A single-center, double-blind, randomized, placebo-controlled, two-arm study to evaluate the safety and efficacy of once-weekly sirolimus (rapamycin) on muscle strength and endurance in older adults following a 13-week exercise program.


Journal

Trials
ISSN: 1745-6215
Titre abrégé: Trials
Pays: England
ID NLM: 101263253

Informations de publication

Date de publication:
01 Oct 2024
Historique:
received: 17 07 2024
accepted: 20 09 2024
medline: 2 10 2024
pubmed: 2 10 2024
entrez: 1 10 2024
Statut: epublish

Résumé

Aging leads to a decline in muscle mass and strength, contributing to frailty and decreased quality of life. Sirolimus (rapamycin) , an mTOR inhibitor, has shown potential in preclinical studies to extend lifespan and improve health span. This study evaluates the safety and efficacy of once-weekly sirolimus (rapamycin) administration on muscle strength and endurance in older adults engaged in a 13-week exercise program. This randomized, double-blind, placebo-controlled trial will enroll 40 participants aged 65-85. Participants will be randomly assigned to receive either sirolimus (rapamycin) 6 mg/week or placebo for 13 weeks, in conjunction with an at-home exercise program. The primary outcome measure is the change in muscle strength and endurance, assessed by the 30-Second Chair-Stand Test. Secondary outcome measures include adverse events, changes in muscle strength and endurance as measured by the 6-min walk test, handgrip strength, and participant-reported outcomes using the SF-36 survey. Assessments will be conducted at baseline, mid-intervention (week 6), and post-intervention (week 13). Blood samples will be collected for hematology and biochemistry analyses, including full blood count, urea and electrolytes, liver function tests, HbA1c, lipids, serum IGF-1, and hs-CRP. DNA methylation will be analyzed using TruDiagnostic™ to explore changes in biological age. This study aims to provide insights into the potential benefits of intermittent sirolimus (rapamycin) administration on muscle performance in older adults. By alternating periods of mTOR inhibition through rapamycin and activation via exercise, this study will explore a novel approach to enhancing muscle strength and endurance in the aging population. The results could have significant implications for developing interventions to improve physical function and overall health outcomes in older adults. Safety and tolerability will also be closely monitored to ensure the feasibility of this regimen for wider application. Australia New Zealand Clinical Trials Registry, ACTRN12624000790549. Registered on 26 June 2024 https://www.anzctr.org.au/Trial/Registration/TrialReview.aspx?ACTRN=12624000790549 .

Sections du résumé

BACKGROUND BACKGROUND
Aging leads to a decline in muscle mass and strength, contributing to frailty and decreased quality of life. Sirolimus (rapamycin) , an mTOR inhibitor, has shown potential in preclinical studies to extend lifespan and improve health span. This study evaluates the safety and efficacy of once-weekly sirolimus (rapamycin) administration on muscle strength and endurance in older adults engaged in a 13-week exercise program.
METHODS METHODS
This randomized, double-blind, placebo-controlled trial will enroll 40 participants aged 65-85. Participants will be randomly assigned to receive either sirolimus (rapamycin) 6 mg/week or placebo for 13 weeks, in conjunction with an at-home exercise program. The primary outcome measure is the change in muscle strength and endurance, assessed by the 30-Second Chair-Stand Test. Secondary outcome measures include adverse events, changes in muscle strength and endurance as measured by the 6-min walk test, handgrip strength, and participant-reported outcomes using the SF-36 survey. Assessments will be conducted at baseline, mid-intervention (week 6), and post-intervention (week 13). Blood samples will be collected for hematology and biochemistry analyses, including full blood count, urea and electrolytes, liver function tests, HbA1c, lipids, serum IGF-1, and hs-CRP. DNA methylation will be analyzed using TruDiagnostic™ to explore changes in biological age.
DISCUSSION CONCLUSIONS
This study aims to provide insights into the potential benefits of intermittent sirolimus (rapamycin) administration on muscle performance in older adults. By alternating periods of mTOR inhibition through rapamycin and activation via exercise, this study will explore a novel approach to enhancing muscle strength and endurance in the aging population. The results could have significant implications for developing interventions to improve physical function and overall health outcomes in older adults. Safety and tolerability will also be closely monitored to ensure the feasibility of this regimen for wider application.
TRIAL REGISTRATION BACKGROUND
Australia New Zealand Clinical Trials Registry, ACTRN12624000790549. Registered on 26 June 2024 https://www.anzctr.org.au/Trial/Registration/TrialReview.aspx?ACTRN=12624000790549 .

Identifiants

pubmed: 39354527
doi: 10.1186/s13063-024-08490-2
pii: 10.1186/s13063-024-08490-2
doi:

Substances chimiques

Sirolimus W36ZG6FT64
MTOR Inhibitors 0

Types de publication

Journal Article Clinical Trial Protocol

Langues

eng

Sous-ensembles de citation

IM

Pagination

642

Informations de copyright

© 2024. The Author(s).

Références

Strasser B, et al. Role of dietary protein and muscular fitness on longevity and aging. Aging Dis. 2018;9(1):119–32.
doi: 10.14336/AD.2017.0202 pubmed: 29392087 pmcid: 5772850
Lebwohl D, et al. Development of everolimus, a novel oral mTOR inhibitor, across a spectrum of diseases. Ann N Y Acad Sci. 2013;1291:14–32.
doi: 10.1111/nyas.12122 pubmed: 23659703
Johnson SC, Rabinovitch PS, Kaeberlein M. mTOR is a key modulator of ageing and age-related disease. Nature. 2013;493(7432):338–45.
doi: 10.1038/nature11861 pubmed: 23325216 pmcid: 3687363
Laplante M, Sabatini DM. mTOR signaling in growth control and disease. Cell. 2012;149(2):274–93.
doi: 10.1016/j.cell.2012.03.017 pubmed: 22500797 pmcid: 3331679
Liu GY, Sabatini DM. mTOR at the nexus of nutrition, growth, ageing and disease. Nat Rev Mol Cell Biol. 2020;21(4):183–203.
doi: 10.1038/s41580-019-0199-y pubmed: 31937935 pmcid: 7102936
Kaeberlein M, et al. Regulation of yeast replicative life span by TOR and Sch9 in response to nutrients. Science. 2005;310(5751):1193–6.
doi: 10.1126/science.1115535 pubmed: 16293764
Vellai T, et al. Genetics: influence of TOR kinase on lifespan in C. elegans. Nature. 2003;426(6967):620.
doi: 10.1038/426620a pubmed: 14668850
Jia K, Chen D, Riddle DL. The TOR pathway interacts with the insulin signaling pathway to regulate C. elegans larval development, metabolism and life span. Development. 2004;131(16):3897–906.
doi: 10.1242/dev.01255 pubmed: 15253933
Kapahi P, et al. Regulation of lifespan in Drosophila by modulation of genes in the TOR signaling pathway. Curr Biol. 2004;14(10):885–90.
doi: 10.1016/j.cub.2004.03.059 pubmed: 15186745 pmcid: 2754830
Wu JJ, et al. Increased mammalian lifespan and a segmental and tissue-specific slowing of aging after genetic reduction of mTOR expression. Cell Rep. 2013;4(5):913–20.
doi: 10.1016/j.celrep.2013.07.030 pubmed: 23994476 pmcid: 3784301
Zhang Y, et al. Rapamycin extends life and health in C57BL/6 mice. J Gerontol A Biol Sci Med Sci. 2014;69(2):119–30.
doi: 10.1093/gerona/glt056 pubmed: 23682161
Bitto A, et al. Transient rapamycin treatment can increase lifespan and healthspan in middle-aged mice. Elife. 2016;5:e16351.
doi: 10.7554/eLife.16351 pubmed: 27549339 pmcid: 4996648
An JY, et al. Rapamycin treatment attenuates age-associated periodontitis in mice. Geroscience. 2017;39(4):457–63.
doi: 10.1007/s11357-017-9994-6 pubmed: 28889220 pmcid: 5636779
Flynn JM, et al. Late-life rapamycin treatment reverses age-related heart dysfunction. Aging Cell. 2013;12(5):851–62.
doi: 10.1111/acel.12109 pubmed: 23734717
Dai DF, et al. Altered proteome turnover and remodeling by short-term caloric restriction or rapamycin rejuvenate the aging heart. Aging Cell. 2014;13(3):529–39.
doi: 10.1111/acel.12203 pubmed: 24612461 pmcid: 4040127
Hebert M, et al. Single rapamycin administration induces prolonged downward shift in defended body weight in rats. PLoS One. 2014;9(5):e93691.
doi: 10.1371/journal.pone.0093691 pubmed: 24787262 pmcid: 4008417
Miller RA, et al. Rapamycin, but not resveratrol or simvastatin, extends life span of genetically heterogeneous mice. J Gerontol A Biol Sci Med Sci. 2011;66(2):191–201.
doi: 10.1093/gerona/glq178 pubmed: 20974732
Xue QL, et al. Rapamycin increases grip strength and attenuates age-related decline in maximal running distance in old low capacity runner rats. Aging (Albany NY). 2016;8(4):769–76.
doi: 10.18632/aging.100929 pubmed: 26997106
Urfer SR, et al. A randomized controlled trial to establish effects of short-term rapamycin treatment in 24 middle-aged companion dogs. Geroscience. 2017;39(2):117–27.
doi: 10.1007/s11357-017-9972-z pubmed: 28374166 pmcid: 5411365
Krebs M, et al. The mammalian target of rapamycin pathway regulates nutrient-sensitive glucose uptake in man. Diabetes. 2007;56(6):1600–7.
doi: 10.2337/db06-1016 pubmed: 17329620
Singh M, et al. Effect of low-dose rapamycin on senescence markers and physical functioning in older adults with coronary artery disease: results of a pilot study. J Frailty Aging. 2016;5(4):204–7.
