Glutaryl-CoA Dehydrogenase Misfolding in Glutaric Acidemia Type 1.


Journal

International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791

Informations de publication

Date de publication:
24 Aug 2023
Historique:
received: 04 07 2023
revised: 11 08 2023
accepted: 19 08 2023
medline: 11 9 2023
pubmed: 9 9 2023
entrez: 9 9 2023
Statut: epublish

Résumé

Glutaric acidemia type 1 (GA1) is a neurotoxic metabolic disorder due to glutaryl-CoA dehydrogenase (GCDH) deficiency. The high number of missense variants associated with the disease and their impact on GCDH activity suggest that disturbed protein conformation can affect the biochemical phenotype. We aimed to elucidate the molecular basis of protein loss of function in GA1 by performing a parallel analysis in a large panel of

Identifiants

pubmed: 37685964
pii: ijms241713158
doi: 10.3390/ijms241713158
pmc: PMC10487539
pii:
doi:

Substances chimiques

Glutaryl-CoA Dehydrogenase EC 1.3.8.6

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Else Kröner Fresenius Clinical Research School - Rare immune system diseases
ID : to AFP-S
Organisme : Funding program for research and teaching (FöFoLe 543 Program) from the medical school of Ludwig-Maximilians-University, 80337 Munich, Germany
ID : 45/2010; 797/2012

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Auteurs

Madalena Barroso (M)

University Children's Research, UCR@Kinder-UKE, University Medical Center Hamburg-Eppendorf, 20246 Hamburg, Germany.

Marcus Gertzen (M)

Department of Molecular Pediatrics, Dr. von Hauner Children's Hospital, Ludwig-Maximilians-University, 80337 Munich, Germany.
Psychiatry and Psychotherapy, Faculty of Medicine, University of Augsburg, 86156 Augsburg, Germany.

Alexandra F Puchwein-Schwepcke (AF)

Department of Molecular Pediatrics, Dr. von Hauner Children's Hospital, Ludwig-Maximilians-University, 80337 Munich, Germany.
Department of Pediatric Neurology and Developmental Medicine, University of Basel Children's Hospital, 4056 Basel, Switzerland.

Heike Preisler (H)

Department of Molecular Pediatrics, Dr. von Hauner Children's Hospital, Ludwig-Maximilians-University, 80337 Munich, Germany.

Andreas Sturm (A)

Department of Molecular Pediatrics, Dr. von Hauner Children's Hospital, Ludwig-Maximilians-University, 80337 Munich, Germany.

Dunja D Reiss (DD)

Department of Molecular Pediatrics, Dr. von Hauner Children's Hospital, Ludwig-Maximilians-University, 80337 Munich, Germany.
Medizinische Klinik und Poliklinik IV, Klinikum der Universität München, 81377 Munich, Germany.

Marta K Danecka (MK)

University Children's Research, UCR@Kinder-UKE, University Medical Center Hamburg-Eppendorf, 20246 Hamburg, Germany.

Ania C Muntau (AC)

University Children's Research, UCR@Kinder-UKE, University Medical Center Hamburg-Eppendorf, 20246 Hamburg, Germany.
University Children's Hospital, University Medical Center Hamburg-Eppendorf, 20246 Hamburg, Germany.

Søren W Gersting (SW)

University Children's Research, UCR@Kinder-UKE, University Medical Center Hamburg-Eppendorf, 20246 Hamburg, Germany.

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Classifications MeSH