CUB Domain-Containing Protein 1 (CDCP1) Is a Target for Radioligand Therapy in Castration-Resistant Prostate Cancer, including PSMA Null Disease.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
15 07 2022
Historique:
received: 01 11 2021
revised: 07 03 2022
accepted: 17 05 2022
pubmed: 24 5 2022
medline: 19 7 2022
entrez: 23 5 2022
Statut: ppublish

Résumé

With the improvement in overall survival with 177Lu-PSMA 617, radioligand therapy (RLT) is now a viable option for patients with metastatic castration-resistant prostate cancer (mCRPC). However, responses are variable, in part due to low PSMA expression in 30% of patients. Herein, we evaluated whether the cell surface protein CUB domain-containing protein 1 (CDCP1) can be exploited to treat mCRPC with RLT, including in PSMA-low subsets. CDCP1 levels were evaluated using RNA sequencing from 119 mCRPC biopsies. CDCP1 levels were assessed in 17 post-enzalutamide- or abiraterone-treated mCRPC biopsies, 12 patient-derived xenografts (PDX), and prostate cancer cell lines. 4A06, a recombinant human antibody that targets the CDCP1 ectodomain, was labeled with Zr-89 or Lu-177 and tested in tumor-bearing mice. CDCP1 expression was observed in 90% of mCRPC biopsies, including small-cell neuroendocrine (SCNC) and adenocarcinomas with low FOLH1 (PSMA) levels. Fifteen of 17 evaluable mCRPC biopsies (85%) demonstrated membranous CDCP1 expression, and 4 of 17 (23%) had higher CDCP1 H-scores compared with PSMA. CDCP1 was expressed in 10 of 12 PDX samples. Bmax values of approximately 22,000, 6,200, and 2,800 fmol/mg were calculated for PC3, DU145, and C4-2B human prostate cancer cells, respectively. 89Zr-4A06 PET detected six human prostate cancer xenografts, including PSMA-low tumors. 177Lu-4A06 significantly suppressed growth of DU145 and C4-2B xenografts. The data provide the first evidence supporting CDCP1-directed RLT to treat mCRPC. Expanded studies are warranted to determine whether CDCP1 is a viable drug target for patients with mCPRC.

Identifiants

pubmed: 35604681
pii: 699115
doi: 10.1158/1078-0432.CCR-21-3858
pmc: PMC9288514
mid: NIHMS1811588
doi:

Substances chimiques

Antigens, Neoplasm 0
CDCP1 protein, human 0
Cell Adhesion Molecules 0
Dipeptides 0
Heterocyclic Compounds, 1-Ring 0
Radioisotopes 0
Radiopharmaceuticals 0
Zirconium C6V6S92N3C
Prostate-Specific Antigen EC 3.4.21.77
Zirconium-89 NTM296JU95

Types de publication

Journal Article Research Support, Non-U.S. Gov't Research Support, U.S. Gov't, Non-P.H.S. Research Support, N.I.H., Extramural

Langues

eng

Sous-ensembles de citation

IM

Pagination

3066-3075

Subventions

Organisme : NIGMS NIH HHS
ID : R01 GM097316
Pays : United States
Organisme : NIGMS NIH HHS
ID : T32 GM141323
Pays : United States
Organisme : NCRR NIH HHS
ID : S10 RR023051
Pays : United States
Organisme : NCI NIH HHS
ID : R01 CA258297
Pays : United States
Organisme : NCI NIH HHS
ID : P41 CA196276
Pays : United States
Organisme : NIBIB NIH HHS
ID : R01 EB025207
Pays : United States
Organisme : NIH HHS
ID : S10 OD012301
Pays : United States
Organisme : NCI NIH HHS
ID : R01 CA191018
Pays : United States

Informations de copyright

©2022 American Association for Cancer Research.

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Auteurs

Ning Zhao (N)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Shalini Chopra (S)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Kai Trepka (K)

Department of Medicine, University of California, San Francisco, San Francisco, California.

Yung-Hua Wang (YH)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Sasank Sakhamuri (S)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Nima Hooshdaran (N)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Hyunjung Kim (H)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Jie Zhou (J)

Department of Pharmaceutical Chemistry, University of California, San Francisco, San Francisco, California.

Shion A Lim (SA)

Department of Pharmaceutical Chemistry, University of California, San Francisco, San Francisco, California.

Kevin K Leung (KK)

Department of Pharmaceutical Chemistry, University of California, San Francisco, San Francisco, California.

Emily A Egusa (EA)

Department of Radiation Oncology, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

Jun Zhu (J)

Department of Radiation Oncology, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

Li Zhang (L)

Department of Medicine, University of California, San Francisco, San Francisco, California.

Adam Foye (A)

Department of Radiation Oncology, University of California, San Francisco, San Francisco, California.

Renuka Sriram (R)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Emily Chan (E)

Department of Pathology, University of California, San Francisco, San Francisco, California.

Youngho Seo (Y)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.

Felix Y Feng (FY)

Department of Radiation Oncology, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

Eric J Small (EJ)

Department of Medicine, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

Jonathan Chou (J)

Department of Medicine, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

James A Wells (JA)

Department of Pharmaceutical Chemistry, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

Rahul Aggarwal (R)

Department of Medicine, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

Michael J Evans (MJ)

Department of Radiology and Biomedical Imaging, University of California, San Francisco, San Francisco, California.
Department of Pharmaceutical Chemistry, University of California, San Francisco, San Francisco, California.
Helen Diller Family Comprehensive Cancer Center, University of California, San Francisco, San Francisco, California.

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