Preclinical discovery and initial clinical data of WVT078, a BCMA × CD3 bispecific antibody.


Journal

Leukemia
ISSN: 1476-5551
Titre abrégé: Leukemia
Pays: England
ID NLM: 8704895

Informations de publication

Date de publication:
06 2023
Historique:
received: 29 08 2022
accepted: 20 03 2023
revised: 16 03 2023
medline: 8 6 2023
pubmed: 7 4 2023
entrez: 6 4 2023
Statut: ppublish

Résumé

B-cell maturation antigen (BCMA) is an ideal target in multiple myeloma (MM) due to highly specific expression in malignant plasma cells. BCMA-directed therapies including antibody drug conjugates, chimeric antigen receptor-T cells and bispecific antibodies (BsAbs) have shown high response rates in MM. WVT078 is an anti-BCMA× anti-CD3 BsAb that binds to BCMA with subnanomolar-affinity. It was selected based on potent T cell activation and anti-MM activity in preclinical models with favorable tolerability in cynomolgus monkey. In the ongoing first-in-human phase I dose-escalation study (NCT04123418), 33 patients received intravenous WVT078 once weekly at escalated dosing. At the active doses of 48-250 µg/kg tested to date (n = 26), the overall response rate (ORR) was 38.5% (90% CI: 22.6-56.4%) and the complete response rate (CRR, stringent complete response + complete response) was 11.5%, (90% CI: 3.2-27.2%). At the highest dose level tested, the ORR was 75% (3 of 4 patients). 26 (78.8%) patients reported at least one Grade ≥3 AE and 16 of these AEs were suspected to be drug related. 20 patients (60.6%) experienced cytokine release syndrome. WVT078 has an acceptable safety profile and shows preliminary evidence of clinical activity at doses tested to date.

Identifiants

pubmed: 37024520
doi: 10.1038/s41375-023-01883-3
pii: 10.1038/s41375-023-01883-3
doi:

Substances chimiques

B-Cell Maturation Antigen 0
Immunoconjugates 0
Antibodies, Bispecific 0

Banques de données

ClinicalTrials.gov
['NCT04123418']

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

1349-1360

Informations de copyright

© 2023. The Author(s), under exclusive licence to Springer Nature Limited.

Références

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Auteurs

Marc S Raab (MS)

Department of Internal Medicine V, Heidelberg University Hospital, Heidelberg, Germany.

Yael C Cohen (YC)

Department of Hematology, Tel-Aviv Sourasky (Ichilov) Medical Center, Tel Aviv University, Tel Aviv, Israel.
Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel.

Fredrik Schjesvold (F)

Oslo Myeloma Center, Department of Hematology, Oslo University Hospital, Oslo, Norway.

Kimberly Aardalen (K)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Adwait Oka (A)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Andrew Spencer (A)

Department of Malignant Haematology, The Alfred Hospital, Melbourne, VIC, Australia.

Martin Wermke (M)

NCT/UCC Early Clinical Trial Unit, Universitätsklinikum Carl Gustav Carus an der Technische Universität, Dresden, Germany.

Anita D Souza (AD)

Division of Hematology & Oncology, Medical College of Wisconsin, Milwaukee, WI, USA.

Jonathan L Kaufman (JL)

Winship Cancer Institute, Emory University, Atlanta, GA, USA.

Anna Maria Cafro (AM)

Department of Hematology, Niguarda Hospital, Niguarda, Milan, Italy.

Enrique M Ocio (EM)

Hospital Universitario Marqués de Valdecilla (IDIVAL), Universidad de Cantabria, Santander, Spain.

Noriko Doki (N)

Hematology Division, Tokyo Metropolitan Cancer and Infectious Diseases Center, Komagome Hospital, Tokyo, Japan.

Kristin Henson (K)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Gina Trabucco (G)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Ana Carrion (A)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Florent C Bender (FC)

Novartis Institutes for BioMedical Research, Basel, Switzerland.

Pierre-Eric Juif (PE)

Novartis Institutes for BioMedical Research, Basel, Switzerland.

Adonai Fessehatsion (A)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Liqiong Fan (L)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Jeffrey P Stonehouse (JP)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

John W Blankenship (JW)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Brian Granda (B)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA.

Serena De Vita (S)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA. serena.de_vita@novartis.com.

Haihui Lu (H)

Novartis Institutes for BioMedical Research, Cambridge, MA, USA. haihui.lu@novartis.com.

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