Beyond Retigabine: Design, Synthesis, and Pharmacological Characterization of a Potent and Chemically Stable Neuronal Kv7 Channel Activator with Anticonvulsant Activity.


Journal

Journal of medicinal chemistry
ISSN: 1520-4804
Titre abrégé: J Med Chem
Pays: United States
ID NLM: 9716531

Informations de publication

Date de publication:
25 08 2022
Historique:
pubmed: 17 8 2022
medline: 27 8 2022
entrez: 16 8 2022
Statut: ppublish

Résumé

Neuronal Kv7 channels represent important pharmacological targets for hyperexcitability disorders including epilepsy. Retigabine is the prototype Kv7 activator clinically approved for seizure treatment; however, severe side effects associated with long-term use have led to its market discontinuation. Building upon the recently described cryoEM structure of Kv7.2 complexed with retigabine and on previous structure-activity relationship studies, a small library of retigabine analogues has been designed, synthesized, and characterized for their Kv7 opening ability using both fluorescence- and electrophysiology-based assays. Among all tested compounds,

Identifiants

pubmed: 35972998
doi: 10.1021/acs.jmedchem.2c00911
pmc: PMC9421656
doi:

Substances chimiques

Anticonvulsants 0
Carbamates 0
KCNQ2 Potassium Channel 0
KCNQ3 Potassium Channel 0
Phenylenediamines 0
ezogabine 12G01I6BBU

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

11340-11364

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Auteurs

Simona Musella (S)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Lidia Carotenuto (L)

Department of Neuroscience, Reproductive Sciences and Dentistry, University Federico II of Naples, Via Pansini, 5, Naples 80131, Italy.

Nunzio Iraci (N)

Department of Chemical, Biological, Pharmaceutical and Environmental Sciences (CHIBIOFARAM), University of Messina, Viale Ferdinando Stagno d'Alcontres 31, Messina 98166, Italy.

Giulia Baroli (G)

Department of Neuroscience, Reproductive Sciences and Dentistry, University Federico II of Naples, Via Pansini, 5, Naples 80131, Italy.

Tania Ciaglia (T)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Piera Nappi (P)

Department of Neuroscience, Reproductive Sciences and Dentistry, University Federico II of Naples, Via Pansini, 5, Naples 80131, Italy.

Manuela Giovanna Basilicata (MG)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Emanuela Salviati (E)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Vincenzo Barrese (V)

Department of Neuroscience, Reproductive Sciences and Dentistry, University Federico II of Naples, Via Pansini, 5, Naples 80131, Italy.

Vincenzo Vestuto (V)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Giuseppe Pignataro (G)

Department of Neuroscience, Reproductive Sciences and Dentistry, University Federico II of Naples, Via Pansini, 5, Naples 80131, Italy.

Giacomo Pepe (G)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Eduardo Sommella (E)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Veronica Di Sarno (V)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Michele Manfra (M)

Department of Science, University of Basilicata, Via dell'Ateneo Lucano 10, Potenza 85100, Italy.

Pietro Campiglia (P)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Isabel Gomez-Monterrey (I)

Department of Pharmacy, University Federico II of Naples, Via D. Montesano 49, Naples 80131, Italy.

Alessia Bertamino (A)

Department of Pharmacy, University of Salerno, Via G. Paolo II 132, Fisciano 84084, Salerno, Italy.

Maurizio Taglialatela (M)

Department of Neuroscience, Reproductive Sciences and Dentistry, University Federico II of Naples, Via Pansini, 5, Naples 80131, Italy.

Carmine Ostacolo (C)

Department of Pharmacy, University Federico II of Naples, Via D. Montesano 49, Naples 80131, Italy.

Francesco Miceli (F)

Department of Neuroscience, Reproductive Sciences and Dentistry, University Federico II of Naples, Via Pansini, 5, Naples 80131, Italy.

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Classifications MeSH