Coagulation disorders in patients with severe hemophagocytic lymphohistiocytosis.


Journal

PloS one
ISSN: 1932-6203
Titre abrégé: PLoS One
Pays: United States
ID NLM: 101285081

Informations de publication

Date de publication:
2021
Historique:
received: 15 04 2021
accepted: 14 06 2021
entrez: 3 8 2021
pubmed: 4 8 2021
medline: 25 11 2021
Statut: epublish

Résumé

Coagulation disorders are common in patients with hemophagocytic lymphohistiocytosis (HLH), associated with an increased risk of bleeding and death. We aim to investigate coagulation disorders and their outcome implications in critically ill patients with HLH. We prospectively evaluated 47 critically ill patients with HLH (median age of 54 years [42-67]) between April 2015 and December 2018. Coagulation assessments were performed at day 1. Abnormal standard coagulation was defined as prothrombin time (PT) <50% and/or fibrinogen <2g/L. HLH aetiology was mostly ascribed to haematological malignancies (74% of patients). Coagulation disorders and severe bleeding events were frequent, occurring in 30 (64%) and 11 (23%) patients respectively. At day 1, median fibrinogen level was 2∙65g/L [1.61-5.66]. Fibrinolytic activity was high as suggested by increased median levels of D-dimers, fibrin monomers, PAI-1 (plasminogen activator inhibitor) and tPA (tissue plasminogen activator). Forty-one (91%) patients had a decreased ADAMTS13 activity (A Disintegrin-like And Metalloproteinase with ThromboSpondin type 1 repeats, member 13). By multivariable analysis, the occurrence of a severe bleeding (OR 3.215 [1.194-8.653], p = 0∙021) and SOFA score (Sepsis-Related Organ Failure Assessment) at day 1 (OR 1.305 per point [1.146-1.485], p<0∙001) were independently associated with hospital mortality. No early biological marker was associated with severe bleeding. Hyperfibrinolysis may be the primary mechanism responsible for hypofibrinogenemia and may also participate in ADAMTS13 degradation. Targeting the plasmin system appears as a promising approach in severe HLH-related coagulation disorders.

Sections du résumé

BACKGROUND
Coagulation disorders are common in patients with hemophagocytic lymphohistiocytosis (HLH), associated with an increased risk of bleeding and death. We aim to investigate coagulation disorders and their outcome implications in critically ill patients with HLH.
METHODS
We prospectively evaluated 47 critically ill patients with HLH (median age of 54 years [42-67]) between April 2015 and December 2018. Coagulation assessments were performed at day 1. Abnormal standard coagulation was defined as prothrombin time (PT) <50% and/or fibrinogen <2g/L. HLH aetiology was mostly ascribed to haematological malignancies (74% of patients).
RESULTS
Coagulation disorders and severe bleeding events were frequent, occurring in 30 (64%) and 11 (23%) patients respectively. At day 1, median fibrinogen level was 2∙65g/L [1.61-5.66]. Fibrinolytic activity was high as suggested by increased median levels of D-dimers, fibrin monomers, PAI-1 (plasminogen activator inhibitor) and tPA (tissue plasminogen activator). Forty-one (91%) patients had a decreased ADAMTS13 activity (A Disintegrin-like And Metalloproteinase with ThromboSpondin type 1 repeats, member 13). By multivariable analysis, the occurrence of a severe bleeding (OR 3.215 [1.194-8.653], p = 0∙021) and SOFA score (Sepsis-Related Organ Failure Assessment) at day 1 (OR 1.305 per point [1.146-1.485], p<0∙001) were independently associated with hospital mortality. No early biological marker was associated with severe bleeding.
CONCLUSIONS
Hyperfibrinolysis may be the primary mechanism responsible for hypofibrinogenemia and may also participate in ADAMTS13 degradation. Targeting the plasmin system appears as a promising approach in severe HLH-related coagulation disorders.

Identifiants

pubmed: 34343182
doi: 10.1371/journal.pone.0251216
pii: PONE-D-21-12544
pmc: PMC8330932
doi:

Substances chimiques

Biomarkers 0
Fibrin Fibrinogen Degradation Products 0
Plasminogen Activator Inhibitor 1 0
SERPINE1 protein, human 0
fibrin fragment D 0
Tissue Plasminogen Activator EC 3.4.21.68
ADAMTS13 Protein EC 3.4.24.87
ADAMTS13 protein, human EC 3.4.24.87

Types de publication

Clinical Trial Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

e0251216

Déclaration de conflit d'intérêts

The authors have declared that no competing interests exist.

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Auteurs

Sandrine Valade (S)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

Bérangère S Joly (BS)

EA3518, Université de Paris, Paris, France.
Hematology Biology Department, AP-HP, Hôpital Lariboisière, Paris, France.

Agnès Veyradier (A)

EA3518, Université de Paris, Paris, France.
Hematology Biology Department, AP-HP, Hôpital Lariboisière, Paris, France.

Jehane Fadlallah (J)

EA3518, Université de Paris, Paris, France.
Department of Clinical Immunology, AP-HP, Hôpital Saint-Louis, Paris, France.

Lara Zafrani (L)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

Virginie Lemiale (V)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

Amélie Launois (A)

EA3518, Université de Paris, Paris, France.
Hematology Biology Department, AP-HP, Hôpital Lariboisière, Paris, France.

Alain Stepanian (A)

EA3518, Université de Paris, Paris, France.
Hematology Biology Department, AP-HP, Hôpital Lariboisière, Paris, France.

Lionel Galicier (L)

EA3518, Université de Paris, Paris, France.
Department of Clinical Immunology, AP-HP, Hôpital Saint-Louis, Paris, France.

Claire Fieschi (C)

EA3518, Université de Paris, Paris, France.
Department of Clinical Immunology, AP-HP, Hôpital Saint-Louis, Paris, France.

Adrien Mirouse (A)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

Jean Jacques Tudesq (JJ)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

Anne-Claire Lepretre (AC)

Transfusion Department, Etablissement Français Du Sang, Hôpital Saint-Louis, Paris, France.

Elie Azoulay (E)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

Michael Darmon (M)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

Eric Mariotte (E)

AP-HP, Medical ICU, Hôpital Saint-Louis, Paris, France.
EA3518, Université de Paris, Paris, France.

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Classifications MeSH