Combined Inhibition of DYRK1A, SMAD, and Trithorax Pathways Synergizes to Induce Robust Replication in Adult Human Beta Cells.


Journal

Cell metabolism
ISSN: 1932-7420
Titre abrégé: Cell Metab
Pays: United States
ID NLM: 101233170

Informations de publication

Date de publication:
05 03 2019
Historique:
received: 20 03 2018
revised: 03 08 2018
accepted: 30 11 2018
pmc-release: 05 03 2020
pubmed: 26 12 2018
medline: 12 5 2020
entrez: 25 12 2018
Statut: ppublish

Résumé

Small-molecule inhibitors of dual-specificity tyrosine-regulated kinase 1A (DYRK1A) induce human beta cells to proliferate, generating a labeling index of 1.5%-3%. Here, we demonstrate that combined pharmacologic inhibition of DYRK1A and transforming growth factor beta superfamily (TGFβSF)/SMAD signaling generates remarkable further synergistic increases in human beta cell proliferation (average labeling index, 5%-8%, and as high as 15%-18%), and increases in both mouse and human beta cell numbers. This synergy reflects activation of cyclins and cdks by DYRK1A inhibition, accompanied by simultaneous reductions in key cell-cycle inhibitors (CDKN1C and CDKN1A). The latter results from interference with the basal Trithorax- and SMAD-mediated transactivation of CDKN1C and CDKN1A. Notably, combined DYRK1A and TGFβ inhibition allows preservation of beta cell differentiated function. These beneficial effects extend from normal human beta cells and stem cell-derived human beta cells to those from people with type 2 diabetes, and occur both in vitro and in vivo.

Identifiants

pubmed: 30581122
pii: S1550-4131(18)30742-3
doi: 10.1016/j.cmet.2018.12.005
pmc: PMC6402958
mid: NIHMS1516423
pii:
doi:

Substances chimiques

KMT2A protein, human 0
Monoamine Oxidase Inhibitors 0
Smad Proteins 0
Transforming Growth Factor beta 0
Myeloid-Lymphoid Leukemia Protein 149025-06-9
Harmine 4FHH5G48T7
Histone-Lysine N-Methyltransferase EC 2.1.1.43
Protein-Tyrosine Kinases EC 2.7.10.1
Protein Serine-Threonine Kinases EC 2.7.11.1

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

638-652.e5

Subventions

Organisme : NIDDK NIH HHS
ID : UC4 DK104211
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK116873
Pays : United States
Organisme : NIDDK NIH HHS
ID : U24 DK098085
Pays : United States
Organisme : NIH HHS
ID : S10 OD018522
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK108905
Pays : United States
Organisme : NIDDK NIH HHS
ID : P60 DK020541
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK105015
Pays : United States
Organisme : NIDDK NIH HHS
ID : P30 DK020541
Pays : United States
Organisme : NIDDK NIH HHS
ID : P30 DK020593
Pays : United States

Commentaires et corrections

Type : CommentIn

Informations de copyright

Copyright © 2018 Elsevier Inc. All rights reserved.

Références

Dev Cell. 2012 Jul 17;23(1):21-34
pubmed: 22814600
Nat Genet. 2014 Feb;46(2):136-143
pubmed: 24413736
Diabetes. 2011 Nov;60(11):2892-902
pubmed: 21940781
Int J Oncol. 2014 Dec;45(6):2221-31
pubmed: 25270361
Genes Dev. 2009 Apr 15;23(8):975-85
pubmed: 19390090
Nephrol Dial Transplant. 2012 Oct;27(10):3686-91
pubmed: 23114895
Endocrinology. 2018 Sep 1;159(9):3143-3157
pubmed: 29514186
Genes Dev. 2009 Apr 15;23(8):906-11
pubmed: 19390085
Kidney Int. 2011 Jun;79(11):1236-43
pubmed: 21368745
Genes Dev. 2011 Apr 15;25(8):801-13
pubmed: 21498570
Nature. 2011 Oct 12;478(7369):349-55
pubmed: 21993628
Diabetologia. 2012 Mar;55(3):694-706
pubmed: 22120512
Diabetes Obes Metab. 2013 Jun;15(6):503-12
pubmed: 23121289
Science. 1997 Apr 18;276(5311):404-7
pubmed: 9103196
Cell. 2017 Sep 7;170(6):1184-1196.e24
pubmed: 28886385
Endocrinology. 2016 Apr;157(4):1348-56
pubmed: 26872091
Semin Cell Dev Biol. 2014 Aug;32:107-18
pubmed: 24503509
Diabetes. 2000 Aug;49(8):1325-33
pubmed: 10923633
Diabetes. 2004 Jan;53(1):149-59
pubmed: 14693709
Nat Rev Cancer. 2013 Aug;13(8):585-95
pubmed: 23842645
Diabetes. 2015 Oct;64(10):3485-98
pubmed: 26159177
Leuk Lymphoma. 2014 Feb;55(2):450-2
pubmed: 23682558
Aging Cell. 2017 Oct;16(5):1146-1154
pubmed: 28779511
Diabetes. 2008 Jun;57(6):1584-94
pubmed: 18334605
Cancer Sci. 2009 Nov;100(11):2133-42
pubmed: 19686287
J Biol Chem. 2010 Oct 8;285(41):31895-906
pubmed: 20696760
Nature. 2006 Sep 21;443(7109):345-9
pubmed: 16988714
J Clin Invest. 2014 Feb;124(2):670-4
pubmed: 24430183
Am J Physiol Endocrinol Metab. 2016 Nov 1;311(5):E859-E868
pubmed: 27624103
Diabetes. 2016 May;65(5):1208-18
pubmed: 26936960
J Med Chem. 2012 Nov 8;55(21):9312-30
pubmed: 22998443
Cell. 2014 Oct 9;159(2):428-39
pubmed: 25303535
Diabetes. 2016 Jul;65(7):2081-93
pubmed: 26993067
Nat Rev Endocrinol. 2015 Apr;11(4):201-12
pubmed: 25687999
Nat Commun. 2017 Oct 3;8(1):767
pubmed: 28974674
Diabetes. 2013 Jul;62(7):2450-9
pubmed: 23493570
Diabetes. 2012 May;61(5):969-75
pubmed: 22517647
Trends Endocrinol Metab. 2010 Jul;21(7):441-8
pubmed: 20382030
Proc Natl Acad Sci U S A. 2007 Jan 23;104(4):1348-53
pubmed: 17229845
J Biol Chem. 1994 Feb 18;269(7):4895-902
pubmed: 8106462
Diabetologia. 2013 Feb;56(2):350-8
pubmed: 23192693
Diabetes. 2015 Jun;64(6):1872-85
pubmed: 25999530
Proc Natl Acad Sci U S A. 2001 Jan 30;98(3):1118-23
pubmed: 11158604
Cell. 2012 Sep 14;150(6):1223-34
pubmed: 22980982
Diabetologia. 2014 Jan;57(1):157-66
pubmed: 24068386
PLoS One. 2009;4(4):e5011
pubmed: 19340297
J Clin Endocrinol Metab. 2012 Sep;97(9):3197-206
pubmed: 22745242
Cell Metab. 2016 Oct 11;24(4):616-626
pubmed: 27732837
Diabetes. 2018 Jan;67(1):26-35
pubmed: 28931519
Diabetes. 2014 Jan;63(1):224-36
pubmed: 24089514
Drug Des Devel Ther. 2015 Aug 10;9:4479-99
pubmed: 26309397
Invest New Drugs. 2014 Jun;32(3):555-60
pubmed: 24566706
Diabetes. 2016 Jun;65(6):1660-71
pubmed: 26953159
J Med Toxicol. 2017 Sep;13(3):245-248
pubmed: 27896660
Mol Cell Biol. 2003 Sep;23(17):6075-85
pubmed: 12917331
Nat Commun. 2015 Oct 26;6:8372
pubmed: 26496802
Proc Natl Acad Sci U S A. 2005 Oct 11;102(41):14659-64
pubmed: 16195383
Nat Commun. 2016 May 10;7:11463
pubmed: 27163171
Nat Med. 2015 Apr;21(4):383-8
pubmed: 25751815
Islets. 2014;6(5-6):e1017226
pubmed: 25833251
PLoS Biol. 2006 Feb;4(2):e39
pubmed: 16435884
Diabetes. 2013 Jul;62(7):2460-70
pubmed: 23493571
Trends Biochem Sci. 2015 Jun;40(6):296-308
pubmed: 25935112
Proc Natl Acad Sci U S A. 2014 Apr 1;111(13):E1211-20
pubmed: 24639504
Prog Neuropsychopharmacol Biol Psychiatry. 2012 Dec 3;39(2):263-72
pubmed: 22691716
Diabetes. 2009 Apr;58(4):882-93
pubmed: 19136653
J Clin Endocrinol Metab. 2016 Mar;101(3):1044-54
pubmed: 26713822
J Clin Invest. 2013 Nov;123(11):4849-58
pubmed: 24216481

Auteurs

Peng Wang (P)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Esra Karakose (E)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Hongtao Liu (H)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Ethan Swartz (E)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Courtney Ackeifi (C)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Viktor Zlatanic (V)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Jessica Wilson (J)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Bryan J González (BJ)

Naomi Berrie Diabetes Center, Columbia University, New York, NY 10032, USA.

Aaron Bender (A)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Karen K Takane (KK)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Lillian Ye (L)

Semma Therapeutics, Cambridge, MA 02142, USA.

George Harb (G)

Semma Therapeutics, Cambridge, MA 02142, USA.

Felicia Pagliuca (F)

Semma Therapeutics, Cambridge, MA 02142, USA.

Dirk Homann (D)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Dieter Egli (D)

Naomi Berrie Diabetes Center, Columbia University, New York, NY 10032, USA.

Carmen Argmann (C)

Department of Genetics and Genomic Sciences, Icahn Institute for Genomics and Multiscale Biology, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Donald K Scott (DK)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Adolfo Garcia-Ocaña (A)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA.

Andrew F Stewart (AF)

Diabetes, Obesity, and Metabolism Institute, Icahn School of Medicine at Mount Sinai, New York, NY 10029, USA. Electronic address: andrew.stewart@mssm.edu.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH