The Next-Generation Oral Selective Estrogen Receptor Degrader Camizestrant (AZD9833) Suppresses ER+ Breast Cancer Growth and Overcomes Endocrine and CDK4/6 Inhibitor Resistance.


Journal

Cancer research
ISSN: 1538-7445
Titre abrégé: Cancer Res
Pays: United States
ID NLM: 2984705R

Informations de publication

Date de publication:
01 Dec 2023
Historique:
received: 03 03 2023
revised: 11 07 2023
accepted: 15 09 2023
medline: 4 12 2023
pubmed: 19 9 2023
entrez: 19 9 2023
Statut: ppublish

Résumé

Oral selective estrogen receptor degraders (SERD) could become the backbone of endocrine therapy (ET) for estrogen receptor-positive (ER+) breast cancer, as they achieve greater inhibition of ER-driven cancers than current ETs and overcome key resistance mechanisms. In this study, we evaluated the preclinical pharmacology and efficacy of the next-generation oral SERD camizestrant (AZD9833) and assessed ER-co-targeting strategies by combining camizestrant with CDK4/6 inhibitors (CDK4/6i) and PI3K/AKT/mTOR-targeted therapy in models of progression on CDK4/6i and/or ET. Camizestrant demonstrated robust and selective ER degradation, modulated ER-regulated gene expression, and induced complete ER antagonism and significant antiproliferation activity in ESR1 wild-type (ESR1wt) and mutant (ESR1m) breast cancer cell lines and patient-derived xenograft (PDX) models. Camizestrant also delivered strong antitumor activity in fulvestrant-resistant ESR1wt and ESR1m PDX models. Evaluation of camizestrant in combination with CDK4/6i (palbociclib or abemaciclib) in CDK4/6-naive and -resistant models, as well as in combination with PI3Kαi (alpelisib), mTORi (everolimus), or AKTi (capivasertib), indicated that camizestrant was active with CDK4/6i or PI3K/AKT/mTORi and that antitumor activity was further increased by the triple combination. The response was observed independently of PI3K pathway mutation status. Overall, camizestrant shows strong and broad antitumor activity in ER+ breast cancer as a monotherapy and when combined with CDK4/6i and PI3K/AKT/mTORi. Camizestrant, a next-generation oral SERD, shows promise in preclinical models of ER+ breast cancer alone and in combination with CDK4/6 and PI3K/AKT/mTOR inhibitors to address endocrine resistance, a current barrier to treatment.

Identifiants

pubmed: 37725704
pii: 729132
doi: 10.1158/0008-5472.CAN-23-0694
pmc: PMC10690091
doi:

Substances chimiques

Receptors, Estrogen 0
AZD9833 0
Proto-Oncogene Proteins c-akt EC 2.7.11.1
Phosphatidylinositol 3-Kinases EC 2.7.1.-
Estrogen Antagonists 0
Protein Kinase Inhibitors 0
Cyclin-Dependent Kinase 4 EC 2.7.11.22
CDK4 protein, human EC 2.7.11.22

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

3989-4004

Subventions

Organisme : AstraZeneca (AstraZeneca PLC)

Informations de copyright

©2023 The Authors; Published by the American Association for Cancer Research.

