Noonan syndrome (NS) and Mazzanti syndrome (NS/LAH) groups.
Results
At the first evaluation (9.5 ± 6.2 years), reduced growth (-1.80 ± 1.07 DS) was associated with a slightly reduced BMI (-0.34 DS ± 1.15 DS). Lipid profiling documented low total cholesterol levels (< 5
Conclusion
The present findings document an unfavourable lipid profile in subjects with NS, in particular

Identifiants

pubmed: 37588986
doi: 10.3389/fendo.2023.1209339
pmc: PMC10425765
doi:

Substances chimiques

Apolipoprotein A-I 0
Glucose IY9XDZ35W2
Cholesterol 97C5T2UQ7J

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1209339

Informations de copyright

Copyright © 2023 Tamburrino, Mazzanti, Scarano, Gibertoni, Sirolli, Zioutas, Schiavariello, Perri, Mantovani, Rossi, Tartaglia and Pession.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

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Auteurs

Federica Tamburrino (F)

Rare Diseases Unit, Department of Pediatrics, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Laura Mazzanti (L)

Alma Mater University of Bologna, Bologna, Italy.

Emanuela Scarano (E)

Rare Diseases Unit, Department of Pediatrics, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Dino Gibertoni (D)

Research and Innovation Unit, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Maria Sirolli (M)

Pathology Unit, Department of Experimental, Diagnostic and Specialty Medicine, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Maximiliano Zioutas (M)

Department of Pediatrics, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Concetta Schiavariello (C)

Rare Diseases Unit, Department of Pediatrics, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Annamaria Perri (A)

Rare Diseases Unit, Department of Pediatrics, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Alessio Mantovani (A)

Department of Pediatrics, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Cesare Rossi (C)

Medical Genetics Unit, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

Marco Tartaglia (M)

Molecular Genetics and Functional Genomics, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome, Italy.

Andrea Pession (A)

Department of Pediatrics, IRCCS Azienda Ospedaliero-Universitaria Di Bologna, Bologna, Italy.

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Classifications MeSH