Rare predicted loss-of-function variants of type I IFN immunity genes are associated with life-threatening COVID-19.


Journal

Genome medicine
ISSN: 1756-994X
Titre abrégé: Genome Med
Pays: England
ID NLM: 101475844

Informations de publication

Date de publication:
05 04 2023
Historique:
received: 15 09 2022
accepted: 10 03 2023
medline: 7 4 2023
entrez: 5 4 2023
pubmed: 6 4 2023
Statut: epublish

Résumé

We previously reported that impaired type I IFN activity, due to inborn errors of TLR3- and TLR7-dependent type I interferon (IFN) immunity or to autoantibodies against type I IFN, account for 15-20% of cases of life-threatening COVID-19 in unvaccinated patients. Therefore, the determinants of life-threatening COVID-19 remain to be identified in ~ 80% of cases. We report here a genome-wide rare variant burden association analysis in 3269 unvaccinated patients with life-threatening COVID-19, and 1373 unvaccinated SARS-CoV-2-infected individuals without pneumonia. Among the 928 patients tested for autoantibodies against type I IFN, a quarter (234) were positive and were excluded. No gene reached genome-wide significance. Under a recessive model, the most significant gene with at-risk variants was TLR7, with an OR of 27.68 (95%CI 1.5-528.7, P = 1.1 × 10 Rare variants of TLR3- and TLR7-dependent type I IFN immunity genes can underlie life-threatening COVID-19, particularly with recessive inheritance, in patients under 60 years old.

Sections du résumé

BACKGROUND
We previously reported that impaired type I IFN activity, due to inborn errors of TLR3- and TLR7-dependent type I interferon (IFN) immunity or to autoantibodies against type I IFN, account for 15-20% of cases of life-threatening COVID-19 in unvaccinated patients. Therefore, the determinants of life-threatening COVID-19 remain to be identified in ~ 80% of cases.
METHODS
We report here a genome-wide rare variant burden association analysis in 3269 unvaccinated patients with life-threatening COVID-19, and 1373 unvaccinated SARS-CoV-2-infected individuals without pneumonia. Among the 928 patients tested for autoantibodies against type I IFN, a quarter (234) were positive and were excluded.
RESULTS
No gene reached genome-wide significance. Under a recessive model, the most significant gene with at-risk variants was TLR7, with an OR of 27.68 (95%CI 1.5-528.7, P = 1.1 × 10
CONCLUSIONS
Rare variants of TLR3- and TLR7-dependent type I IFN immunity genes can underlie life-threatening COVID-19, particularly with recessive inheritance, in patients under 60 years old.

Identifiants

pubmed: 37020259
doi: 10.1186/s13073-023-01173-8
pii: 10.1186/s13073-023-01173-8
pmc: PMC10074346
doi:

Substances chimiques

Toll-Like Receptor 3 0
Toll-Like Receptor 7 0
Interferon Type I 0
Autoantibodies 0

Banques de données

ClinicalTrials.gov
['NCT04262921', 'NCT04259892', 'NCT04352348']

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't Research Support, N.I.H., Intramural

Langues

eng

Sous-ensembles de citation

IM

Pagination

22

Subventions

Organisme : NHGRI NIH HHS
ID : UM1 HG006504
Pays : United States
Organisme : NIAID NIH HHS
ID : R01 AI088364
Pays : United States
Organisme : NIH HHS
ID : S10 OD018521
Pays : United States
Organisme : NCRR NIH HHS
ID : UL1 RR024143
Pays : United States
Organisme : Medical Research Council
ID : MR/S032304/1
Pays : United Kingdom
Organisme : NIAID NIH HHS
ID : R01 AI163029
Pays : United States
Organisme : NHGRI NIH HHS
ID : U24 HG008956
Pays : United States
Organisme : Howard Hughes Medical Institute
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR001866
Pays : United States

