Mutation spectrum analysis of


Journal

F1000Research
ISSN: 2046-1402
Titre abrégé: F1000Res
Pays: England
ID NLM: 101594320

Informations de publication

Date de publication:
2022
Historique:
accepted: 13 11 2023
medline: 28 11 2023
pubmed: 27 11 2023
entrez: 27 11 2023
Statut: epublish

Résumé

Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD) are allelic disorders caused by mutations in the This study is a cross sectional study that enrolled 43 male patients with a clinical suspicion of Out of 43 subjects, deletions accounted for 69.77% (n=30) cases, while duplications were found in 11.63% (n=5) cases. One novel duplication spanning exons 2 to 62 was identified. Deletion mutations clustered around the distal (66.67%) and proximal (26.67%) hot spot regions of the This is the first comprehensive study showing the feasibility of implementing the MLPA method for routine screening of

Sections du résumé

Background UNASSIGNED
Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD) are allelic disorders caused by mutations in the
Methods UNASSIGNED
This study is a cross sectional study that enrolled 43 male patients with a clinical suspicion of
Results UNASSIGNED
Out of 43 subjects, deletions accounted for 69.77% (n=30) cases, while duplications were found in 11.63% (n=5) cases. One novel duplication spanning exons 2 to 62 was identified. Deletion mutations clustered around the distal (66.67%) and proximal (26.67%) hot spot regions of the
Conclusion UNASSIGNED
This is the first comprehensive study showing the feasibility of implementing the MLPA method for routine screening of

Identifiants

pubmed: 38009102
doi: 10.12688/f1000research.73476.3
pmc: PMC10668572
doi:

Substances chimiques

Dystrophin 0
DMD protein, human 0

Banques de données

figshare
['10.6084/m9.figshare.15172167.V2']

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

148

Informations de copyright

Copyright: © 2023 Dwianingsih EK et al.

Déclaration de conflit d'intérêts

No competing interests were disclosed.

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Auteurs

Ery Kus Dwianingsih (EK)

Genetics Working Group, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.
Dr. Sardjito General Hospital, Yogyakarta, 55281, Indonesia.
Department of Anatomical Pathology, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.

Kristy Iskandar (K)

Genetics Working Group, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.
Academic Hospital, Universitas Gadjah Mada, Yogyakarta, 55291, Indonesia.
Department of Child Health, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.

Sunartini Hapsara (S)

Academic Hospital, Universitas Gadjah Mada, Yogyakarta, 55291, Indonesia.
Department of Child Health, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.

Chun Ping Liu (C)

Department of Pediatrics, Yong Loo Lin School of Medicine, National University of Singapore, Singapore, 119228, Singapore.

Rusdy Ghazali Malueka (RG)

Genetics Working Group, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.
Dr. Sardjito General Hospital, Yogyakarta, 55281, Indonesia.
Department of Neurology, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.
Genetics Working Group, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.
Dr. Sardjito General Hospital, Yogyakarta, 55281, Indonesia.
Pediatric Surgery Division, Department of Surgery, Faculty of Medicine, Public Health and Nursing, Universitas Gadjah Mada, Yogyakarta, 55281, Indonesia.

Masafumi Matsuo (M)

KNC Department of Nucleic Acid Drug Discovery, Faculty of Rehabilitation, Kobegakuin University, Kobe, 651-2180, Japan.

Poh San Lai (PS)

Department of Pediatrics, Yong Loo Lin School of Medicine, National University of Singapore, Singapore, 119228, Singapore.

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