Osimertinib in advanced EGFR-T790M mutation-positive non-small cell lung cancer patients treated within the Special Use Medication Program in Spain: OSIREX-Spanish Lung Cancer Group.


Journal

BMC cancer
ISSN: 1471-2407
Titre abrégé: BMC Cancer
Pays: England
ID NLM: 100967800

Informations de publication

Date de publication:
06 Mar 2021
Historique:
received: 20 09 2020
accepted: 17 02 2021
entrez: 7 3 2021
pubmed: 8 3 2021
medline: 4 5 2021
Statut: epublish

Résumé

AURA study reported 61% objective response rate and progression-free survival of 9.6 months with osimertinib in patients with EGFR/T790M+ non-small cell lung cancer. Due to lack of real-world data, we proposed this study to describe the experience with osimertinib in Spain. Post-authorization, non-interventional Special Use Medication Program, multicenter, retrospective study in advanced EGFR/T790M+ non-small cell lung cancer. One hundred-fifty five patients were enrolled (August 2016-December 2018) from 30 sites. progression-free survival. Secondary objectives: toxicity profile, objective response rate, and use of health service resources. 70% women, median age 66. 63.9% were non-smokers and 99% had adenocarcinoma. Most patients had received at least one prior treatment (97%), 91.7% had received previous EGFR-tyrosine kinase inhibitors and 2.8% osimertinib as first-line treatment. At data cutoff, median follow-up was 11.8 months. One hundred-fifty five patients were evaluable for response, 1.3% complete response, 40.6% partial response, 31% stable disease and 11.6% disease progression. Objective response rate was 42%. Median progression-free survival was 9.4 months. Of the 155 patients who received treatment, 76 (49%) did not reported any adverse event, 51% presented some adverse event, most of which were grade 1 or 2. The resource cost study indicates early use is warranted. This study to assess the real-world clinical impact of osimertinib showed high drug activity in pretreated advanced EGFR/T790M+ non-small cell lung cancer, with manageable adverse events. Clinical trial registration number: NCT03790397 .

Sections du résumé

BACKGROUND BACKGROUND
AURA study reported 61% objective response rate and progression-free survival of 9.6 months with osimertinib in patients with EGFR/T790M+ non-small cell lung cancer. Due to lack of real-world data, we proposed this study to describe the experience with osimertinib in Spain.
METHODS METHODS
Post-authorization, non-interventional Special Use Medication Program, multicenter, retrospective study in advanced EGFR/T790M+ non-small cell lung cancer. One hundred-fifty five patients were enrolled (August 2016-December 2018) from 30 sites.
PRIMARY OBJECTIVE OBJECTIVE
progression-free survival. Secondary objectives: toxicity profile, objective response rate, and use of health service resources.
RESULTS RESULTS
70% women, median age 66. 63.9% were non-smokers and 99% had adenocarcinoma. Most patients had received at least one prior treatment (97%), 91.7% had received previous EGFR-tyrosine kinase inhibitors and 2.8% osimertinib as first-line treatment. At data cutoff, median follow-up was 11.8 months. One hundred-fifty five patients were evaluable for response, 1.3% complete response, 40.6% partial response, 31% stable disease and 11.6% disease progression. Objective response rate was 42%. Median progression-free survival was 9.4 months. Of the 155 patients who received treatment, 76 (49%) did not reported any adverse event, 51% presented some adverse event, most of which were grade 1 or 2. The resource cost study indicates early use is warranted.
CONCLUSION CONCLUSIONS
This study to assess the real-world clinical impact of osimertinib showed high drug activity in pretreated advanced EGFR/T790M+ non-small cell lung cancer, with manageable adverse events.
TRIAL REGISTRATION BACKGROUND
Clinical trial registration number: NCT03790397 .

Identifiants

pubmed: 33676426
doi: 10.1186/s12885-021-07922-5
pii: 10.1186/s12885-021-07922-5
pmc: PMC7937205
doi:

Substances chimiques

Acrylamides 0
Aniline Compounds 0
Protein Kinase Inhibitors 0
osimertinib 3C06JJ0Z2O
EGFR protein, human EC 2.7.10.1
ErbB Receptors EC 2.7.10.1

Banques de données

ClinicalTrials.gov
['NCT03790397']

Types de publication

Journal Article Multicenter Study Observational Study

Langues

eng

Sous-ensembles de citation

IM

Pagination

230

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Auteurs

Mariano Provencio (M)

Medical Oncology Department, Hospital Universitario Puerta de Hierro, Majadahonda, Madrid, Spain. mprovenciop@gmail.com.
Health Research Institute, Hospital Universitario Puerta de Hierro, Majadahonda, Madrid, Spain. mprovenciop@gmail.com.
Universidad Autónoma de Madrid, Madrid, Spain. mprovenciop@gmail.com.

Josefa Terrasa (J)

Medical Oncology Department, Hospital Universitari Son Espases, Islas Balears, Palma de Mallorca, Spain.

Pilar Garrido (P)

Medical Oncology Department, IRYCIS Hospital Universitario Ramón y Cajal, Madrid, Spain.

Rosario García Campelo (RG)

Medical Oncology Department, Hospital Universitario A Coruña, A Coruña, Spain.
Instituto de Investigación Biomédica A Coruña INIBIC, A Coruña, Spain.

Francisco Aparisi (F)

Medical Oncology Department Valencia, Hospital General Universitario de Valencia, Madrid, Spain.

Pilar Diz (P)

Medical Oncology Department León, Complejo Asistencial Universitario de León, Madrid, Spain.

David Aguiar (D)

Medical Oncology Department, Hospital Universitario de Gran Canaria Dr. Negrín, Las Palmas de GC, Spain.

Carlos García-Giron (C)

Medical Oncology Department, Hospital Universitario De Burgos, Burgos, Spain.

Julia Hidalgo (J)

Medical Oncology Department, Hospital Lluís Alcanyis, Xátiva, Valencia, Spain.

Carlos Aguado (C)

Medical Oncology Department, Hospital Clínico San Carlos, Madrid, Spain.

Jorge García González (JG)

Medical Oncology Department Santiago de Compostela, Hospital Clínico Universitario de Santiago, Madrid, Spain.

Emilio Esteban (E)

Medical Oncology Department, Hospital Universitario Central de Asturias, Oviedo, Spain.

Lorenzo Gómez-Aldavarí (L)

Medical Oncology Department, Complejo Hospitalario Universitario de Albacete, Albacete, Spain.

Teresa Moran (T)

Institut Català d'Oncologia Badalona, Medical Oncology Department, Badalona, Barcelona, Spain.
Hospital Universitari Germans Trias i Pujol, Barcelona, Badalona, Spain.
Department of Medicine, Universitat Autònoma de Barcelona, Barcelona, Spain.
Badalona Applied Research Group in Oncology, Barcelona, Spain.
Fundació Germans Trias i Pujol, Barcelona, Spain.

Oscar Juan (O)

Medical Oncology Department, Hospital Universitari i Politècnic La Fe, Valencia, Spain.

Luís Enrique Chara (LE)

Medical Oncology Department, Hospital Universitario de Guadalajara, Guadalajara, Spain.

Juan L Marti (JL)

Medical Oncology Department, Hospital General Universitario de Alicante, Alicante, Spain.

Rafael López Castro (RL)

Medical Oncology Department, Hospital Clínico Universitario de Valladolid, Valladolid, Spain.

Ana Laura Ortega (AL)

Medical Oncology Department, Complejo Hospitalario de Jaen, Jaen, Spain.

Elia Martínez Moreno (EM)

Medical Oncology Department, Hospital Virgen de la Salud, Toledo, Spain.

Juan Coves (J)

Medical Oncology Department, Hospital Son Llàtzer, Palma de Mallorca, Spain.

Ana M Sánchez Peña (AM)

Medical Oncology Department, Hospital Universitario de Getafe, Getafe, Madrid, Spain.

Joaquim Bosch-Barrera (J)

Department of Oncology, Catalan Institute of Oncology. Dr. Josep Trueta University Hospital, Girona, Spain.

Amparo Sánchez Gastaldo (AS)

Medical Oncology Department, Hospital Universitario Virgen del Rocío, Sevilla, Spain.

Natalia Fernández Núñez (NF)

Medical Oncology Department, Hospital Universitario Lucus Augusti, Lugo, Spain.

Edel Del Barco (E)

Medical Oncology Department, Hospital Universitario de Salamanca, Salamanca, Spain.

Manuel Cobo (M)

Hospitales Universitarios Regional y Virgen de la Victoria, IBIMA, Unidad de Gestión Clínica Intercentros de Oncología Médica, Málaga, Spain.

Dolores Isla (D)

Medical Oncology Department, Hospital Universitario Lozano Blesa, Zaragoza, Aragón, Spain.

Margarita Majem (M)

Medical Oncology Department, Hospital de la Santa Creu i Sant Pau, Barcelona, Spain.

Fátima Navarro (F)

Medical Oncology Department, Hospital Universitario Príncipe de Asturias, Alcalá de Henares, Madrid, Spain.

Virginia Calvo (V)

Medical Oncology Department, Hospital Universitario Puerta de Hierro, Majadahonda, Madrid, Spain. vircalvo@hotmail.com.
Health Research Institute, Hospital Universitario Puerta de Hierro, Majadahonda, Madrid, Spain. vircalvo@hotmail.com.

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