Références

Nat Rev Clin Oncol. 2015 Oct;12(10):573-83
pubmed: 26122181
Cancer Cell. 2018 Sep 10;34(3):427-438.e6
pubmed: 30205045
Breast Cancer Res. 2020 Aug 14;22(1):89
pubmed: 32795346
NPJ Breast Cancer. 2023 Apr 5;9(1):20
pubmed: 37019913
Endocr Relat Cancer. 2015 Oct;22(5):713-24
pubmed: 26162914
Breast. 2015 Nov;24 Suppl 2:S60-6
pubmed: 26271713
Nat Commun. 2021 Aug 25;12(1):5112
pubmed: 34433817
Nat Commun. 2014 Aug 07;5:4577
pubmed: 25099679
Ther Adv Med Oncol. 2022 Jul 30;14:17588359221113694
pubmed: 35923930
Endocr Relat Cancer. 2019 Jan;26(1):R15-R30
pubmed: 30389903
Oncogene. 2003 Oct 20;22(47):7316-39
pubmed: 14576841
Breast Cancer Res Treat. 2020 Jan;179(1):67-77
pubmed: 31562570
Clin Cancer Res. 2018 Aug 1;24(15):3510-3518
pubmed: 29440181
Breast Cancer Res. 2021 Aug 15;23(1):85
pubmed: 34392831
Cell. 2019 Aug 8;178(4):949-963.e18
pubmed: 31353221
Adv Protein Chem Struct Biol. 2019;116:135-170
pubmed: 31036290
Eur J Cancer. 2003 May;39(7):861-9
pubmed: 12706354
Front Oncol. 2019 Jul 23;9:666
pubmed: 31396487
Breast Cancer Res. 2004;6(6):269-74
pubmed: 15535858
Nat Commun. 2022 Sep 7;13(1):5258
pubmed: 36071033
Genome Biol. 2014;15(12):550
pubmed: 25516281
Elife. 2016 Jul 13;5:
pubmed: 27410477
Br J Cancer. 2019 Feb;120(3):331-339
pubmed: 30555156
Bioinformatics. 2012 Oct 15;28(20):2678-9
pubmed: 22914218
Nat Biotechnol. 2019 Aug;37(8):907-915
pubmed: 31375807
Ther Adv Med Oncol. 2020 Jul 28;12:1758835920940939
pubmed: 32782489
Cancer Discov. 2018 Nov;8(11):1390-1403
pubmed: 30206110
J Med Chem. 2020 Dec 10;63(23):14530-14559
pubmed: 32910656
Breast Cancer Res Treat. 2012 May;133(1):237-46
pubmed: 22286314
Cell Chem Biol. 2019 Aug 15;26(8):1067-1080.e8
pubmed: 31178407
Br J Cancer. 2004 Mar;90 Suppl 1:S7-10
pubmed: 15094758
Breast Cancer Res. 2020 Aug 8;22(1):84
pubmed: 32771039
Int J Mol Sci. 2020 Sep 03;21(17):
pubmed: 32899139
J Med Chem. 2021 Aug 26;64(16):11841-11856
pubmed: 34251202
Future Oncol. 2023 Mar;19(8):559-573
pubmed: 37070653
Lancet. 1994 Feb 19;343(8895):448-52
pubmed: 7905955
Breast Cancer Res. 2020 Apr 6;22(1):33
pubmed: 32252811
Sci Transl Med. 2015 Apr 15;7(283):283ra51
pubmed: 25877889
J Clin Oncol. 2010 Oct 20;28(30):4594-600
pubmed: 20855825
Mol Cancer Ther. 2021 Feb;20(2):250-262
pubmed: 33310762
J Clin Oncol. 2022 Oct 1;40(28):3246-3256
pubmed: 35584336
Cancer Res. 2016 Jun 1;76(11):3307-18
pubmed: 27020862
Nat Methods. 2017 Apr;14(4):417-419
pubmed: 28263959
Lancet Oncol. 2020 Oct;21(10):1296-1308
pubmed: 32919527
Br J Cancer. 2001 Nov;85 Suppl 2:11-4
pubmed: 11900210

Auteurs

Mandy Lawson (M)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Natalie Cureton (N)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Susana Ros (S)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Azadeh Cheraghchi-Bashi (A)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Jelena Urosevic (J)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Sophie D'Arcy (S)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Oona Delpuech (O)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Michelle DuPont (M)

Research and Early Development, Oncology R&D, AstraZeneca, Waltham, Massachusetts.

David I Fisher (DI)

Discovery Sciences, Biopharmaceuticals R&D, AstraZeneca, Cambridge, United Kingdom.

Eric T Gangl (ET)

Research and Early Development, Oncology R&D, AstraZeneca, Waltham, Massachusetts.

Hilary Lewis (H)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Dawn Trueman (D)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Neha Wali (N)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Stuart C Williamson (SC)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Jennifer Moss (J)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Elodie Montaudon (E)

Institut Curie, Paris, France.

Heloise Derrien (H)

Institut Curie, Paris, France.

Ricardo J Miragaia (RJ)

Oncology Data Science, Oncology R&D, AstraZeneca, Cambridge, United Kingdom.

Sladjana Gagrica (S)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Pablo Morentin-Gutierrez (P)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Thomas A Moss (TA)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Gareth Maglennon (G)

Clinical Pharmacology and Safety Sciences, Biopharmaceuticals R&D, AstraZeneca, Cambridge, United Kingdom.

Daniel Sutton (D)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Radoslaw Polanski (R)

Discovery Sciences, Biopharmaceuticals R&D, AstraZeneca, Cambridge, United Kingdom.

Alan Rosen (A)

Research and Early Development, Oncology R&D, AstraZeneca, Waltham, Massachusetts.

Jonathan Cairns (J)

Discovery Sciences, Biopharmaceuticals R&D, AstraZeneca, Cambridge, United Kingdom.

Pei Zhang (P)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Mònica Sánchez-Guixé (M)

Experimental Therapeutics Group, Vall d'Hebron Institute of Oncology (VHIO), Barcelona, Spain.

Violeta Serra (V)

Experimental Therapeutics Group, Vall d'Hebron Institute of Oncology (VHIO), Barcelona, Spain.

Susan E Critchlow (SE)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

James S Scott (JS)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Justin P O Lindemann (JPO)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Simon T Barry (ST)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Teresa Klinowska (T)

Late Development, Oncology R&D, AstraZeneca, Cambridge, United Kingdom.

Christopher J Morrow (CJ)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

Larissa S Carnevalli (L)

The Discovery Centre, Biomedical Campus, AstraZeneca, Cambridge, United Kingdom.

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