Hermansky-Pudlak syndrome type 1 causes impaired anti-microbial immunity and inflammation due to dysregulated immunometabolism.


Journal

Mucosal immunology
ISSN: 1935-3456
Titre abrégé: Mucosal Immunol
Pays: United States
ID NLM: 101299742

Informations de publication

Date de publication:
06 2022
Historique:
received: 11 01 2022
accepted: 24 08 2022
revised: 11 08 2022
pubmed: 28 10 2022
medline: 1 12 2022
entrez: 27 10 2022
Statut: ppublish

Résumé

Hermansky-Pudlak syndrome (HPS) types 1 and 4 are caused by defective vesicle trafficking. The mechanism for Crohn's disease-like inflammation, lung fibrosis, and macrophage lipid accumulation in these patients remains enigmatic. The aim of this study is to understand the cellular basis of inflammation in HPS-1. We performed mass cytometry, proteomic and transcriptomic analyses to investigate peripheral blood cells and serum of HPS-1 patients. Using spatial transcriptomics, granuloma-associated signatures in the tissue of an HPS-1 patient with granulomatous colitis were dissected. In vitro studies were conducted to investigate anti-microbial responses of HPS-1 patient macrophages and cell lines. Monocytes of HPS-1 patients exhibit an inflammatory phenotype associated with dysregulated TNF, IL-1α, OSM in serum, and monocyte-derived macrophages. Inflammatory macrophages accumulate in the intestine and granuloma-associated macrophages in HPS-1 show transcriptional signatures suggestive of a lipid storage and metabolic defect. We show that HPS1 deficiency leads to an altered metabolic program and Rab32-dependent amplified mTOR signaling, facilitated by the accumulation of mTOR on lysosomes. This pathogenic mechanism translates into aberrant bacterial clearance, which can be rescued with mTORC1 inhibition. Rab32-mediated mTOR signaling acts as an immuno-metabolic checkpoint, adding to the evidence that defective bioenergetics can drive hampered anti-microbial activity and contribute to inflammation.

Identifiants

pubmed: 36302964
doi: 10.1038/s41385-022-00572-1
pii: S1933-0219(22)01765-2
pmc: PMC9607658
doi:

Substances chimiques

TOR Serine-Threonine Kinases EC 2.7.11.1
Lipids 0

Types de publication

Journal Article Research Support, N.I.H., Intramural Research Support, Non-U.S. Gov't Research Support, N.I.H., Extramural

Langues

eng

Sous-ensembles de citation

IM

Pagination

1431-1446

Subventions

Organisme : Wellcome Trust
ID : 211276/Z/18/Z
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 218597/Z/19/Z
Pays : United Kingdom
Organisme : Department of Health
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 222426/Z/21/Z
Pays : United Kingdom
Organisme : Wellcome Trust
ID : 211122/Z/18/Z
Pays : United Kingdom

Informations de copyright

© 2022. The Author(s).

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Auteurs

Athena Cavounidis (A)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.
GSK, Wavre, Belgium.

Sumeet Pandey (S)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.
GSK Immunology Network, GSK Medicines Research Center, Stevenage, UK.

Melania Capitani (M)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.
SenTcell Ltd, London, UK.

Matthias Friedrich (M)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.
Kennedy Institute of Rheumatology, Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences, University of Oxford, Oxford, UK.

Amy Cross (A)

Nuffield Department of Surgical Sciences, University of Oxford, Oxford, UK.

Lisa Gartner (L)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.

Dominik Aschenbrenner (D)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.
Autoimmunity, Transplantation and Inflammation, Novartis Institutes for BioMedical Research, Novartis Pharma AG, Basel, Switzerland.

Seunghee Kim-Schulze (S)

Human Immune Monitoring Center, Icahn School of Medicine at Mount Sinai, New York, NY, USA.

Ying Ka Lam (YK)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.

Georgina Berridge (G)

Target Discovery Institute, Center for Medicines Discovery, Nuffield Department of Medicine, University of Oxford, Oxford, UK.

Dermot P B McGovern (DPB)

F. Widjaja Foundation Inflammatory Bowel and Immunobiology Institute, Cedars-Sinai Medical Center, Los Angeles, CA, USA.

Benedikt Kessler (B)

Target Discovery Institute, Center for Medicines Discovery, Nuffield Department of Medicine, University of Oxford, Oxford, UK.

Roman Fischer (R)

Target Discovery Institute, Center for Medicines Discovery, Nuffield Department of Medicine, University of Oxford, Oxford, UK.

Paul Klenerman (P)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK.

Joanna Hester (J)

Nuffield Department of Surgical Sciences, University of Oxford, Oxford, UK.

Fadi Issa (F)

Nuffield Department of Surgical Sciences, University of Oxford, Oxford, UK.

Esther A Torres (EA)

University of Puerto Rico School of Medicine, Puerto Rico, USA.

Fiona Powrie (F)

Kennedy Institute of Rheumatology, Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences, University of Oxford, Oxford, UK.

Bernadette R Gochuico (BR)

Medical Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.

William A Gahl (WA)

Medical Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD, USA.

Louis Cohen (L)

Icahn School of Medicine at Mount Sinai, New York, NY, USA.

Holm H Uhlig (HH)

Translational Gastroenterology Unit, Nuffield Department of Medicine, University of Oxford, Oxford, UK. holm.uhlig@ndm.ox.ac.uk.
Department of Paediatrics, University of Oxford, Oxford, UK. holm.uhlig@ndm.ox.ac.uk.
Oxford NIHR Biomedical Research Centre, Oxford, UK. holm.uhlig@ndm.ox.ac.uk.

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