Investigateurs

Laurent Abel (L)
Saleh Al-Muhsen (S)
Fahd Al-Mulla (F)
Mark S Anderson (MS)
Evangelos Andreakos (E)
Andrés A Arias (AA)
Hagit Baris Feldman (HB)
Alexandre Belot (A)
Catherine M Biggs (CM)
Dusan Bogunovic (D)
Anastasiia Bondarenko (A)
Ahmed A Bousfiha (AA)
Petter Brodin (P)
Yenan Bryceson (Y)
Carlos D Bustamante (CD)
Samya Chakravorty (S)
John Christodoulou (J)
Murkesh Desai (M)
Beth A Drolet (BA)
Jamila El Baghdadi (JE)
Sara Espinosa-Padilla (S)
José Luis Franco (JL)
Antoine Froidure (A)
David Hagin (D)
Sarah E Henrickson (SE)
Elena W Y Hsieh (EWY)
Eystein Husebye (E)
Kohsuke Imai (K)
Yuval Itan (Y)
Erich D Jarvis (ED)
Timokratis Karamitros (T)
Kai Kisand (K)
Cheng-Lung Ku (CL)
Yun Ling (Y)
Carrie L Lucas (CL)
László Maródi (L)
Isabelle Meyts (I)
Joshua D Milner (JD)
Kristina Mironska (K)
Tomohiro Morio (T)
Lisa F P Ng (LFP)
Luigi D Notarangelo (LD)
Cliona O'Farrelly (C)
Satoshi Okada (S)
Anna M Planas (AM)
Lluis Quintana-Murci (L)
Laurent Renia (L)
Igor Resnick (I)
Carlos Rodríguez-Gallego (C)
Vanessa Sancho-Shimizu (V)
Anna Sediva (A)
Mikko R J Seppänen (MRJ)
Anna Shcherbina (A)
Ondrej Slaby (O)
Andrew L Snow (AL)
Pere Soler-Palacín (P)
András N Spaan (AN)
Ivan Tancevski (I)
Stuart G Tangye (SG)
Sathishkumar Ramaswamy (S)
Stuart E Turvey (SE)
Furkan Uddin (F)
Mohammed J Uddin (MJ)
Diederik van de Beek (D)
Donald C Vinh (DC)
Mayana Zatz (M)
Helen C Su (HC)
Jean-Laurent Casanova (JL)
Serge Bureau (S)
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Lauren Demerville (L)
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Sebastien Abad (S)
Radhiya Abassi (R)
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Abdelkrim Abdelmalek (A)
Hendy Abdoul (H)
Helene Abergel (H)
Fariza Abeud (F)
Sophie Abgrall (S)
Noemie Abisror (N)
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Commentaires et corrections

Type : UpdateOf
Type : ErratumIn

Informations de copyright

© 2023. The Author(s).

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Auteurs

Daniela Matuozzo (D)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.

Estelle Talouarn (E)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.

Astrid Marchal (A)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.

Peng Zhang (P)

St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Jeremy Manry (J)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.

Yoann Seeleuthner (Y)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.

Yu Zhang (Y)

Laboratory of Clinical Immunology and Microbiology, Division of Intramural Research, NIAID, Bethesda, MD, USA.

Alexandre Bolze (A)

Helix, San Mateo, CA, USA.

Matthieu Chaldebas (M)

St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Baptiste Milisavljevic (B)

St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Adrian Gervais (A)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.

Paul Bastard (P)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.
Pediatric Hematology-Immunology and Rheumatology Unit, Necker Hospital for Sick Children, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France.

Takaki Asano (T)

St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Lucy Bizien (L)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.

Federica Barzaghi (F)

Department of Paediatric Immunohematology, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Hassan Abolhassani (H)

Department of Biosciences and Nutrition, Karolinska Institute, Stockholm, Sweden.
Research Center for Immunodeficiencies, Pediatrics Center of Excellence, Children's Medical Center, Tehran, Iran.

Ahmad Abou Tayoun (A)

Genomics Center of Excellence, Al Jalila Children's Specialty Hospital, Dubai, United Arab Emirates.
Center for Genomic Discovery, Mohammed Bin Rashid University of Medicine and Health Sciences, Dubai, United Arab Emirates.

Alessandro Aiuti (A)

San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), IRCSS San Raffaele Scientific Institute, Milan, Italy.
Vita-Salute San Raffaele University, Milan, Italy.

Ilad Alavi Darazam (I)

Infectious Diseases and Tropical Medicine Research Center, Shahid Beheshti University of Medical Sciences, Tehran, Iran.
Department of Infectious Diseases and Tropical Medicine, Loghman Hakim Hospital, Shahid Beheshti University of Medical Sciences, Tehran, Iran.

Luis M Allende (LM)

Immunology Department, University Hospital 12 de Octubre, Research Institute imas12 and Complutense University, Madrid, Spain.

Rebeca Alonso-Arias (R)

Immunology Department, Hospital Universitario Central de Asturias; Health Research Institute of Principality of Asturias, Oviedo, Spain.

Andrés Augusto Arias (AA)

St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.
Department of Microbiology and Parasitology, Primary Immunodeficiencies Group, School of Medicine, University of Antioquia UdeA, 050010, Medellin, Colombia.
School of Microbiology, University of Antioquia UdeA, 050010, Medellin, Colombia.

Gokhan Aytekin (G)

Deparment of Internal Medicine, Division of Allergy and Immunology, Konya City Hospital, Konya, Turkey.

Peter Bergman (P)

Department of Infectious Diseases, The Immunodeficiency Unit, Karolinska University Hospital, Stockholm, Sweden.
Department of Laboratory Medicine, Division of Clinical Immunology, Stockholm, Sweden.

Simone Bondesan (S)

Clinical Genomics, IRCSS San Raffaele Scientific Institute, Milan, Italy.

Yenan T Bryceson (YT)

Department of Medicine, Centre for Hematology and Regenerative Medicine, Karolinska Institute, Stockholm, Sweden.

Ingrid G Bustos (IG)

Universidad de La Sabana, Chía, Colombia.

Oscar Cabrera-Marante (O)

Institute of Biomedical Research of IdiPAZ, University Hospital "La Paz", Madrid, Spain.

Sheila Carcel (S)

Unidad de Gestión Clínica de Cuidados Intensivos, Instituto Maimónides de Investigación Biomédica de Córdoba (IMIBIC), Hospital Universitario Reina Sofía, Universidad de Córdoba (UCO), Córdoba, Spain.

Paola Carrera (P)

Clinical Genomics, IRCSS San Raffaele Scientific Institute, Milan, Italy.

Giorgio Casari (G)

Division of Genetics and Cell Biology, Genome-Phenome Relationship, San Raffaele Hospital, Milan, Italy.
School of Medicine, Vita-Salute San Raffaele University, Milan, Italy.

Khalil Chaïbi (K)

Intensive Care Unit Department, Avicenne Hospital, Assistance Publique-Hôpitaux de Paris, Bobigny, France.
Common and Rare Kidney Diseases, Sorbonne University, INSERM UMR-S 1155, Paris, France.

Roger Colobran (R)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Catalonia, Spain.
Translational Immunology Research Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Barcelona, Catalonia, Spain.
Genetics Department, Immunology Division, Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Autonomous University of Barcelona (UAB), Barcelona, Catalonia, Spain.

Antonio Condino-Neto (A)

Department of Immunology, Institute of Biomedical Sciences, University of São Paulo, São Paulo, Brazil.

Laura E Covill (LE)

Department of Medicine, Centre for Hematology and Regenerative Medicine, Karolinska Institute, Stockholm, Sweden.

Ottavia M Delmonte (OM)

Laboratory of Clinical Immunology and Microbiology, Division of Intramural Research, NIAID, Bethesda, MD, USA.

Loubna El Zein (L)

Biology Department, Lebanese University, Beirut, Lebanon.

Carlos Flores (C)

Genomics Division, Institute of Technology and Renewable Energies (ITER), Santa Cruz de Tenerife, Spain.
CIBER de Enfermedades Respiratorias, Carlos III Health Institute, Madrid, Spain.
Research Unit, University Hospital of Ntra. Sra. de Candelaria, Santa Cruz de Tenerife, Spain.
Faculty of Health Sciences, University of Fernando Pessoa Canarias, Las Palmas de Gran Canaria, Spain.

Peter K Gregersen (PK)

Feinstein Institute for Medical Research, Northwell Health USA, Manhasset, NY, USA.

Marta Gut (M)

CNAG-CRG, Centre for Genomic Regulation (CRG), The Barcelona Institute of Science and Technology (BIST), Barcelona, Spain.

Filomeen Haerynck (F)

Department of Internal Diseases and Pediatrics, Primary Immune Deficiency Research Laboratory, Centre for Primary Immunodeficiency Ghent, Jeffrey Modell Diagnosis and Research Centre, Ghent, Belgium.

Rabih Halwani (R)

Research Institute for Medical and Health Sciences, University of Sharjah, Sharjah, United Arab Emirates.

Selda Hancerli (S)

Department of Pediatrics (Infectious Diseases), Istanbul Faculty of Medicine, Istanbul University, Istanbul, Turkey.

Lennart Hammarström (L)

Department of Biosciences and Nutrition, Karolinska Institute, Stockholm, Sweden.

Nevin Hatipoğlu (N)

Pediatric Infectious Diseases Unit, Bakirkoy Dr Sadi Konuk Training and Research Hospital, University of Health Sciences, Istanbul, Turkey.

Adem Karbuz (A)

Department of Pediatric Infectious Disease, Dr. Cemil Tascioglu City Hospital, Istanbul, Turkey.

Sevgi Keles (S)

Meram Medical Faculty, Pediatric Infectious Diseases Department, Necmettin Erbakan University, Konya, Turkey.

Christèle Kyheng (C)

Department of General Paediatrics, Hôpital Bicêtre, Assistance Publique-Hôpitaux de Paris, University of Paris Saclay, Le Kremlin-Bicêtre, France.

Rafael Leon-Lopez (R)

Unidad de Gestión Clínica de Cuidados Intensivos, Instituto Maimónides de Investigación Biomédica de Córdoba (IMIBIC), Hospital Universitario Reina Sofía, Universidad de Córdoba (UCO), Córdoba, Spain.

Jose Luis Franco (JL)

Primary Immunodeficiencies Group, Department of Microbiology and Parasitology, School of Medicine, University of Antioquia UDEA, Medellin, 050010, Colombia.

Davood Mansouri (D)

The Clinical Tuberculosis and Epidemiology Research Center, National Research Institute of Tuberculosis and Lung Diseases, Shahid Beheshti University of Medical Sciences, Tehran, Iran.
Department of Clinical Immunology and Infectious Diseases, National Research Institute of Tuberculosis and Lung Diseases, Shahid Beheshti University of Medical Sciences, Tehran, Iran.
Pediatric Respiratory Diseases Research Center, National Research Institute of Tuberculosis and Lung Diseases, Shahid Beheshti University of Medical Sciences, Tehran, Iran.

Javier Martinez-Picado (J)

IrsiCaixa AIDS Research Institute and Institute for Health Science Research Germans Trias I Pujol (IGTP), Badalona, Spain.
Institute for Health Science Research Germans Trias I Pujol (IGTP), Badalona, Spain.
Department of Infectious Diseases and Immunity, University of Vic-Central University of Catalonia, Vic, Spain.
Catalan Institution of Research and Advanced Studies (ICREA), Barcelona, Spain.
Consorcio Centro de Investigación Biomédica en Red de Enfermedades Infecciosas (CIBERINFEC), Instituto de Salud Carlos III, Madrid, Spain.

Ozge Metin Akcan (O)

Meram Medical Faculty, Pediatric Infectious Diseases Department, Necmettin Erbakan University, Konya, Turkey.

Isabelle Migeotte (I)

Centre de Génétique Humaine de L'Université Libre de Bruxelles, Hôpital Erasme, Brussels, Belgium.

Pierre-Emmanuel Morange (PE)

Laboratory of Haematology, La Timone Hospital, Marseille, France.
C2VN, INSERM, INRAE, Aix-Marseille University, Marseille, France.

Guillaume Morelle (G)

Department of General Paediatrics, Hôpital Bicêtre, Assistance Publique-Hôpitaux de Paris, University of Paris Saclay, Le Kremlin-Bicêtre, France.

Andrea Martin-Nalda (A)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Catalonia, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Autonomous University of Barcelona (UAB), Barcelona, Catalonia, Spain.
Infection and Immunity in Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Barcelona, Catalonia, Spain.

Giuseppe Novelli (G)

Department of Biomedicine and Prevention, Tor Vergata University of Rome, Rome, Italy.
IRCCS Neuromed, Pozzilli, Italy.

Antonio Novelli (A)

Laboratory of Medical Genetics, Translational Cytogenomics Research Unit, Bambino Gesù Children Hospital, IRCCS, Rome, Italy.

Tayfun Ozcelik (T)

Department of Molecular Biology and Genetics, Bilkent University, Ankara, Turkey.

Figen Palabiyik (F)

Pediatric Infectious Diseases Unit, Bakirkoy Dr Sadi Konuk Training and Research Hospital, University of Health Sciences, Istanbul, Turkey.

Qiang Pan-Hammarström (Q)

Department of Biosciences and Nutrition, Karolinska Institute, Stockholm, Sweden.

Rebeca Pérez de Diego (RP)

Laboratory of Immunogenetics of Human Diseases, IdiPAZ Institute for Health Research, University Hospital "La Paz", Madrid, Spain.

Laura Planas-Serra (L)

Neurometabolic Diseases Laboratory, Bellvitge Biomedical Research Institute (IDIBELL), Barcelona, Catalonia, Spain.
Center for Biomedical Research On Rare Diseases (CIBERER), ISCIII, Madrid, Spain.

Daniel E Pleguezuelo (DE)

Immunology Department, University Hospital 12 de Octubre, Research Institute imas12 and Complutense University, Madrid, Spain.

Carolina Prando (C)

Faculdades Pequeno Príncipe, Instituto de Pesquisa Pelé Pequeno Príncipe, Curitiba, Brazil.

Aurora Pujol (A)

Catalan Institution of Research and Advanced Studies (ICREA), Barcelona, Spain.
Neurometabolic Diseases Laboratory, Bellvitge Biomedical Research Institute (IDIBELL), Barcelona, Catalonia, Spain.
Center for Biomedical Research On Rare Diseases (CIBERER), ISCIII, Madrid, Spain.

Luis Felipe Reyes (LF)

Universidad de La Sabana, Chía, Colombia.

Jacques G Rivière (JG)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Catalonia, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Autonomous University of Barcelona (UAB), Barcelona, Catalonia, Spain.
Infection and Immunity in Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Barcelona, Catalonia, Spain.

Carlos Rodriguez-Gallego (C)

Department of Immunology, University Hospital of Gran Canaria Dr. Negrin, Canarian Health System, Las Palmas de Gran Canaria, Spain.
Department of Clinical Sciences, University of Fernando Pessoa Canarias, Las Palmas de Gran Canaria, Spain.

Julian Rojas (J)

Primary Immunodeficiencies Group, Department of Microbiology and Parasitology, School of Medicine, University of Antioquia UDEA, Medellin, 050010, Colombia.

Patrizia Rovere-Querini (P)

Vita-Salute San Raffaele University, Milan, Italy.
Division of Immunology, Transplantation and Infectious Diseases, IRCCS San Raffaele Scientific Institute, Milan, Italy.

Agatha Schlüter (A)

Neurometabolic Diseases Laboratory, Bellvitge Biomedical Research Institute (IDIBELL), Barcelona, Catalonia, Spain.
Center for Biomedical Research On Rare Diseases (CIBERER), ISCIII, Madrid, Spain.

Mohammad Shahrooei (M)

Specialized Immunology Laboratory of Dr Shahrooei, Sina Medical Complex, Ahvaz, Iran.
Department of Microbiology and Immunology, Clinical and Diagnostic Immunology, KU Leuven, Leuven, Belgium.

Ali Sobh (A)

Department of Pediatrics, Mansoura University Children's Hospital, Mansoura University Faculty of Medicine, Mansoura, Egypt.

Pere Soler-Palacin (P)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Catalonia, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Autonomous University of Barcelona (UAB), Barcelona, Catalonia, Spain.
Infection and Immunity in Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Vall d'Hebron University Hospital (HUVH), Vall d'Hebron Barcelona Hospital Campus, Barcelona, Catalonia, Spain.

Yacine Tandjaoui-Lambiotte (Y)

Hypoxia and Lung, INSERM U1272, Avicenne Hospital, Assistance Publique-Hôpitaux de Paris, Bobigny, France.

Imran Tipu (I)

Department of Life Sciences, School of Science, University of Management and Technology, Lahore, Pakistan.

Cristina Tresoldi (C)

Division of Immunology, Transplantation and Infectious Diseases, IRCCS Ospedale San Raffaele, Milan, Italy.

Jesus Troya (J)

Department of Internal Medicine, Infanta Leonor University Hospital, Madrid, Spain.

Diederik van de Beek (D)

Department of Neurology, Amsterdam UMC, Amsterdam Neuroscience, Amsterdam, Netherlands.

Mayana Zatz (M)

Biosciences Institute, University of São Paulo, São Paulo, Brazil.

Pawel Zawadzki (P)

Gordion Bioscience Inc, Cambridge, MA, USA.
Faculty of Physics, Adam Mickiewicz University, Poznan, Poland.

Saleh Zaid Al-Muhsen (SZ)

Department of Pediatrics, Immunology Research Laboratory, College of Medicine and King Saud University Medical City, King Saud University, Riyadh, Saudi Arabia.

Mohammed Faraj Alosaimi (MF)

Department of Pediatrics, Immunology Research Laboratory, College of Medicine and King Saud University Medical City, King Saud University, Riyadh, Saudi Arabia.

Fahad M Alsohime (FM)

Department of Pediatrics, Immunology Research Laboratory, College of Medicine and King Saud University Medical City, King Saud University, Riyadh, Saudi Arabia.

Hagit Baris-Feldman (H)

The Genetics Institute, Tel Aviv Sourasky Medical Center, Tel Aviv, Israel.
Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel.

Manish J Butte (MJ)

Departments of Pediatrics and Microbiology, Immunology, and Molecular Genetics, Division of Immunology, Allergy, and Rheumatology, University of California Los Angeles, Los Angeles, CA, USA.

Stefan N Constantinescu (SN)

Ludwig Institute for Cancer Research, Brussels, Belgium.
SIGN Unit, de Duve Institute, Université Catholique de Louvain, Brussels, Belgium.
WELBIO (Walloon Excellence in Life Sciences and Biotechnology), Brussels, Belgium.
Nuffield Department of Medicine, Ludwig Institute for Cancer Research, Oxford University, Oxford, UK.

Megan A Cooper (MA)

Department of Pediatrics, Division of Rheumatology/Immunology, Washington University in St. Louis, St. Louis, MO, USA.

Clifton L Dalgard (CL)

The American Genome Center, Uniformed Services University of the Health Sciences, Bethesda, USA.
Department of Anatomy, Physiology & Genetics, Uniformed Services University of the Health Sciences, Bethesda, MD, USA.

Jacques Fellay (J)

School of Life Sciences, École Polytechnique Fédérale de Lausanne, Lausanne, Switzerland.
Swiss Institute of Bioinformatics, Lausanne, Switzerland.
Precision Medicine Unit, Lausanne University Hospital and University of Lausanne, Lausanne, Switzerland.

James R Heath (JR)

Institute for Systems Biology, Seattle, WA, USA.

Yu-Lung Lau (YL)

Department of Paediatrics and Adolescent Medicine, Queen Mary Hospital, Li Ka Shing Faculty of Medicine, University of Hong Kong, Hong Kong, China.

Richard P Lifton (RP)

Laboratory of Genetics and Genomics, The Rockefeller University, New York, NY, USA.
Department of Genetics, Yale University School of Medicine, New Haven, CT, USA.
Yale Center for Genome Analysis, Yale School of Medicine, New Haven, CT, USA.

Tom Maniatis (T)

Zukerman Mind Brain Behavior Institute, Columbia University, New York, NY, USA.
New York Genome Center, New York, NY, USA.

Trine H Mogensen (TH)

Department of Biomedicine, Aarhus University, Aarhus, Denmark.
Department of Infectious Diseases, Aarhus University Hospital, Aarhus, Denmark.

Horst von Bernuth (H)

Department of Paediatric Respiratory Medicine, Immunology, and Critical Care Medicine, Charité Universitätsmedizin Berlin, Berlin, Germany.

Alban Lermine (A)

Laboratoire de Biologie Médicale Multisites Seqoia, MG2025, MG2025, Paris, France.

Michel Vidaud (M)

Laboratoire de Biologie Médicale Multisites Seqoia, MG2025, MG2025, Paris, France.

Anne Boland (A)

Université Paris-Saclay, CEA, Centre National de Recherche en Génomique Humaine (CNRGH), Evry, France.

Jean-François Deleuze (JF)

Université Paris-Saclay, CEA, Centre National de Recherche en Génomique Humaine (CNRGH), Evry, France.

Robert Nussbaum (R)

Invitae, San Francisco, CA, USA.

Amanda Kahn-Kirby (A)

Invitae, San Francisco, CA, USA.

France Mentre (F)

Unité de Recherche Clinique, Hôpital Bichat, Assistance Publique-Hôpitaux de Paris, Paris, France.

Sarah Tubiana (S)

Centre d'Investigation Clinique, Hôpital Bichat, Assistance Publique-Hôpitaux de Paris, Paris, France.

Guy Gorochov (G)

Sorbonne Université, INSERM Centre d'Immunologie et des Maladies Infectieuses, CIMI-Paris, Département d'immunologie Hôpital Pitié-Salpêtrière, Assistance Publique-Hôpitaux de Paris, Paris, France.

Florence Tubach (F)

Sorbonne Université, INSERM, Institut Pierre Louis d'Epidémiologie et de Santé Publique, AP-HP, Hôpital Pitié Salpêtrière, Département de Santé Publique, Unité de Recherche Clinique PSL-CFX , CIC-1901, Paris, France.

Pierre Hausfater (P)

Emergency Department, Hôpital Pitié-Salpêtrière, APHP-Sorbonne Université, Paris, France.
GRC-14 BIOFAST Sorbonn Université, UMR INSERM 1135, CIMI, Sorbonne Université, Paris, France.

Isabelle Meyts (I)

Department of Microbiology, Immunology and Transplantation, Laboratory for Inborn Errors of Immunity, KU Leuven, Leuven, Belgium.

Shen-Ying Zhang (SY)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Anne Puel (A)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Luigi D Notarangelo (LD)

Laboratory of Host Defenses, NIAID, National Institutes of Health, Bethesda, MA, USA.

Stephanie Boisson-Dupuis (S)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Helen C Su (HC)

Laboratory of Clinical Immunology and Microbiology, Division of Intramural Research, NIAID, Bethesda, MD, USA.

Bertrand Boisson (B)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Emmanuelle Jouanguy (E)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Jean-Laurent Casanova (JL)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France. casanova@rockefeller.edu.
University Paris Cité, Imagine Institute, Paris, France. casanova@rockefeller.edu.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA. casanova@rockefeller.edu.
Howard Hughes Medical Institute, New York, NY, USA. casanova@rockefeller.edu.

Qian Zhang (Q)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Laurent Abel (L)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France.
University Paris Cité, Imagine Institute, Paris, France.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA.

Aurélie Cobat (A)

Laboratory of Human Genetics of Infectious Diseases, Necker Branch, INSERM U1163, Paris, France. aurelie.cobat@inserm.fr.
University Paris Cité, Imagine Institute, Paris, France. aurelie.cobat@inserm.fr.
St. Giles Laboratory of Human Genetics of Infectious Diseases, Rockefeller Branch, The Rockefeller University, New York, NY, USA. aurelie.cobat@inserm.fr.

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