Diego Leon-Rico

Affiliations

Infection, Immunity and Inflammation Research and Teaching Department, Great Ormond Street Institute of Child Health, University College London, 30 Guilford Street, London, WC1N 1EH, UK.

Publications (6)

Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich Syndrome.

Nature communications

Avec: Rajeev Rai , Marianna Romito , Elizabeth Rivers , Giandomenico Turchiano , Georges Blattner , Winston Vetharoy , Dariusz Ladon , Geoffroy Andrieux , Fang Zhang , Marta Zinicola , Diego Leon-Rico , Giorgia Santilli , Adrian J Thrasher , Alessia Cavazza

Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.

The New England journal of medicine

Avec: Donald B Kohn , Claire Booth , Kit L Shaw , Jinhua Xu-Bayford , Elizabeth Garabedian , Valentina Trevisan , Denise A Carbonaro-Sarracino , Kajal Soni , Dayna Terrazas , Katie Snell , Alan Ikeda , Diego Leon-Rico , Theodore B Moore , Karen F Buckland , Ami J Shah , Kimberly C Gilmour , Satiro De Oliveira , Christine Rivat , Gay M Crooks , Natalia Izotova , John Tse , Stuart Adams , Sally Shupien , Hilory Ricketts , Alejandra Davila , Chilenwa Uzowuru , Amalia Icreverzi , Provaboti Barman , Beatriz Campo Fernandez , Roger P Hollis , Maritess Coronel , Allen Yu , Krista M Chun , Christian E Casas , Ruixue Zhang , Serena Arduini , Frances Lynn , Mahesh Kudari , Andrea Spezzi , Marco Zahn , Rene Heimke , Ivan Labik , Roberta Parrott , Rebecca H Buckley , Lilith Reeves , Kenneth Cornetta , Robert Sokolic , Michael Hershfield , Manfred Schmidt , Fabio Candotti , Harry L Malech , Adrian J Thrasher , H Bobby Gaspar

The downregulated membrane expression of CD18 in CD34

Stem cell research & therapy

Avec: Cristina Mesa-Núñez , Diego Leon-Rico , Montserrat Aldea , Carlos Damián , Raquel Sanchez-Baltasar , Rebeca Sanchez , Omaira Alberquilla , José Carlos Segovia , Juan Antonio Bueren , Elena Almarza

Preclinical Optimization and Safety Studies of a New Lentiviral Gene Therapy for p47

Human gene therapy

Avec: Andrea Schejtman , Winston Vetharoy , Uimook Choi , Christine Rivat , Narda Theobald , Giuseppa Piras , Diego Leon-Rico , Karen Buckland , Elena Armenteros-Monterroso , Sara Benedetti , Michael T Ashworth , Michael Rothe , Axel Schambach , Hubert Bobby Gaspar , Elizabeth M Kang , Harry L Malech , Adrian J Thrasher , Giorgia Santilli

Lentiviral gene therapy for X-linked chronic granulomatous disease.

Nature medicine

Avec: Donald B Kohn , Claire Booth , Elizabeth M Kang , Sung-Yun Pai , Kit L Shaw , Giorgia Santilli , Myriam Armant , Karen F Buckland , Uimook Choi , Suk See De Ravin , Morna J Dorsey , Caroline Y Kuo , Diego Leon-Rico , Christine Rivat , Natalia Izotova , Kimberly Gilmour , Katie Snell , Jinhua Xu-Bayford Dip , Jinan Darwish , Emma C Morris , Dayna Terrazas , Leo D Wang , Christopher A Bauser , Tobias Paprotka , Douglas B Kuhns , John Gregg , Hayley E Raymond , John K Everett , Geraldine Honnet , Luca Biasco , Peter E Newburger , Frederic D Bushman , Manuel Grez , H Bobby Gaspar , David A Williams , Harry L Malech , Anne Galy , Adrian J Thrasher , Auteur inconnu

Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease.

Molecular therapy. Methods & clinical development

Avec: Giuseppa Piras , Claudia Montiel-Equihua , Yee-Ka Agnes Chan , Slawomir Wantuch , Daniel Stuckey , Derek Burke , Helen Prunty , Rahul Phadke , Darren Chambers , Armando Partida-Gaytan , Diego Leon-Rico , Neelam Panchal , Kathryn Whitmore , Miguel Calero , Sara Benedetti , Giorgia Santilli , Adrian J Thrasher , H Bobby Gaspar

Réseau de co-auteurs

Adrian J Thrasher 5 collaborations

Giorgia Santilli 4 collaborations

Christine Rivat 3 collaborations

Harry L Malech 3 collaborations

H Bobby Gaspar 3 collaborations

Winston Vetharoy 2 collaborations

Donald B Kohn 2 collaborations

Claire Booth 2 collaborations

Kit L Shaw 2 collaborations

Dayna Terrazas 2 collaborations

Katie Snell 2 collaborations

Karen F Buckland 2 collaborations

Natalia Izotova 2 collaborations

Uimook Choi 2 collaborations

Giuseppa Piras 2 collaborations

Sara Benedetti 2 collaborations

Elizabeth M Kang 2 collaborations

Rajeev Rai 1 collaboration

Marianna Romito 1 collaboration

Elizabeth Rivers 1 collaboration

Giandomenico Turchiano 1 collaboration

Georges Blattner 1 collaboration

Dariusz Ladon 1 collaboration

Geoffroy Andrieux 1 collaboration

Fang Zhang 1 collaboration

Marta Zinicola 1 collaboration

Alessia Cavazza 1 collaboration

Jinhua Xu-Bayford 1 collaboration

Elizabeth Garabedian 1 collaboration

Valentina Trevisan 1 collaboration

Denise A Carbonaro-Sarracino 1 collaboration

Kajal Soni 1 collaboration

Alan Ikeda 1 collaboration

Theodore B Moore 1 collaboration

Ami J Shah 1 collaboration

Kimberly C Gilmour 1 collaboration

Satiro De Oliveira 1 collaboration

Gay M Crooks 1 collaboration

John Tse 1 collaboration

Stuart Adams 1 collaboration

Sally Shupien 1 collaboration

Hilory Ricketts 1 collaboration

Alejandra Davila 1 collaboration

Chilenwa Uzowuru 1 collaboration

Amalia Icreverzi 1 collaboration

Provaboti Barman 1 collaboration

Beatriz Campo Fernandez 1 collaboration

Roger P Hollis 1 collaboration

Maritess Coronel 1 collaboration

Allen Yu 1 collaboration

Krista M Chun 1 collaboration

Christian E Casas 1 collaboration

Ruixue Zhang 1 collaboration

Serena Arduini 1 collaboration

Frances Lynn 1 collaboration

Mahesh Kudari 1 collaboration

Andrea Spezzi 1 collaboration

Marco Zahn 1 collaboration

Rene Heimke 1 collaboration

Ivan Labik 1 collaboration

Roberta Parrott 1 collaboration

Rebecca H Buckley 1 collaboration

Lilith Reeves 1 collaboration

Kenneth Cornetta 1 collaboration

Robert Sokolic 1 collaboration

Michael Hershfield 1 collaboration

Manfred Schmidt 1 collaboration

Fabio Candotti 1 collaboration

Cristina Mesa-Núñez 1 collaboration

Montserrat Aldea 1 collaboration

Carlos Damián 1 collaboration

Raquel Sanchez-Baltasar 1 collaboration

Rebeca Sanchez 1 collaboration

Omaira Alberquilla 1 collaboration

José Carlos Segovia 1 collaboration

Juan Antonio Bueren 1 collaboration

Elena Almarza 1 collaboration

Andrea Schejtman 1 collaboration

Narda Theobald 1 collaboration

Karen Buckland 1 collaboration

Elena Armenteros-Monterroso 1 collaboration

Michael T Ashworth 1 collaboration

Michael Rothe 1 collaboration

Axel Schambach 1 collaboration

Hubert Bobby Gaspar 1 collaboration

Sung-Yun Pai 1 collaboration

Myriam Armant 1 collaboration

Suk See De Ravin 1 collaboration

Morna J Dorsey 1 collaboration

Caroline Y Kuo 1 collaboration

Kimberly Gilmour 1 collaboration

Jinhua Xu-Bayford Dip 1 collaboration

Jinan Darwish 1 collaboration

Emma C Morris 1 collaboration

Leo D Wang 1 collaboration

Christopher A Bauser 1 collaboration

Tobias Paprotka 1 collaboration

Douglas B Kuhns 1 collaboration

John Gregg 1 collaboration

Hayley E Raymond 1 collaboration

John K Everett 1 collaboration

Geraldine Honnet 1 collaboration

Luca Biasco 1 collaboration

Peter E Newburger 1 collaboration

Frederic D Bushman 1 collaboration

Manuel Grez 1 collaboration

David A Williams 1 collaboration

Anne Galy 1 collaboration

None None 1 collaboration

Claudia Montiel-Equihua 1 collaboration

Yee-Ka Agnes Chan 1 collaboration

Slawomir Wantuch 1 collaboration

Daniel Stuckey 1 collaboration

Derek Burke 1 collaboration

Helen Prunty 1 collaboration

Rahul Phadke 1 collaboration

Darren Chambers 1 collaboration

Armando Partida-Gaytan 1 collaboration

Neelam Panchal 1 collaboration

Kathryn Whitmore 1 collaboration

Miguel Calero 1 collaboration