Germline

FG repeats NUP98 variants Rothmund–Thomson spectrum endocrine perturbation intrinsic disordered regions juvenile cataracts protein molecular modeling whole exome sequencing

Journal

International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791

Informations de publication

Date de publication:
16 Feb 2023
Historique:
received: 22 12 2022
revised: 08 02 2023
accepted: 14 02 2023
entrez: 25 2 2023
pubmed: 26 2 2023
medline: 3 3 2023
Statut: epublish

Résumé

Two adult siblings born to first-cousin parents presented a clinical phenotype reminiscent of Rothmund-Thomson syndrome (RTS), implying fragile hair, absent eyelashes/eyebrows, bilateral cataracts, mottled pigmentation, dental decay, hypogonadism, and osteoporosis. As the clinical suspicion was not supported by the sequencing of

Identifiants

pubmed: 36835439
pii: ijms24044028
doi: 10.3390/ijms24044028
pmc: PMC9965077
pii:
doi:

Substances chimiques

Nuclear Pore Complex Proteins 0
Nup98 protein, human 0

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Italian Ministry of Health
ID : 08C624
Organisme : pan-European research infrastructure for Biobanking and BioMolecular Resources Research Infrastructure

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Auteurs

Elisa Adele Colombo (EA)

Genetica Medica, Dipartimento di Scienze Della Salute, Università Degli Studi di Milano, 20142 Milano, Italy.

Michele Valiante (M)

Laboratory of Medical Genetics, Department of Experimental Medicine, Sapienza University, San Camillo-Forlanini Hospital, 00152 Roma, Italy.

Matteo Uggeri (M)

Department of Biomedical Sciences National Research Council, Institute for Biomedical Technologies, 20054 Segrate, Italy.
Department of Pharmacy, Section of Medicinal Chemistry, School of Medical and Pharmaceutical Sciences, University of Genoa, 16132 Genoa, Italy.

Alessandro Orro (A)

Department of Biomedical Sciences National Research Council, Institute for Biomedical Technologies, 20054 Segrate, Italy.

Silvia Majore (S)

Laboratory of Medical Genetics, Department of Experimental Medicine, Sapienza University, San Camillo-Forlanini Hospital, 00152 Roma, Italy.

Paola Grammatico (P)

Laboratory of Medical Genetics, Department of Experimental Medicine, Sapienza University, San Camillo-Forlanini Hospital, 00152 Roma, Italy.

Davide Gentilini (D)

Bioinformatics and Statistical Genomics Unit, IRCCS Istituto Auxologico Italiano, Via Ariosto 13, 20145 Milan, Italy.
Department of Brain and Behavioral Sciences, University of Pavia, 27100 Pavia, Italy.

Palma Finelli (P)

Experimental Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, Via Ariosto 13, 20145 Milan, Italy.
Department of Medical Biotechnology and Translational Medicine, University of Milan, 20133 Milan, Italy.

Cristina Gervasini (C)

Genetica Medica, Dipartimento di Scienze Della Salute, Università Degli Studi di Milano, 20142 Milano, Italy.

Pasqualina D'Ursi (P)

Department of Biomedical Sciences National Research Council, Institute for Biomedical Technologies, 20054 Segrate, Italy.

Lidia Larizza (L)

Experimental Research Laboratory of Medical Cytogenetics and Molecular Genetics, IRCCS Istituto Auxologico Italiano, Via Ariosto 13, 20145 Milan, Italy.

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Classifications MeSH