Maternal mosaicism for a missense variant in the

bilateral sensorineural hearing impairment congenital hypothyroidism defect in the atrial septum hyperinsulinemic hypoglycemia severe muscular hypotonia

Journal

Cold Spring Harbor molecular case studies
ISSN: 2373-2873
Titre abrégé: Cold Spring Harb Mol Case Stud
Pays: United States
ID NLM: 101660017

Informations de publication

Date de publication:
12 2021
Historique:
received: 01 07 2021
accepted: 30 09 2021
pubmed: 21 10 2021
medline: 13 1 2022
entrez: 20 10 2021
Statut: epublish

Résumé

There is increasing recognition for the contribution of genetic mosaicism to human disease, particularly as high-throughput sequencing has enabled detection of sequence variants at very low allele frequencies. Here, we describe an infant male who presented at 9 mo of age with hypotonia, dysmorphic features, congenital heart disease, hyperinsulinemic hypoglycemia, hypothyroidism, and bilateral sensorineural hearing loss. Whole-genome sequencing of the proband and the parents uncovered an apparent de novo mutation in the X-linked

Identifiants

pubmed: 34667072
pii: mcs.a006122
doi: 10.1101/mcs.a006122
pmc: PMC8751409
pii:
doi:

Substances chimiques

Spermine Synthase EC 2.5.1.22

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© 2021 Marhabaie et al.; Published by Cold Spring Harbor Laboratory Press.

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Auteurs

Mohammad Marhabaie (M)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

Scott E Hickey (SE)

Division of Genetic and Genomic Medicine at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.
Department of Pediatrics at The Ohio State University College of Medicine, Columbus, Ohio 43210, USA.

Katherine Miller (K)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

Olivia Grischow (O)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

Kathleen M Schieffer (KM)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

Samuel J Franklin (SJ)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

David M Gordon (DM)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

Samantha Choi (S)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

Theresa Mihalic Mosher (T)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.

Peter White (P)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.
Department of Pediatrics at The Ohio State University College of Medicine, Columbus, Ohio 43210, USA.

Daniel C Koboldt (DC)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.
Department of Pediatrics at The Ohio State University College of Medicine, Columbus, Ohio 43210, USA.

Richard K Wilson (RK)

The Steve and Cindy Rasmussen Institute for Genomic Medicine, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, Ohio 43205, USA.
Department of Pediatrics at The Ohio State University College of Medicine, Columbus, Ohio 43210, USA.

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