PKU dietary handbook to accompany PKU guidelines.

Diet Guidelines PKU Phenylketonuria Recommendations Treatment

Journal

Orphanet journal of rare diseases
ISSN: 1750-1172
Titre abrégé: Orphanet J Rare Dis
Pays: England
ID NLM: 101266602

Informations de publication

Date de publication:
30 06 2020
Historique:
received: 09 09 2019
accepted: 04 05 2020
entrez: 2 7 2020
pubmed: 2 7 2020
medline: 22 6 2021
Statut: epublish

Résumé

Phenylketonuria (PKU) is an autosomal recessive inborn error of phenylalanine metabolism caused by deficiency in the enzyme phenylalanine hydroxylase that converts phenylalanine into tyrosine. In 2017 the first European PKU Guidelines were published. These guidelines contained evidence based and/or expert opinion recommendations regarding diagnosis, treatment and care for patients with PKU of all ages. This manuscript is a supplement containing the practical application of the dietary treatment. This handbook can support dietitians, nutritionists and physicians in starting, adjusting and maintaining dietary treatment.

Sections du résumé

BACKGROUND
Phenylketonuria (PKU) is an autosomal recessive inborn error of phenylalanine metabolism caused by deficiency in the enzyme phenylalanine hydroxylase that converts phenylalanine into tyrosine.
MAIN BODY
In 2017 the first European PKU Guidelines were published. These guidelines contained evidence based and/or expert opinion recommendations regarding diagnosis, treatment and care for patients with PKU of all ages. This manuscript is a supplement containing the practical application of the dietary treatment.
CONCLUSION
This handbook can support dietitians, nutritionists and physicians in starting, adjusting and maintaining dietary treatment.

Identifiants

pubmed: 32605583
doi: 10.1186/s13023-020-01391-y
pii: 10.1186/s13023-020-01391-y
pmc: PMC7329487
doi:

Substances chimiques

Tyrosine 42HK56048U
Phenylalanine 47E5O17Y3R
Phenylalanine Hydroxylase EC 1.14.16.1

Types de publication

Journal Article Research Support, Non-U.S. Gov't Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

171

Commentaires et corrections

Type : ErratumIn

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Auteurs

A MacDonald (A)

Dietetic Department, Birmingham Children's Hospital, Birmingham, UK.

A M J van Wegberg (AMJ)

Division of Metabolic Diseases, Beatrix Children's Hospital, University Medical Centre Groningen, University of Groningen, Hanzeplein 1, 9700, RB, Groningen, The Netherlands.

K Ahring (K)

Department of PKU, Kennedy Centre, Glostrup, Denmark.

S Beblo (S)

Department of Women and Child Health, Center for Pediatric Research Leipzig, Hospital for Children and Adolescents, University Hospitals, Leipzig, Germany.

A Bélanger-Quintana (A)

Metabolic Diseases Unit, Department of Paediatrics, Hospital Ramon y Cajal Madrid, Madrid, Spain.

A Burlina (A)

Division of Inherited Metabolic Diseases, Department of Paediatrics, University Hospital of Padova, Padova, Italy.

J Campistol (J)

Neuropaediatrics Department, Hospital Sant Joan de Déu, Universitat de Barcelona, Barcelona, Spain.

T Coşkun (T)

Hacettepe University Faculty of Medicine, Ankara, Turkey.

F Feillet (F)

Department of Paediatrics, Hôpital d'Enfants Brabois, CHU Nancy, Vandoeuvre les Nancy, France.

M Giżewska (M)

Department of Paediatrics, Endocrinology, Diabetology, Metabolic Diseases and Cardiology of the Developmental Age, Pomeranian Medical University, Szczecin, Poland.

S C Huijbregts (SC)

Department of Clinical Child and Adolescent Studies-Neurodevelopmental Disorders, Faculty of Social Sciences, Leiden University, Leiden, The Netherlands.

V Leuzzi (V)

Department of Paediatrics, Child Neurology and Psychiatry, Sapienza University of Rome, Via dei Sabelli 108, 00185, Rome, Italy.

F Maillot (F)

CHRU de Tours, Université François Rabelais, INSERM U1069, Tours, France.

A C Muntau (AC)

University Children's Hospital, University Medical Centre Hamburg-Eppendorf, 20246, Hamburg, Germany.

J C Rocha (JC)

Nutrition & Metabolism, NOVA Medical School, Faculdade de Ciências Médicas, Universidade Nova de Lisboa, Lisbon, Portugal. Centre for Health Technology and Services Research (CINTESIS), Porto, Portugal.

C Romani (C)

School of Life and Health Sciences, Aston University, Birmingham, UK.

F Trefz (F)

Department of Paediatrics, University of Heidelberg, Heidelberg, Germany.

F J van Spronsen (FJ)

Division of Metabolic Diseases, Beatrix Children's Hospital, University Medical Centre Groningen, University of Groningen, Hanzeplein 1, 9700, RB, Groningen, The Netherlands. f.j.van.spronsen@umcg.nl.

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Classifications MeSH