A phase II study of Navitoclax (ABT-263) as single agent in women heavily pretreated for recurrent epithelial ovarian cancer: The MONAVI - GINECO study.


Journal

Gynecologic oncology
ISSN: 1095-6859
Titre abrégé: Gynecol Oncol
Pays: United States
ID NLM: 0365304

Informations de publication

Date de publication:
04 2022
Historique:
received: 22 11 2021
revised: 14 01 2022
accepted: 16 01 2022
pubmed: 7 2 2022
medline: 27 4 2022
entrez: 6 2 2022
Statut: ppublish

Résumé

There are limited treatment options for ovarian cancer patients with early relapse after platinum chemotherapy. In preclinical studies, we previously demonstrated the promising activity of ABT-737, a Bcl-2/Bcl-x We conducted a prospective multicenter single-arm phase II study to assess the efficacy of Navitoclax (orally available ABT-737 analogue) monotherapy in 46 heavily pretreated (2-12 lines, median = 4) patients with high-grade serous platinum-resistant ovarian tumors. Navitoclax was administered at the daily dose of 150 mg during a lead-in period (7-14 days) and then increased to 250 mg daily in the absence of dose-limiting thrombocytopenia (<G3). Progression-free survival (PFS) based on RECIST v1.1 criteria was the primary endpoint. Analysis of efficacy according to the expression of Bcl-2 family proteins in tumor biopsies was also planned. The 3-month PFS was 22.7% [ Navitoclax monotherapy had poor activity that was not correlated with the expression of Bim, Mcl-1 and P-ERK, without unacceptable toxicity. Clinicaltrials.gov identifier: NCT02591095.

Sections du résumé

BACKGROUND
There are limited treatment options for ovarian cancer patients with early relapse after platinum chemotherapy. In preclinical studies, we previously demonstrated the promising activity of ABT-737, a Bcl-2/Bcl-x
METHODS
We conducted a prospective multicenter single-arm phase II study to assess the efficacy of Navitoclax (orally available ABT-737 analogue) monotherapy in 46 heavily pretreated (2-12 lines, median = 4) patients with high-grade serous platinum-resistant ovarian tumors. Navitoclax was administered at the daily dose of 150 mg during a lead-in period (7-14 days) and then increased to 250 mg daily in the absence of dose-limiting thrombocytopenia (<G3). Progression-free survival (PFS) based on RECIST v1.1 criteria was the primary endpoint. Analysis of efficacy according to the expression of Bcl-2 family proteins in tumor biopsies was also planned.
RESULTS
The 3-month PFS was 22.7% [
CONCLUSIONS
Navitoclax monotherapy had poor activity that was not correlated with the expression of Bim, Mcl-1 and P-ERK, without unacceptable toxicity.
TRIAL REGISTRATION
Clinicaltrials.gov identifier: NCT02591095.

Identifiants

pubmed: 35123771
pii: S0090-8258(22)00048-8
doi: 10.1016/j.ygyno.2022.01.021
pii:
doi:

Substances chimiques

Aniline Compounds 0
Myeloid Cell Leukemia Sequence 1 Protein 0
Proto-Oncogene Proteins c-bcl-2 0
Sulfonamides 0
Platinum 49DFR088MY
navitoclax XKJ5VVK2WD

Banques de données

ClinicalTrials.gov
['NCT02591095']

Types de publication

Clinical Trial, Phase II Journal Article Multicenter Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

30-39

Informations de copyright

Copyright © 2022 Elsevier Inc. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of Competing Interest F. Joly: Abbvie for Navitoclax provision, consulting for Roche, GSK, Astra Zeneca, Clovis, MSD, Ipsen, Janssen, Astellas, Pfizer, Sanofi, BMS, Bayer. M. Fabbro: Consulting for GSK, Astra-Zeneca, and Clovis Oncology. P. Follana: GSK, Astra Zeneca, Clovis, MSD, Novartis, DAIICHI. J.S. Frenel: Consulting for Novartis, Pfizer, Astra Zeneca, Lilly, Roche, BIOCAD, DAIICHI, GSK-Tesaro, Pierre Fabre, and Clovis oncology. B.You: Consulting for MSD, Astra-Zeneca, GSK-TESARO, BAYER, Roche-Genentech, ECS Progastrine, Novartis, LEK, Amgen, Clovis Oncology, Merck Serono, BMS, SEAGEN, and Myriad. J. Lequesne, J. Medioni, A. Lesoin, S. Abadie-Lacourtoisie, A. Floquet, L. Gladieff, C. Gavoille, E. Kalbacher, M. Briand, P.E. Brachet, F. Giffard, L-B. Weiswald, P.A. Just, C. Blanc-Fournier, A. Leconte, B. Clarisse, A. Leary, L. Poulain: no conflicts of interest to disclose in relation with this work.

Auteurs

Florence Joly (F)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France; Normandie University, UNICAEN, INSERM U1086 "ANTICIPE" (Interdisciplinary Research Unit for Cancers Prevention and Treatment), Centre François Baclesse, 3 avenue Général Harris, 14000 Caen, France. Electronic address: f.joly@baclesse.unicancer.fr.

Michel Fabbro (M)

Institut du Cancer Val d'Aurelle, UNICANCER, 208 rue des Apothicaires, 34298 Montpellier, France. Electronic address: michel.fabbro@icm.unicancer.fr.

