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Anna Majowicz
Anna Majowicz
Affiliations
Immunology Department, Spark Therapeutics, Inc., Philadelphia, Pennsylvania, USA.
Publications (3)
Complement System Response to Adeno-Associated Virus Vector Gene Therapy.
Human gene therapy
Avec:
Elizabeth Kropf
,
David M Markusic
,
Anna Majowicz
,
Federico Mingozzi
,
Klaudia Kuranda
Pre-existing humoral immunity and complement pathway contribute to immunogenicity of adeno-associated virus (AAV) vector in human blood.
Frontiers in immunology
Avec:
Corinne J Smith
,
Nikki Ross
,
Ali Kamal
,
Kevin Y Kim
,
Elizabeth Kropf
,
Pascal Deschatelets
,
Cedric Francois
,
William J Quinn
,
Inderpal Singh
,
Anna Majowicz
,
Federico Mingozzi
,
Klaudia Kuranda
Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs.
Molecular therapy. Methods & clinical development
Avec:
Anna Majowicz
,
Bart Nijmeijer
,
Margit H Lampen
,
Lisa Spronck
,
Martin de Haan
,
Harald Petry
,
Sander J van Deventer
,
Christian Meyer
,
Marco Tangelder
,
Valerie Ferreira
Réseau de co-auteurs
Elizabeth Kropf
2 collaborations
Federico Mingozzi
2 collaborations
Klaudia Kuranda
2 collaborations
David M Markusic
1 collaboration
Corinne J Smith
1 collaboration
Nikki Ross
1 collaboration
Ali Kamal
1 collaboration
Kevin Y Kim
1 collaboration
Pascal Deschatelets
1 collaboration
Cedric Francois
1 collaboration
William J Quinn
1 collaboration
Inderpal Singh
1 collaboration
Bart Nijmeijer
1 collaboration
Margit H Lampen
1 collaboration
Lisa Spronck
1 collaboration
Martin de Haan
1 collaboration
Harald Petry
1 collaboration
Sander J van Deventer
1 collaboration
Christian Meyer
1 collaboration
Marco Tangelder
1 collaboration
Valerie Ferreira
1 collaboration