Maternal Uniparental Disomy of Chromosome 20 (UPD(20)mat) as Differential Diagnosis of Silver Russell Syndrome: Identification of Three New Cases.


Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
17 04 2021
Historique:
received: 15 03 2021
revised: 02 04 2021
accepted: 12 04 2021
entrez: 30 4 2021
pubmed: 1 5 2021
medline: 13 8 2021
Statut: epublish

Résumé

Silver Russell Syndrome (SRS, MIM #180860) is a rare growth retardation disorder in which clinical diagnosis is based on six features: pre- and postnatal growth failure, relative macrocephaly, prominent forehead, body asymmetry, and feeding difficulties (Netchine-Harbison clinical scoring system (NH-CSS)). The molecular mechanisms consist in (epi)genetic deregulations at multiple loci: the loss of methylation (LOM) at the paternal

Identifiants

pubmed: 33920573
pii: genes12040588
doi: 10.3390/genes12040588
pmc: PMC8073552
pii:
doi:

Substances chimiques

Chromogranins 0
GNAS protein, human EC 3.6.1.-
GTP-Binding Protein alpha Subunits, Gs EC 3.6.5.1

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Références

Prenat Diagn. 2000 Feb;20(2):103-22
pubmed: 10694683
Genes (Basel). 2020 Mar 26;11(4):
pubmed: 32224912
J Clin Endocrinol Metab. 2021 Mar 8;106(3):802-813
pubmed: 33236057
J Bone Miner Res. 2018 Aug;33(8):1480-1488
pubmed: 29693731
Nat Rev Endocrinol. 2017 Feb;13(2):105-124
pubmed: 27585961
Genet Med. 2018 Feb;20(2):250-258
pubmed: 28796236
Eur J Med Genet. 2019 Jul;62(7):103671
pubmed: 31100449
Am J Med Genet A. 2016 Mar;170(3):743-9
pubmed: 26663145
J Biol Chem. 2006 Jul 14;281(28):18989-99
pubmed: 16672216
PLoS One. 2013 Jun 18;8(6):e65639
pubmed: 23822972
Front Genet. 2019 Oct 15;10:955
pubmed: 31749829
Nat Genet. 2004 Aug;36(8):818-26
pubmed: 15273686
Genet Med. 2016 Apr;18(4):309-15
pubmed: 26248010
J Clin Endocrinol Metab. 2018 Jun 1;103(6):2083-2088
pubmed: 29878129
Clin Genet. 2020 Jun;97(6):902-907
pubmed: 32087029
J Med Genet. 2001 Feb;38(2):86-9
pubmed: 11158171
J Clin Endocrinol Metab. 2007 Mar;92(3):1073-9
pubmed: 17164301
Nat Rev Endocrinol. 2018 Aug;14(8):476-500
pubmed: 29959430
J Med Genet. 2015 Jul;52(7):446-53
pubmed: 25951829
J Clin Invest. 2000 Mar;105(5):615-23
pubmed: 10712433
Prenat Diagn. 2001 Oct;21(10):860-3
pubmed: 11746130
Am J Med Genet A. 2005 Apr 15;134A(2):202-6
pubmed: 15690403
J Appl Genet. 2009;50(3):293-6
pubmed: 19638687
Nature. 2004 Nov 4;432(7013):53-7
pubmed: 15525980
Eur J Hum Genet. 2002 Nov;10(11):694-8
pubmed: 12404100
Eur J Hum Genet. 1999 Jul;7(5):533-40
pubmed: 10439958
Clin Case Rep. 2018 May 08;6(7):1208-1213
pubmed: 29988648
Horm Res. 2005;63(2):65-74
pubmed: 15711092

Auteurs

Pierpaola Tannorella (P)

Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, 20095 Milan, Italy.

Daniele Minervino (D)

Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, 20095 Milan, Italy.

Sara Guzzetti (S)

Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, 20095 Milan, Italy.

Alessandro Vimercati (A)

Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, 20095 Milan, Italy.

Luciano Calzari (L)

Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, 20095 Milan, Italy.

Giuseppa Patti (G)

Department of Pediatrics, IRCCS Istituto Giannina Gaslini, 16147 Genova, Italy.
Department of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health (DINOGMI), University of Genova, 16132 Genova, Italy.

Mohamad Maghnie (M)

Department of Pediatrics, IRCCS Istituto Giannina Gaslini, 16147 Genova, Italy.
Department of Neuroscience, Rehabilitation, Ophthalmology, Genetics, Maternal and Child Health (DINOGMI), University of Genova, 16132 Genova, Italy.

Anna Elsa Maria Allegri (AEM)

Department of Pediatrics, IRCCS Istituto Giannina Gaslini, 16147 Genova, Italy.

Donatella Milani (D)

Pediatric Highly Intensive Care Unit, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, 20122 Milan, Italy.

Giulietta Scuvera (G)

Pediatric Highly Intensive Care Unit, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, 20122 Milan, Italy.
Medical Genetics Unit, Woman-Child-Newborn Department, Fondazione IRCCS Ca' Granda-Ospedale Maggiore Policlinico, via Francesco Sforza 28, 20122 Milan, Italy.

Milena Mariani (M)

UOC Pediatria, ASST Lariana, 22100 Como, Italy.

Piergiorgio Modena (P)

SOS-ID Laboratorio di Genetica, ASST Lariana, 22100 Como, Italy.

Angelo Selicorni (A)

UOC Pediatria, ASST Lariana, 22100 Como, Italy.

Lidia Larizza (L)

Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, 20095 Milan, Italy.

Silvia Russo (S)

Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, 20095 Milan, Italy.

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Classifications MeSH