A new case with Hermansky-Pudlak syndrome type 9, a rare cause of syndromic albinism with severe defect of platelets dense bodies.


Journal

Platelets
ISSN: 1369-1635
Titre abrégé: Platelets
Pays: England
ID NLM: 9208117

Informations de publication

Date de publication:
03 Apr 2021
Historique:
pubmed: 5 4 2020
medline: 8 10 2021
entrez: 5 4 2020
Statut: ppublish

Résumé

Hermansky-Pudlak syndrome (HPS) is a rare form of syndromic oculocutaneous albinism caused by disorders in lysosome-related organelles. Ten genes are associated with different forms of HPS. HPS type 9 (HPS-9) is caused by biallelic variants of

Identifiants

pubmed: 32245340
doi: 10.1080/09537104.2020.1742315
doi:

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

420-423

Auteurs

Vincent Michaud (V)

Service Génétique Médicale, CHU Bordeaux, Bordeaux, France.

Mathieu Fiore (M)

Service d'Hématologie Biologique, Centre de Référence des Pathologies Plaquettaires, CHU Bordeaux, Bordeaux, France.

Valentine Coste (V)

Service d'Ophtalmologie, CHU Bordeaux, Bordeaux, France.

Yoann Huguenin (Y)

Centre de Ressources et de Compétences des Maladies Hémorragiques Constitutionnelles, CHU Bordeaux, Bordeaux, France.

Jean-Claude Bordet (JC)

Laboratoire d'Hématologie, CHU Lyon, Lyon, France.

Claudio Plaisant (C)

Service Génétique Médicale, CHU Bordeaux, Bordeaux, France.

Eulalie Lasseaux (E)

Service Génétique Médicale, CHU Bordeaux, Bordeaux, France.

Fanny Morice-Picard (F)

Service de Dermatologie Pédiatrique, CHU Bordeaux, Bordeaux, France.

Benoit Arveiler (B)

Service Génétique Médicale, CHU Bordeaux, Bordeaux, France.
INSERM U1211, Maladies Rares, Génétique et Métabolisme, Université de Bordeaux, Bordeaux, France.

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Classifications MeSH