A new case of Greenberg dysplasia and literature review suggest that Greenberg dysplasia, dappled diaphyseal dysplasia, and Astley-Kendall dysplasia are allelic disorders.


Journal

Molecular genetics & genomic medicine
ISSN: 2324-9269
Titre abrégé: Mol Genet Genomic Med
Pays: United States
ID NLM: 101603758

Informations de publication

Date de publication:
06 2020
Historique:
received: 28 01 2020
accepted: 30 01 2020
pubmed: 19 4 2020
medline: 14 4 2021
entrez: 19 4 2020
Statut: ppublish

Résumé

Greenberg dysplasia is a rare, autosomal recessive, prenatal lethal bone dysplasia caused by biallelic pathogenic variants in the lamin B receptor (LBR) gene. Pathogenic variants in LBR are also associated with Pelger-Huët anomaly, an autosomal dominant benign abnormality of the nuclear shape and chromatin organization of blood granulocytes, and Pelger-Huët anomaly with variable skeletal anomalies, a mild, regressing to moderate-severe autosomal recessive condition. Conditions with abnormal sterol metabolism and different genetic basis have clinical and radiographic features similar to Greenberg dysplasia, for example X-linked dominant chondrodysplasia punctata, Conradi-Hünermann type, and CHILD syndrome, and other conditions with unknown genetic etiology display very similar features, for example, dappled diaphyseal dysplasia and Astley-Kendall dysplasia. We present a fetus with typical clinical and radiographic features of Greenberg dysplasia, and review the literature. Genetic testing confirmed the diagnosis Greenberg dysplasia: homozygosity for a pathogenic variant in LBR. Comparing the clinical and radiographic phenotypes of Greenberg dysplasia, dappled diaphyseal dysplasia, and Astley-Kendall dysplasia, we suggest that these are allelic disorders.

Sections du résumé

BACKGROUND
Greenberg dysplasia is a rare, autosomal recessive, prenatal lethal bone dysplasia caused by biallelic pathogenic variants in the lamin B receptor (LBR) gene. Pathogenic variants in LBR are also associated with Pelger-Huët anomaly, an autosomal dominant benign abnormality of the nuclear shape and chromatin organization of blood granulocytes, and Pelger-Huët anomaly with variable skeletal anomalies, a mild, regressing to moderate-severe autosomal recessive condition. Conditions with abnormal sterol metabolism and different genetic basis have clinical and radiographic features similar to Greenberg dysplasia, for example X-linked dominant chondrodysplasia punctata, Conradi-Hünermann type, and CHILD syndrome, and other conditions with unknown genetic etiology display very similar features, for example, dappled diaphyseal dysplasia and Astley-Kendall dysplasia.
METHODS
We present a fetus with typical clinical and radiographic features of Greenberg dysplasia, and review the literature.
RESULTS
Genetic testing confirmed the diagnosis Greenberg dysplasia: homozygosity for a pathogenic variant in LBR.
CONCLUSION
Comparing the clinical and radiographic phenotypes of Greenberg dysplasia, dappled diaphyseal dysplasia, and Astley-Kendall dysplasia, we suggest that these are allelic disorders.

Identifiants

pubmed: 32304187
doi: 10.1002/mgg3.1173
pmc: PMC7284023
doi:

Substances chimiques

Receptors, Cytoplasmic and Nuclear 0

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

e1173

Informations de copyright

© 2020 The Authors. Molecular Genetics & Genomic Medicine published by Wiley Periodicals, Inc.

Références

Am J Hum Genet. 2003 Apr;72(4):1013-7
pubmed: 12618959
Elife. 2016 Jun 23;5:
pubmed: 27336722
Nat Genet. 1999 Jul;22(3):291-4
pubmed: 10391219
Am J Med Genet. 1988 Mar;29(3):623-32
pubmed: 3377005
Am J Med Genet A. 2015 Dec;167A(12):2869-92
pubmed: 26394607
J Med Genet. 1998 Jun;35(6):505-7
pubmed: 9643294
Mol Genet Genomic Med. 2020 Jun;8(6):e1173
pubmed: 32304187
Prenat Diagn. 2008 Apr;28(4):309-12
pubmed: 18382993
Bone. 2019 Mar;120:354-363
pubmed: 30448303
Rofo. 1989 Feb;150(2):228-9
pubmed: 2537527
Am J Obstet Gynecol. 2018 Dec;219(6):545-562
pubmed: 30048634
Nucleus. 2010 Jul-Aug;1(4):319-24
pubmed: 21327079
Prenat Diagn. 2000 Dec;20(12):1008-11
pubmed: 11113916
Am J Med Genet A. 2015 Jan;167A(1):159-63
pubmed: 25348816
Am J Med Genet A. 2019 Feb;179(2):306-311
pubmed: 30561119
Pediatr Radiol. 1989;19(4):253-7
pubmed: 2748234
Am J Med Genet. 1993 Aug 15;47(2):272-7
pubmed: 8213919
Nat Genet. 2002 Aug;31(4):410-4
pubmed: 12118250
J Med Genet. 2003 Dec;40(12):e129
pubmed: 14684697
Am J Med Genet A. 2013 Aug;161A(8):2066-73
pubmed: 23824842
Nucleus. 2010 Jul-Aug;1(4):354-66
pubmed: 21327084
Ann Radiol (Paris). 1980 Feb;23(2):121-3
pubmed: 7189652
Biochim Biophys Acta. 2000 Dec 15;1529(1-3):357-73
pubmed: 11111102
Hum Mol Genet. 2003 Apr 1;12 Spec No 1:R75-88
pubmed: 12668600

Auteurs

Pernille A Gregersen (PA)

Department of Clinical Genetics, Aarhus University Hospital, Aarhus, Denmark.
Pediatrics and Adolescent Medicine, Centre for Rare Diseases, Aarhus University Hospital, Aarhus, Denmark.
Victorian Clinical Genetics Services, The Royal Children's Hospital, Melbourne, VIC, Australia.

Victoria McKay (V)

Department of Clinical Genetics, Merseyside and Cheshire Regional Clinical Genetics Service, Liverpool Women's NHS Foundation Trust, Liverpool, UK.

Maie Walsh (M)

Victorian Clinical Genetics Services, The Royal Children's Hospital, Melbourne, VIC, Australia.
Victorian Clinical Genetics Services, Royal Melbourne Hospital, Melbourne, VIC, Australia.

Erica Brown (E)

Victorian Clinical Genetics Services, Royal Women's Hospital, Melbourne, VIC, Australia.

George McGillivray (G)

Victorian Clinical Genetics Services, The Royal Children's Hospital, Melbourne, VIC, Australia.
Victorian Clinical Genetics Services, Royal Women's Hospital, Melbourne, VIC, Australia.
Murdoch Children's Research Institute, University of Melbourne, Parkville, VIC, Australia.

Ravi Savarirayan (R)

Victorian Clinical Genetics Services, The Royal Children's Hospital, Melbourne, VIC, Australia.
Murdoch Children's Research Institute, University of Melbourne, Parkville, VIC, Australia.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH