IND-Enabling Studies for a Clinical Trial to Genetically Program a Persistent Cancer-Targeted Immune System.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
01 02 2019
Historique:
received: 27 03 2018
revised: 21 06 2018
accepted: 05 11 2018
pubmed: 10 11 2018
medline: 14 4 2020
entrez: 10 11 2018
Statut: ppublish

Résumé

To improve persistence of adoptively transferred T-cell receptor (TCR)-engineered T cells and durable clinical responses, we designed a clinical trial to transplant genetically-modified hematopoietic stem cells (HSCs) together with adoptive cell transfer of T cells both engineered to express an NY-ESO-1 TCR. Here, we report the preclinical studies performed to enable an investigational new drug (IND) application. HSCs transduced with a lentiviral vector expressing NY-ESO-1 TCR and the PET reporter/suicide gene HSV1-sr39TK and T cells transduced with a retroviral vector expressing NY-ESO-1 TCR were coadministered to myelodepleted HLA-A2/K TCR genetically modified and Coadministration of HSCs and T cells expressing an NY-ESO-1 TCR is safe in preclinical models. The results presented in this article led to the FDA approval of IND 17471.

Identifiants

pubmed: 30409823
pii: 1078-0432.CCR-18-0963
doi: 10.1158/1078-0432.CCR-18-0963
pmc: PMC6359988
mid: NIHMS1512381
doi:

Substances chimiques

Antigens, Neoplasm 0
CTAG1B protein, human 0
Drugs, Investigational 0
HLA-A2 Antigen 0
Membrane Proteins 0
Receptors, Antigen, T-Cell 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't Research Support, U.S. Gov't, Non-P.H.S.

Langues

eng

Sous-ensembles de citation

IM

Pagination

1000-1011

Subventions

Organisme : NCI NIH HHS
ID : R35 CA197633
Pays : United States
Organisme : NCI NIH HHS
ID : P30 CA016042
Pays : United States
Organisme : NIAID NIH HHS
ID : P30 AI028697
Pays : United States
Organisme : NHLBI NIH HHS
ID : P40 HL116242
Pays : United States
Organisme : NCI NIH HHS
ID : P01 CA168585
Pays : United States

Informations de copyright

©2018 American Association for Cancer Research.

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Auteurs

Cristina Puig-Saus (C)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California. aribas@mednet.ucla.edu cpuigsaus@mednet.ucla.edu.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Giulia Parisi (G)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Angel Garcia-Diaz (A)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Paige E Krystofinski (PE)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Salemiz Sandoval (S)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Ruixue Zhang (R)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Ameya S Champhekar (AS)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

James McCabe (J)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Gardenia C Cheung-Lau (GC)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Nhat A Truong (NA)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Agustin Vega-Crespo (A)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Marie Desiles S Komenan (MDS)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Jia Pang (J)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Mignonette H Macabali (MH)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Justin D Saco (JD)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Jeffrey L Goodwin (JL)

Division of Laboratory Animal Medicine (DLAM), Department of Medicine, DGSOM, UCLA, Los Angeles, California.

Brad Bolon (B)

GEMpath, Inc., Longmont, Colorado.

Christopher S Seet (CS)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.

Amelie Montel-Hagen (A)

Department of Pathology and Laboratory Medicine, DGSOM, UCLA, Los Angeles, California.

Gay M Crooks (GM)

Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.
Department of Pathology and Laboratory Medicine, DGSOM, UCLA, Los Angeles, California.
Division of Pediatric Hematology-Oncology, Department of Pediatrics, DGSOM, UCLA, Los Angeles, California.
Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, UCLA, Los Angeles, California.

Roger P Hollis (RP)

Department of Microbiology, Immunology and Molecular Genetics, UCLA, Los Angeles, California.

Beatriz Campo-Fernandez (B)

Department of Microbiology, Immunology and Molecular Genetics, UCLA, Los Angeles, California.

Daniela Bischof (D)

Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indiana University Vector Production Facility, Indianapolis, Indiana.

Kenneth Cornetta (K)

Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indiana University Vector Production Facility, Indianapolis, Indiana.

Eric H Gschweng (EH)

Department of Microbiology, Immunology and Molecular Genetics, UCLA, Los Angeles, California.

Celia Adelson (C)

Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, UCLA, Los Angeles, California.

Alexander Nguyen (A)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Lili Yang (L)

Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.
Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, UCLA, Los Angeles, California.
Department of Microbiology, Immunology and Molecular Genetics, UCLA, Los Angeles, California.

Owen N Witte (ON)

Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, UCLA, Los Angeles, California.
Department of Microbiology, Immunology and Molecular Genetics, UCLA, Los Angeles, California.
Department of Molecular and Medical Pharmacology, UCLA, Los Angeles, California.

David Baltimore (D)

Department of Biology and Biological Engineering, California Institute of Technology, Pasadena, California.

Begonya Comin-Anduix (B)

Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.
Division of Surgical Oncology, Department of Surgery, UCLA, Los Angeles, California.

Donald B Kohn (DB)

Department of Microbiology, Immunology and Molecular Genetics, UCLA, Los Angeles, California.
Department of Pediatrics, UCLA Children's Discovery and Innovation Institute, DGSOM, University of California, Los Angeles, California.

Xiaoyan Wang (X)

Statistics Core, Department of Medicine, UCLA, Los Angeles, California.

Paula Cabrera (P)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Paula J Kaplan-Lefko (PJ)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Beata Berent-Maoz (B)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.

Antoni Ribas (A)

Division of Hematology-Oncology, Department of Medicine, David Geffen School of Medicine (DGSOM), University of California, Los Angeles (UCLA), Los Angeles, California. aribas@mednet.ucla.edu cpuigsaus@mednet.ucla.edu.
Jonsson Comprehensive Cancer Center, UCLA, Los Angeles, California.
Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, UCLA, Los Angeles, California.
Department of Molecular and Medical Pharmacology, UCLA, Los Angeles, California.
Division of Surgical Oncology, Department of Surgery, UCLA, Los Angeles, California.

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