ORVAL: a novel platform for the prediction and exploration of disease-causing oligogenic variant combinations.


Journal

Nucleic acids research
ISSN: 1362-4962
Titre abrégé: Nucleic Acids Res
Pays: England
ID NLM: 0411011

Informations de publication

Date de publication:
02 07 2019
Historique:
accepted: 09 05 2019
revised: 01 05 2019
received: 21 02 2019
pubmed: 31 5 2019
medline: 15 5 2020
entrez: 1 6 2019
Statut: ppublish

Résumé

A tremendous amount of DNA sequencing data is being produced around the world with the ambition to capture in more detail the mechanisms underlying human diseases. While numerous bioinformatics tools exist that allow the discovery of causal variants in Mendelian diseases, little to no support is provided to do the same for variant combinations, an essential task for the discovery of the causes of oligogenic diseases. ORVAL (the Oligogenic Resource for Variant AnaLysis), which is presented here, provides an answer to this problem by focusing on generating networks of candidate pathogenic variant combinations in gene pairs, as opposed to isolated variants in unique genes. This online platform integrates innovative machine learning methods for combinatorial variant pathogenicity prediction with visualization techniques, offering several interactive and exploratory tools, such as pathogenic gene and protein interaction networks, a ranking of pathogenic gene pairs, as well as visual mappings of the cellular location and pathway information. ORVAL is the first web-based exploration platform dedicated to identifying networks of candidate pathogenic variant combinations with the sole ambition to help in uncovering oligogenic causes for patients that cannot rely on the classical disease analysis tools. ORVAL is available at https://orval.ibsquare.be.

Identifiants

pubmed: 31147699
pii: 5506854
doi: 10.1093/nar/gkz437
pmc: PMC6602484
doi:

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

W93-W98

Informations de copyright

© The Author(s) 2019. Published by Oxford University Press on behalf of Nucleic Acids Research.

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Auteurs

Alexandre Renaux (A)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Machine Learning Group, Université Libre de Bruxelles, 1050 Brussels, Belgium.
Artificial Intelligence lab, Vrije Universiteit Brussel, 1050 Brussels, Belgium.

Sofia Papadimitriou (S)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Machine Learning Group, Université Libre de Bruxelles, 1050 Brussels, Belgium.
Artificial Intelligence lab, Vrije Universiteit Brussel, 1050 Brussels, Belgium.

Nassim Versbraegen (N)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Machine Learning Group, Université Libre de Bruxelles, 1050 Brussels, Belgium.

Charlotte Nachtegael (C)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Machine Learning Group, Université Libre de Bruxelles, 1050 Brussels, Belgium.

Simon Boutry (S)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Laboratory of Human Molecular Genetics, de Duve Institute, UCLouvain, 1200 Brussels, Belgium.

Ann Nowé (A)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Artificial Intelligence lab, Vrije Universiteit Brussel, 1050 Brussels, Belgium.

Guillaume Smits (G)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Hôpital Universitaire des Enfants Reine Fabiola, 1020 Brussels, Belgium.
Center of Human Genetics, Hôpital Erasme, 1070 Brussels, Belgium.

Tom Lenaerts (T)

Interuniversity Institute of Bioinformatics in Brussels, Université Libre de Bruxelles-Vrije Universiteit Brussel, 1050 Brussels, Belgium.
Machine Learning Group, Université Libre de Bruxelles, 1050 Brussels, Belgium.
Artificial Intelligence lab, Vrije Universiteit Brussel, 1050 Brussels, Belgium.

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Classifications MeSH