Congenital Generalized Lipoatrophy (Berardinelli-Seip Syndrome) Type 1: Description of Novel


Journal

Frontiers in endocrinology
ISSN: 1664-2392
Titre abrégé: Front Endocrinol (Lausanne)
Pays: Switzerland
ID NLM: 101555782

Informations de publication

Date de publication:
2020
Historique:
received: 21 10 2019
accepted: 21 01 2020
entrez: 3 3 2020
pubmed: 3 3 2020
medline: 3 3 2020
Statut: epublish

Résumé

Berardinelli-Seip congenital lipoatrophy (BSCL) is characterized by near total fat atrophy, associated with the progressive development of metabolic complications. BSCL type 1 (BSCL1) is caused by mutations in

Identifiants

pubmed: 32117065
doi: 10.3389/fendo.2020.00039
pmc: PMC7034310
doi:

Substances chimiques

Codon, Nonsense 0
Acyltransferases EC 2.3.-
2-acylglycerophosphate acyltransferase EC 2.3.1.52

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Pagination

39

Informations de copyright

Copyright © 2020 Ceccarini, Magno, Pelosini, Ferrari, Sessa, Scabia, Maffei, Jéru, Lascols, Vigouroux and Santini.

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Auteurs

Giovanni Ceccarini (G)

Obesity and Lipodystrophy Center at Endocrinology Unit, University Hospital of Pisa, Pisa, Italy.

Silvia Magno (S)

Obesity and Lipodystrophy Center at Endocrinology Unit, University Hospital of Pisa, Pisa, Italy.

Caterina Pelosini (C)

Obesity and Lipodystrophy Center at Endocrinology Unit, University Hospital of Pisa, Pisa, Italy.
Chemistry and Endocrinology Laboratory at University Hospital of Pisa, Pisa, Italy.

Federica Ferrari (F)

Obesity and Lipodystrophy Center at Endocrinology Unit, University Hospital of Pisa, Pisa, Italy.

Maria Rita Sessa (MR)

Chemistry and Endocrinology Laboratory at University Hospital of Pisa, Pisa, Italy.

Gaia Scabia (G)

Obesity and Lipodystrophy Center at Endocrinology Unit, University Hospital of Pisa, Pisa, Italy.
Institute of Clinical Physiology, National Research Council, Pisa, Italy.

Margherita Maffei (M)

Obesity and Lipodystrophy Center at Endocrinology Unit, University Hospital of Pisa, Pisa, Italy.
Institute of Clinical Physiology, National Research Council, Pisa, Italy.

Isabelle Jéru (I)

Sorbonne Université, Inserm UMR_S 938, Centre de Recherche Saint-Antoine, Institut Hospitalo-Universitaire de Cardio-métabolisme et Nutrition (ICAN), Paris, France.
Assistance Publique-Hôpitaux de Paris, Hôpital Saint-Antoine, Laboratoire Commun de Biologie et Génétique Moléculaires, Paris, France.

Olivier Lascols (O)

Sorbonne Université, Inserm UMR_S 938, Centre de Recherche Saint-Antoine, Institut Hospitalo-Universitaire de Cardio-métabolisme et Nutrition (ICAN), Paris, France.
Assistance Publique-Hôpitaux de Paris, Hôpital Saint-Antoine, Laboratoire Commun de Biologie et Génétique Moléculaires, Paris, France.

Corinne Vigouroux (C)

Sorbonne Université, Inserm UMR_S 938, Centre de Recherche Saint-Antoine, Institut Hospitalo-Universitaire de Cardio-métabolisme et Nutrition (ICAN), Paris, France.
Assistance Publique-Hôpitaux de Paris, Hôpital Saint-Antoine, Laboratoire Commun de Biologie et Génétique Moléculaires, Paris, France.
Assistance Publique-Hôpitaux de Paris, Hôpital Saint-Antoine, Centre National de Référence des Pathologies Rares de l'Insulino-Sécrétion et de l'Insulino-Sensibilité (PRISIS), Service d'Endocrinologie, Diabétologie et Endocrinologie de la Reproduction, Paris, France.

Ferruccio Santini (F)

Obesity and Lipodystrophy Center at Endocrinology Unit, University Hospital of Pisa, Pisa, Italy.

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Classifications MeSH