pubmed: 27883166
Kraig E, et al. A randomized control trial to establish the feasibility and safety of rapamycin treatment in an older human cohort: immunological, physical performance, and cognitive effects. Exp Gerontol. 2018;105:53–69.
doi: 10.1016/j.exger.2017.12.026 pubmed: 29408453 pmcid: 5869166
Mannick JB, et al. TORC1 inhibition enhances immune function and reduces infections in the elderly. Sci Transl Med. 2018;10(449):eaaq1564.
doi: 10.1126/scitranslmed.aaq1564 pubmed: 29997249
Mannick JB, et al. mTOR inhibition improves immune function in the elderly. Sci Transl Med. 2014;6(268):268ra179.
doi: 10.1126/scitranslmed.3009892 pubmed: 25540326
Chung CL, et al. Topical rapamycin reduces markers of senescence and aging in human skin: an exploratory, prospective, randomized trial. Geroscience. 2019;41(6):861–9.
doi: 10.1007/s11357-019-00113-y pubmed: 31761958 pmcid: 6925069
Gundermann DM, et al. Activation of mTORC1 signaling and protein synthesis in human muscle following blood flow restriction exercise is inhibited by rapamycin. Am J Physiol Endocrinol Metab. 2014;306(10):E1198–204.
doi: 10.1152/ajpendo.00600.2013 pubmed: 24691032 pmcid: 4116405
Klawitter J, Nashan B, Christians U. Everolimus and sirolimus in transplantation-related but different. Expert Opin Drug Saf. 2015;14(7):1055–70.
doi: 10.1517/14740338.2015.1040388 pubmed: 25912929 pmcid: 6053318
Weichhart T. mTOR as regulator of lifespan, aging, and cellular senescence: a mini-review. Gerontology. 2018;64(2):127–34.
doi: 10.1159/000484629 pubmed: 29190625
Yoon MS. mTOR as a key regulator in maintaining skeletal muscle mass. Front Physiol. 2017;8:788.
doi: 10.3389/fphys.2017.00788 pubmed: 29089899 pmcid: 5650960
Beaudart C, et al. Assessment of muscle function and physical performance in daily clinical practice : a position paper endorsed by the European Society for Clinical and Economic Aspects of Osteoporosis, Osteoarthritis and Musculoskeletal Diseases (ESCEO). Calcif Tissue Int. 2019;105(1):1–14.
doi: 10.1007/s00223-019-00545-w pubmed: 30972475
Jones CJ, Rikli RE, Beam WC. A 30-s chair-stand test as a measure of lower body strength in community-residing older adults. Res Q Exerc Sport. 1999;70(2):113–9.
doi: 10.1080/02701367.1999.10608028 pubmed: 10380242
Cao ZB, et al. The effect of a 12-week combined exercise intervention program on physical performance and gait kinematics in community-dwelling elderly women. J Physiol Anthropol. 2007;26(3):325–32.
doi: 10.2114/jpa2.26.325 pubmed: 17641451
Islam MM, et al. Effects of combined sensory and muscular training on balance in Japanese older adults. Prev Med. 2004;39(6):1148–55.
doi: 10.1016/j.ypmed.2004.04.048 pubmed: 15539049
Julious SA. Sample size of 12 per group rule of thumb for a pilot study. Pharmaceutical Statistics. 2005;4:287–91.
doi: 10.1002/pst.185
Flachaire E. Bootstrapping heteroskedastic regression models: wild bootstrap vs. pairs bootstrap. Comput Stat Data Anal. 2005;49(2):361–76.
doi: 10.1016/j.csda.2004.05.018
Modugno L, Giannerini S. The wild bootstrap for multilevel models. Commun Stat Theory Methods. 2015;44(22):4812–25.
doi: 10.1080/03610926.2013.802807

Auteurs

Brad Stanfield (B)

Royal New Zealand College of General Practitioners, Wellington Central, Wellington, 6011, New Zealand. brad@drstanfield.com.
University of Auckland, Auckland, New Zealand. brad@drstanfield.com.

Matt Kaeberlein (M)

Optispan, Inc., Seattle, WA, USA.
Department of Oral Health Sciences, University of Washington, Seattle, WA, USA.

Brian Leroux (B)

Department of Oral Health Sciences, University of Washington, Seattle, WA, USA.
Department of Biostatistics, University of Washington, Seattle, WA, USA.

Julie Jones (J)

BioValeo, Wellington, New Zealand.

Ruth Lucas (R)

BioValeo, Wellington, New Zealand.

Bruce Arroll (B)

General Practice and Primary Health Care, University of Auckland, Auckland, New Zealand.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH