Absence of pathogenic mutations in CD59 in chronic inflammatory demyelinating polyradiculoneuropathy.


Journal

PloS one
ISSN: 1932-6203
Titre abrégé: PLoS One
Pays: United States
ID NLM: 101285081

Informations de publication

Date de publication:
2019
Historique:
received: 05 11 2018
accepted: 06 02 2019
entrez: 23 2 2019
pubmed: 23 2 2019
medline: 22 11 2019
Statut: epublish

Résumé

Mutations in CD59 cause CIDP-like polyneuropathy in children with inherited chronic hemolysis. We hypothesized that mutations in CD59 might be found in a subset of sporadic CIDP patients. 35 patients from two centers, fulfilling the EFNS/PNS diagnostic criteria for CIDP were included. CD59 coding region was amplified by PCR and Sanger sequenced. One rare variant was detected in a patient which resulted in a synonymous change and predicted to be neutral. Pathogenic variants were absent in our cohort. Our pilot study suggests that mutations in CD59 are absent in adult-onset sporadic CIDP.

Identifiants

pubmed: 30794663
doi: 10.1371/journal.pone.0212647
pii: PONE-D-18-31831
pmc: PMC6386293
doi:

Substances chimiques

CD59 Antigens 0
CD59 protein, human 101754-01-2

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

e0212647

Commentaires et corrections

Type : ErratumIn

Déclaration de conflit d'intérêts

LQ has provided expert testimony for Grifols, Genzyme and CSL Behring, received speaking honoraria from Biogen Spain and Roche and received research funds from Grifols (Spin Award) and LFB. This does not alter the authors' adherence to PLOS ONE policies on sharing data and materials.

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Auteurs

Lena Duchateau (L)

Memory Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.

Lorena Martín-Aguilar (L)

Neuromuscular Diseases Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.

Cinta Lleixà (C)

Neuromuscular Diseases Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.

Andrea Cortese (A)

IRCCS Mondino Foundation, Pavia, Italy.

Oriol Dols-Icardo (O)

Memory Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.
Centro para la Investigación Biomédica en Red en Enfermedades Neurodegenerativas (CIBERNED), Madrid, Spain.

Laura Cervera-Carles (L)

Memory Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.
Centro para la Investigación Biomédica en Red en Enfermedades Neurodegenerativas (CIBERNED), Madrid, Spain.

Elba Pascual-Goñi (E)

Neuromuscular Diseases Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.

Jordi Diaz-Manera (J)

Neuromuscular Diseases Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.
Centro para la Investigación Biomédica en Red en Enfermedades Raras (CIBERER), Madrid, Spain.

Ilaria Calegari (I)

IRCCS Mondino Foundation, Pavia, Italy.

Diego Franciotta (D)

IRCCS Mondino Foundation, Pavia, Italy.

Ricard Rojas-Garcia (R)

Neuromuscular Diseases Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.
Centro para la Investigación Biomédica en Red en Enfermedades Raras (CIBERER), Madrid, Spain.

Isabel Illa (I)

Neuromuscular Diseases Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.
Centro para la Investigación Biomédica en Red en Enfermedades Raras (CIBERER), Madrid, Spain.

Jordi Clarimon (J)

Memory Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.
Centro para la Investigación Biomédica en Red en Enfermedades Neurodegenerativas (CIBERNED), Madrid, Spain.

Luis Querol (L)

Neuromuscular Diseases Unit, Hospital de la Santa Creu i Sant Pau, Universitat Autònoma de Barcelona, Barcelona, Spain.
Centro para la Investigación Biomédica en Red en Enfermedades Raras (CIBERER), Madrid, Spain.

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Classifications MeSH