Neurons contribute to pathology in a mouse model of Krabbe disease in a cell-autonomous manner.


Journal

PLoS biology
ISSN: 1545-7885
Titre abrégé: PLoS Biol
Pays: United States
ID NLM: 101183755

Informations de publication

Date de publication:
07 2022
Historique:
entrez: 6 7 2022
pubmed: 7 7 2022
medline: 9 7 2022
Statut: epublish

Résumé

In this issue of PLOS Biology, Kreher and colleagues show in a mouse model that in vivo, neurons and not only myelinating glia are primary effectors of disease progression in Krabbe disease. The neuron-specific model generated allows the unprecedented capacity to investigate the neuronal autonomous component of this disorder.

Identifiants

pubmed: 35793314
doi: 10.1371/journal.pbio.3001706
pii: PBIOLOGY-D-22-01121
pmc: PMC9258894
doi:

Substances chimiques

Galactosylceramidase EC 3.2.1.46

Types de publication

Journal Article Research Support, Non-U.S. Gov't Comment

Langues

eng

Sous-ensembles de citation

IM

Pagination

e3001706

Commentaires et corrections

Type : CommentOn

Déclaration de conflit d'intérêts

The authors have declared that no competing interests exist.

Références

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pubmed: 33097716
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pubmed: 29623914
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pubmed: 24415155
J Neurosci. 2013 Jun 12;33(24):10048-56
pubmed: 23761900
ASN Neuro. 2022 Jan-Dec;14:17590914221087817
pubmed: 35300522
Neurobiol Dis. 2014 Jun;66:92-103
pubmed: 24607884
Glia. 2021 Oct;69(10):2309-2331
pubmed: 33851745
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pubmed: 27780934
J Neurosci. 2009 May 13;29(19):6068-77
pubmed: 19439584
Acta Neuropathol. 2011 Jul;122(1):35-48
pubmed: 21373782

Auteurs

Pedro Brites (P)

Neurolipid Biology Group, Instituto de Biologia Molecular e Celular (IBMC), Instituto de Investigação e Inovação em Saúde (i3S), University of Porto, Porto, Portugal.

Monica M Sousa (MM)

Nerve Regeneration Group, Instituto de Biologia Molecular e Celular (IBMC), Instituto de Investigação e Inovação em Saúde (i3S), University of Porto, Porto, Portugal.

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Classifications MeSH