Mosaicism for KCNJ5 Causing Early-Onset Primary Aldosteronism due to Bilateral Adrenocortical Hyperplasia.


Journal

American journal of hypertension
ISSN: 1941-7225
Titre abrégé: Am J Hypertens
Pays: United States
ID NLM: 8803676

Informations de publication

Date de publication:
22 02 2020
Historique:
received: 23 07 2019
revised: 19 09 2019
accepted: 18 10 2019
pubmed: 23 10 2019
medline: 22 12 2020
entrez: 23 10 2019
Statut: ppublish

Résumé

Somatic variants in KCNJ5 are the most common cause of primary aldosteronism (PA). There are few patients with PA in whom the disease is caused by germline variants in the KCNJ5 potassium channel gene (familial hyperaldosteronism type III-FH-III). A 5-year-old patient who developed hypertension due to bilateral adrenocortical hyperplasia (BAH) causing PA had negative peripheral DNA testing for any known genetic causes of PA. He was treated medically with adequate control of his PA but by the third decade of his life, due to worsening renal function, he underwent bilateral adrenalectomy. Focused exome sequencing in multiple nodules of his BAH uncovered a "hot-spot" pathogenic KCNJ5 variant, while repeated Sanger sequencing showed no detectable DNA defects in peripheral blood and other tissues. However, whole exome, "deep" sequencing revealed that 0.23% of copies of germline DNA did in fact carry the same KCNJ5 variant that was present in the adrenocortical nodules, suggesting low level germline mosaicism for this PA-causing KCNJ5 defect. Thus, this patient represents a unique case of BAH due to a mosaic KCNJ5 defect. Undoubtedly, his milder PA compared with other known cases of FH-III, was due to his mosaicism. This case has a number of implications for the prognosis, treatment, and counseling of the many patients with PA due to BAH that are seen in hypertension clinics.

Sections du résumé

BACKGROUND
Somatic variants in KCNJ5 are the most common cause of primary aldosteronism (PA). There are few patients with PA in whom the disease is caused by germline variants in the KCNJ5 potassium channel gene (familial hyperaldosteronism type III-FH-III).
METHODS
A 5-year-old patient who developed hypertension due to bilateral adrenocortical hyperplasia (BAH) causing PA had negative peripheral DNA testing for any known genetic causes of PA. He was treated medically with adequate control of his PA but by the third decade of his life, due to worsening renal function, he underwent bilateral adrenalectomy.
RESULTS
Focused exome sequencing in multiple nodules of his BAH uncovered a "hot-spot" pathogenic KCNJ5 variant, while repeated Sanger sequencing showed no detectable DNA defects in peripheral blood and other tissues. However, whole exome, "deep" sequencing revealed that 0.23% of copies of germline DNA did in fact carry the same KCNJ5 variant that was present in the adrenocortical nodules, suggesting low level germline mosaicism for this PA-causing KCNJ5 defect.
CONCLUSIONS
Thus, this patient represents a unique case of BAH due to a mosaic KCNJ5 defect. Undoubtedly, his milder PA compared with other known cases of FH-III, was due to his mosaicism. This case has a number of implications for the prognosis, treatment, and counseling of the many patients with PA due to BAH that are seen in hypertension clinics.

Identifiants

pubmed: 31637427
pii: 5601961
doi: 10.1093/ajh/hpz172
pmc: PMC8204147
doi:

Substances chimiques

G Protein-Coupled Inwardly-Rectifying Potassium Channels 0
KCNJ5 protein, human 0

Types de publication

Case Reports Research Support, N.I.H., Intramural

Langues

eng

Sous-ensembles de citation

IM

Pagination

124-130

Subventions

Organisme : Intramural NIH HHS
ID : Z01 HD008720
Pays : United States

Informations de copyright

© American Journal of Hypertension, Ltd 2019. All rights reserved. For Permissions, please email: journals.permissions@oup.com.

Références

Mol Cell Endocrinol. 2014 Apr 5;386(1-2):85-91
pubmed: 24012779
J Med Genet. 2000 Nov;37(11):831-5
pubmed: 11073536
J Clin Endocrinol Metab. 2015 Jan;100(1):E114-8
pubmed: 25322277
Trends Genet. 2015 Jul;31(7):382-92
pubmed: 25910407
Am J Med Genet C Semin Med Genet. 2014 Dec;166C(4):397-405
pubmed: 25424979
J Clin Endocrinol Metab. 2016 Mar;101(3):999-1007
pubmed: 26765578
J Clin Endocrinol Metab. 2018 Oct 1;103(10):3869-3876
pubmed: 30085035
N Engl J Med. 2012 Sep 6;367(10):922-30
pubmed: 22931260
Horm Metab Res. 2015 Dec;47(13):941-6
pubmed: 26445452
Genome Med. 2016 Oct 5;8(1):100
pubmed: 27716394
Endocr Relat Cancer. 2016 Oct;23(10):R437-54
pubmed: 27485459
Nat Genet. 2013 Apr;45(4):440-4, 444e1-2
pubmed: 23416519
J Mol Diagn. 2016 May;18(3):446-453
pubmed: 26944031
Endocr Rev. 2017 Dec 1;38(6):516-537
pubmed: 28973103
Mol Cell Endocrinol. 2017 Feb 5;441:134-139
pubmed: 27514282
J Hum Hypertens. 2017 Dec;31(12):776-781
pubmed: 28447626
Nat Genet. 2018 Mar;50(3):349-354
pubmed: 29403011
Science. 2011 Feb 11;331(6018):768-72
pubmed: 21311022
Endocr Relat Cancer. 2012 May 03;19(3):255-60
pubmed: 22323562
Endocr Relat Cancer. 2017 Oct;24(10):531-541
pubmed: 28747387
Nat Genet. 2013 Sep;45(9):1050-4
pubmed: 23913001
Nat Rev Genet. 2017 Feb;18(2):128-142
pubmed: 27941868
Genome Res. 2017 Oct;27(10):1704-1714
pubmed: 28855261
J Clin Endocrinol Metab. 2014 Feb;99(2):E369-73
pubmed: 24276449
Hypertension. 2015 Nov;66(5):1014-22
pubmed: 26351028

Auteurs

Andrea G Maria (AG)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.

Mari Suzuki (M)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.
National Institute of Diabetes and Digestive and Kidney Disorders, Bethesda, Maryland, USA.

Annabel Berthon (A)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.

Crystal Kamilaris (C)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.

Andrew Demidowich (A)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.

Justin Lack (J)

NIAID Collaborative Bioinformatics Resource (NCBR), National Institute of Allergy and Infectious Disease, Frederick, Maryland, USA.
Advanced Biomedical Computational Science, Frederick National Laboratory for Cancer Research, Frederick, Maryland, USA.

Mihail Zilbermint (M)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.
Division of Endocrinology, Diabetes, and Metabolism, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.
Johns Hopkins Community Physicians at Suburban Hospital, Bethesda, Maryland, USA.

Fady Hannah-Shmouni (F)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.

Fabio R Faucz (FR)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.

Constantine A Stratakis (CA)

Section on Genetics & Endocrinology, The Eunice Kennedy Shriver National Institute of Child Health and Human Development, Bethesda, Maryland, USA.

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