NMR solution structure of tricyclo-DNA containing duplexes: insight into enhanced thermal stability and nuclease resistance.


Journal

Nucleic acids research
ISSN: 1362-4962
Titre abrégé: Nucleic Acids Res
Pays: England
ID NLM: 0411011

Informations de publication

Date de publication:
21 05 2019
Historique:
accepted: 13 03 2019
revised: 12 03 2019
received: 08 12 2018
pubmed: 28 3 2019
medline: 26 11 2019
entrez: 28 3 2019
Statut: ppublish

Résumé

Tc-DNA is a conformationally constrained oligonucleotide analogue which shows significant increase in thermal stability when hybridized with RNA, DNA or tc-DNA. Remarkably, recent studies revealed that tc-DNA antisense oligonucleotides (AO) hold great promise for the treatment of Duchenne muscular dystrophy and spinal muscular atrophy. To date, no high-resolution structural data is available for fully modified tc-DNA duplexes and little is known about the origins of their enhanced thermal stability. Here, we report the structures of a fully modified tc-DNA oligonucleotide paired with either complementary RNA, DNA or tc-DNA. All three investigated duplexes maintain a right-handed helical structure with Watson-Crick base pairing and overall geometry intermediate between A- and B-type, but closer to A-type structures. All sugars of the tc-DNA and RNA residues adopt a North conformation whereas the DNA deoxyribose are found in a South-East-North conformation equilibrium. The conformation of the tc-DNA strand in the three determined structures is nearly identical and despite the different nature and local geometry of the complementary strand, the overall structures of the examined duplexes are very similar suggesting that the tc-DNA strand dominates the duplex structure.

Identifiants

pubmed: 30916334
pii: 5420530
doi: 10.1093/nar/gkz197
pmc: PMC6511864
doi:

Substances chimiques

Oligonucleotides 0
Deoxyribose 533-67-5
RNA 63231-63-0
DNA 9007-49-2

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

4872-4882

Informations de copyright

© The Author(s) 2019. Published by Oxford University Press on behalf of Nucleic Acids Research.

Références

J Comput Chem. 2005 Dec;26(16):1701-18
pubmed: 16211538
Phys Chem Chem Phys. 2010 Jul 28;12(28):7821-39
pubmed: 20574571
Mol Ther Nucleic Acids. 2017 Jun 16;7:20-30
pubmed: 28624195
Biopolymers. 1997;42(1):113-24
pubmed: 19350745
Nat Med. 2015 Mar;21(3):270-5
pubmed: 25642938
J Am Chem Soc. 2002 May 29;124(21):5993-6002
pubmed: 12022832
J Am Chem Soc. 2002 May 29;124(21):5974-82
pubmed: 12022830
Eur J Biochem. 1993 Jul 15;215(2):297-306
pubmed: 7688302
Nucleic Acids Res. 1987 Aug 11;15(15):6131-48
pubmed: 3627981
Biochemistry. 1995 Apr 18;34(15):4969-82
pubmed: 7711019
J Mol Biol. 1983 Dec 15;171(3):319-36
pubmed: 6317867
Chem Commun (Camb). 2008 Feb 21;(7):883-5
pubmed: 18253536
Nucleic Acid Ther. 2012 Apr;22(2):77-89
pubmed: 22352814
Chem Biol. 2000 Sep;7(9):719-31
pubmed: 10980452
Angew Chem Int Ed Engl. 2013 Nov 11;52(46):12065-8
pubmed: 24115468
Biochemistry. 1990 Mar 6;29(9):2357-68
pubmed: 2337605
Nucleic Acids Res. 2011 Apr;39(8):3482-95
pubmed: 21183463
Proc Natl Acad Sci U S A. 1982 Jul;79(13):4040-4
pubmed: 6955789
Nucleic Acids Res. 2010 Oct;38(19):6729-36
pubmed: 20530536
J Am Chem Soc. 2005 Mar 9;127(9):2937-43
pubmed: 15740130
Biochim Biophys Acta. 1999 Dec 10;1489(1):117-30
pubmed: 10807002
Nucleic Acids Res. 2002 Jul 1;30(13):2751-7
pubmed: 12087157
Biochemistry. 1998 Jan 6;37(1):73-80
pubmed: 9425027
Nucleic Acids Res. 2010 Apr;38(7):2498-511
pubmed: 20071751
Mol Ther Nucleic Acids. 2017 Jun 16;7:81-89
pubmed: 28624227
J Mol Biol. 1993 Oct 5;233(3):509-23
pubmed: 8411159
J Biomol NMR. 1995 Nov;6(3):277-93
pubmed: 8520220
Nucleic Acids Res. 1999 Jan 15;27(2):555-61
pubmed: 9862980
J Org Chem. 2015 Apr 3;80(7):3556-65
pubmed: 25767996
Trends Biotechnol. 2003 Feb;21(2):74-81
pubmed: 12573856
J Org Chem. 2012 May 18;77(10):4566-77
pubmed: 22551389
Biochemistry. 1993 Aug 3;32(30):7832-8
pubmed: 7688569
J Mol Biol. 1989 Oct 5;209(3):459-74
pubmed: 2479753
J Neuromuscul Dis. 2016 May 27;3(2):157-167
pubmed: 27854216
J Am Chem Soc. 2002 Feb 13;124(6):928-33
pubmed: 11829600
Org Lett. 2015 Apr 17;17(8):1950-3
pubmed: 25837683
Nucleic Acids Res. 2003 Oct 15;31(20):5858-67
pubmed: 14530434
Bioconjug Chem. 2004 May-Jun;15(3):449-57
pubmed: 15149171
J Med Chem. 1993 Apr 2;36(7):831-41
pubmed: 8464037
Chem Biodivers. 2010 Jan;7(1):60-89
pubmed: 20087997
Cell. 2005 Jul 1;121(7):1005-16
pubmed: 15989951
Q Rev Biophys. 1987 Aug;20(1-2):1-34
pubmed: 3324162
Mol Cell. 2007 Oct 26;28(2):264-76
pubmed: 17964265

Auteurs

Andrei Istrate (A)

Department of Chemistry and Biochemistry, University of Bern, Freiestrasse 3, Bern CH-3012, Switzerland.

Silke Johannsen (S)

Department of Chemistry, Winterthurerstrasse 190, University of Zürich, Zürich CH-8057, Switzerland.

Alena Istrate (A)

Department of Chemistry and Biochemistry, University of Bern, Freiestrasse 3, Bern CH-3012, Switzerland.

Roland K O Sigel (RKO)

Department of Chemistry, Winterthurerstrasse 190, University of Zürich, Zürich CH-8057, Switzerland.

Christian J Leumann (CJ)

Department of Chemistry and Biochemistry, University of Bern, Freiestrasse 3, Bern CH-3012, Switzerland.

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Classifications MeSH