Duplex high resolution melting analysis (dHRMA) to detect two hot spot CYP24A1 pathogenic variants (PVs) associated to idiopathic infantile hypercalcemia (IIH).


Journal

Molecular biology reports
ISSN: 1573-4978
Titre abrégé: Mol Biol Rep
Pays: Netherlands
ID NLM: 0403234

Informations de publication

Date de publication:
Apr 2021
Historique:
received: 18 02 2021
accepted: 27 03 2021
pubmed: 18 4 2021
medline: 30 9 2021
entrez: 17 4 2021
Statut: ppublish

Résumé

Pathogenic variants (PVs) in CYP24A1 gene are associated with Idiopathic Infantile Hypercalcemia disease (IIH). The identification of CYP24A1 PVs can be a useful tool for the improvement of target therapeutic strategies. Aim of this study is to set up a rapid and inexpensive High Resolution Melting Analysis (HRMA)-based method for the simultaneous genotyping of two hot spot PVs in CYP24A1 gene, involved in IIH. A duplex-HRMA (dHRMA) was designed in order to detect simultaneously CYP24A1 c.428_430delAAG, p.(Glu143del) (rs777676129) and c.1186C > T, p.(Arg396Trp) (rs114368325), in peculiar cases addressed to our Laboratory. dHRMA was able to identify clearly and simultaneously both hot spot CYP24A1 PVs evaluating melting curve shape and melting temperature (T

Identifiants

pubmed: 33864587
doi: 10.1007/s11033-021-06324-x
pii: 10.1007/s11033-021-06324-x
pmc: PMC8172411
doi:

Substances chimiques

CYP24A1 protein, human EC 1.14.15.16
Vitamin D3 24-Hydroxylase EC 1.14.15.16

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

3303-3311

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Auteurs

Maria De Bonis (M)

UOS Diagnostica Molecolare E Genomica, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy. maria.debonis@policlinicogemelli.it.

Elisa De Paolis (E)

UOS Diagnostica Molecolare E Genomica, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.

Maria Elisabetta Onori (ME)

UOS Diagnostica Molecolare E Genomica, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.

Giorgia Mazzuccato (G)

UOS Diagnostica Molecolare E Genomica, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.

Antonio Gatto (A)

UOC Pediatria, Dipartimento Scienze della Salute della Donna, del Bambino E Di Sanità Pubblica- Area Salute del Bambino, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.

Pietro Ferrara (P)

UOC Pediatria, Dipartimento Scienze della Salute della Donna, del Bambino E Di Sanità Pubblica- Area Salute del Bambino, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.

Pietro Manuel Ferraro (PM)

UOC Nefrologia, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.
Università Cattolica del Sacro Cuore, Largo Francesco Vito, 1, 00168, Rome, Italy.

Andrea Urbani (A)

UOS Diagnostica Molecolare E Genomica, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.
Università Cattolica del Sacro Cuore, Largo Francesco Vito, 1, 00168, Rome, Italy.

Angelo Minucci (A)

UOS Diagnostica Molecolare E Genomica, Fondazione Policlinico Universitario A. Gemelli-IRCCS, Largo Agostino Gemelli, 00168, Rome, Italy.

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Classifications MeSH