Philippe Follana (P)

Centre Antoine Lacassagne, UNICANCER, 33 avenue de Valombrose, 06189 Nice, France. Electronic address: philippe.follana@nice.unicancer.fr.

Justine Lequesne (J)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France. Electronic address: j.lequesne@baclesse.unicancer.fr.

Jacques Medioni (J)

Assistance Publique - Hôpitaux de Paris, Hôpital Européen Georges Pompidou, 20 Rue Leblanc, 75015 Paris, France; UFR de Médecine Paris Centre, Université de Paris, UMR_S1138-INSERM, France. Electronic address: jacques.medioni@aphp.fr.

Anne Lesoin (A)

Centre Oscar Lambret, UNICANCER, 3 rue Frédéric Combemale, 59000 Lille, France. Electronic address: a-lesoin@o-lambret.fr.

Jean-Sébastien Frenel (JS)

Institut de Cancérologie de l'Ouest, Centre René Gauducheau, UNICANCER, Boulevard Professeur Jacques Monod, 44805 Saint-Herblain, France. Electronic address: jean-sebastien.frenel@ico.unicancer.fr.

Sophie Abadie-Lacourtoisie (S)

Institut de Cancérologie de l'Ouest, Centre Paul Papin, UNICANCER, 15 rue Bocquel 49055 Angers cedex, France. Electronic address: sophie.abadie-lacourtoisie@ico.unicancer.fr.

Anne Floquet (A)

Institut Bergonié, UNICANCER, 229 Cours de l'Argonne, 33076 Bordeaux, France. Electronic address: a.floquet@bordeaux.unicancer.fr.

Laurence Gladieff (L)

Institut Claudius Regaud, UNICANCER, Institut Universitaire du Cancer de Toulouse Oncopole, 1 Avenue Irène Joliot-Curie, 31059 Toulouse, France. Electronic address: gladieff.laurence@iuct-oncopole.fr.

Benoît You (B)

CITOHL, Centre Hospitalier Lyon Sud, Institut de Cancérologie des Hospices Civils de Lyon (IC-HCL), 69310 Pierre-Bénite, France; Université Claude Bernard Lyon 1, UCBL, EA3738 CICLY, Lyon, France. Electronic address: benoit.you@chu-lyon.fr.

Céline Gavoille (C)

Institut de Cancérologie de Lorraine, UNICANCER, 6 Avenue de Bourgogne Brabois, 54511 Vandoeuvre-lès-Nancy, France. Electronic address: c.gavoille@nancy.unicancer.fr.

Elsa Kalbacher (E)

Centre Hospitalier Universitaire Jean Minjoz, 3 boulevard Alexandre Fleming, 25030 Besançon, France. Electronic address: ekalbacher@chu-besancon.fr.

Mélanie Briand (M)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France; Normandie University, UNICAEN, INSERM U1086 "ANTICIPE" (Interdisciplinary Research Unit for Cancers Prevention and Treatment), Centre François Baclesse, 3 avenue Général Harris, 14000 Caen, France. Electronic address: m.briand@baclesse.unicancer.fr.

Pierre-Emmanuel Brachet (PE)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France; Normandie University, UNICAEN, INSERM U1086 "ANTICIPE" (Interdisciplinary Research Unit for Cancers Prevention and Treatment), Centre François Baclesse, 3 avenue Général Harris, 14000 Caen, France. Electronic address: pe.brachet@baclesse.unicancer.fr.

Florence Giffard (F)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France; Normandie University, UNICAEN, INSERM U1086 "ANTICIPE" (Interdisciplinary Research Unit for Cancers Prevention and Treatment), Centre François Baclesse, 3 avenue Général Harris, 14000 Caen, France. Electronic address: giffard-f@baclesse.unicancer.fr.

Louis-Bastien Weiswald (LB)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France; Normandie University, UNICAEN, INSERM U1086 "ANTICIPE" (Interdisciplinary Research Unit for Cancers Prevention and Treatment), Centre François Baclesse, 3 avenue Général Harris, 14000 Caen, France. Electronic address: lb.weiswald@baclesse.unicancer.fr.

Pierre-Alexandre Just (PA)

Université de Paris, APHP, Cochin Hospital, 27 rue du Faubourg Saint-Jacques, 75014 Paris, France. Electronic address: pierre-alexandre.just@aphp.fr.

Cécile Blanc-Fournier (C)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France; Normandie University, UNICAEN, INSERM U1086 "ANTICIPE" (Interdisciplinary Research Unit for Cancers Prevention and Treatment), Centre François Baclesse, 3 avenue Général Harris, 14000 Caen, France. Electronic address: c.blanc.fournier@baclesse.unicancer.fr.

Alexandra Leconte (A)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France. Electronic address: a.leconte@baclesse.unicancer.fr.

Bénédicte Clarisse (B)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France. Electronic address: b.clarisse@baclesse.unicancer.fr.

Alexandra Leary (A)

Institut Gustave Roussy, UNICANCER, 39 rue Camille Desmoulins, 94805 Villejuif, France. Electronic address: alexandra.leary@gustaveroussy.fr.

Laurent Poulain (L)

Centre François Baclesse, UNICANCER, 3 avenue Général Harris, 14000 Caen, France; Normandie University, UNICAEN, INSERM U1086 "ANTICIPE" (Interdisciplinary Research Unit for Cancers Prevention and Treatment), Centre François Baclesse, 3 avenue Général Harris, 14000 Caen, France. Electronic address: l.poulain@baclesse.unicancer.fr.

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Classifications MeSH