Tubular aggregate myopathy and Stormorken syndrome: Mutation spectrum and genotype/phenotype correlation.


Journal

Human mutation
ISSN: 1098-1004
Titre abrégé: Hum Mutat
Pays: United States
ID NLM: 9215429

Informations de publication

Date de publication:
01 2020
Historique:
received: 09 05 2019
revised: 29 07 2019
accepted: 21 08 2019
pubmed: 27 8 2019
medline: 20 5 2021
entrez: 27 8 2019
Statut: ppublish

Résumé

Calcium (Ca

Identifiants

pubmed: 31448844
doi: 10.1002/humu.23899
doi:

Substances chimiques

Biomarkers 0
Neoplasm Proteins 0
ORAI1 Protein 0
STIM1 protein, human 0
Stromal Interaction Molecule 1 0
Calcium SY7Q814VUP

Types de publication

Journal Article Research Support, Non-U.S. Gov't Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

17-37

Informations de copyright

© 2019 Wiley Periodicals, Inc.

Auteurs

Gilles Morin (G)

Clinical Genetics, Amiens University Hospital, Amiens, France.
University of Picardy Jules Verne, EA 4666, Amiens, France.
Department of translational medicine and Neurogenetics, Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), Illkirch, France.

Valérie Biancalana (V)

Department of translational medicine and Neurogenetics, Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), Illkirch, France.
Inserm U1258, Illkirch, France.
CNRS UMR7104, Illkirch, France.
Strasbourg University, Illkirch, France.
Laboratoire Diagnostic Génétique, CHRU, Strasbourg, France.

Andoni Echaniz-Laguna (A)

Department of Neurology, APHP, CHU de Bicêtre, Le Kremlin Bicêtre, France.
French National Reference Center for Rare Neuropathies (NNERF), Le Kremlin Bicêtre, France.
Inserm U1195 & Paris-Sud University, Le Kremlin Bicêtre, France.

Jean-Baptiste Noury (JB)

Department of Neurology, CHRU Cavale Blanche, Brest, France.

Xavière Lornage (X)

Department of translational medicine and Neurogenetics, Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), Illkirch, France.
Inserm U1258, Illkirch, France.
CNRS UMR7104, Illkirch, France.
Strasbourg University, Illkirch, France.

Maurizio Moggio (M)

Neuromuscular and Rare Diseases Unit, Department of Neuroscience, Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Milan, Italy.

Michela Ripolone (M)

Neuromuscular and Rare Diseases Unit, Department of Neuroscience, Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Milan, Italy.

Raffaella Violano (R)

Neuromuscular and Rare Diseases Unit, Department of Neuroscience, Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Milan, Italy.

Pascale Marcorelles (P)

Department of Pathology - EA 4685 LNB, CHRU Morvan, Brest, France.

Denis Maréchal (D)

Department of Neurology, CHRU Cavale Blanche, Brest, France.

Florence Renaud (F)

Department of Pathology, Lille University Hospital, Lille, France.

Claude-Alain Maurage (CA)

Department of Pathology, Lille University Hospital, Lille, France.

Céline Tard (C)

CHU Lille, Inserm U1171, Service de neurologie, Centre de Référence des Maladies Neuromusculaires Nord Est Ile-de-France, Lille University, Lille, France.

Jean-Marie Cuisset (JM)

Service de Neuropédiatrie, CHRU de Lille, Lille, France.

Jocelyn Laporte (J)

Department of translational medicine and Neurogenetics, Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), Illkirch, France.
Inserm U1258, Illkirch, France.
CNRS UMR7104, Illkirch, France.
Strasbourg University, Illkirch, France.

Johann Böhm (J)

Department of translational medicine and Neurogenetics, Institut de Génétique et de Biologie Moléculaire et Cellulaire (IGBMC), Illkirch, France.
Inserm U1258, Illkirch, France.
CNRS UMR7104, Illkirch, France.
Strasbourg University, Illkirch, France.

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Classifications MeSH